Open reading frame correction using splice-switching antisense oligonucleotides for the treatment of cystic fibrosis
Michaels, Wren E, Pena-Rasgado, Cecilia, Kotaria, Rusudan, Bridges, Robert J, Hastings, Michelle L
Published in Proceedings of the National Academy of Sciences - PNAS (18.01.2022)
Published in Proceedings of the National Academy of Sciences - PNAS (18.01.2022)
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