Adeno-associated virus serotype 9 antibodies in patients screened for treatment with onasemnogene abeparvovec
Day, John W., Finkel, Richard S., Mercuri, Eugenio, Swoboda, Kathryn J., Menier, Melissa, van Olden, Rudolf, Tauscher-Wisniewski, Sitra, Mendell, Jerry R.
Published in Molecular therapy. Methods & clinical development (11.06.2021)
Published in Molecular therapy. Methods & clinical development (11.06.2021)
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Journal Article
Impact of Age and Motor Function in a Phase 1/2A Study of Infants With SMA Type 1 Receiving Single-Dose Gene Replacement Therapy
Lowes, Linda P., Alfano, Lindsay N., Arnold, W. David, Shell, Richard, Prior, Thomas W., McColly, Markus, Lehman, Kelly J., Church, Kathleen, Sproule, Douglas M., Nagendran, Sukumar, Menier, Melissa, Feltner, Douglas E., Wells, Courtney, Kissel, John T., Al-Zaidy, Samiah, Mendell, Jerry
Published in Pediatric neurology (01.09.2019)
Published in Pediatric neurology (01.09.2019)
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Journal Article
AVXS-101 (Onasemnogene Abeparvovec) for SMA1: Comparative Study with a Prospective Natural History Cohort
Al-Zaidy, Samiah A, Kolb, Stephen J, Lowes, Linda, Alfano, Lindsay N, Shell, Richard, Church, Kathleen R, Nagendran, Sukumar, Sproule, Douglas M, Feltner, Douglas E, Wells, Courtney, Ogrinc, Francis, Menier, Melissa, L'Italien, James, Arnold, W David, Kissel, John T, Kaspar, Brian K, Mendell, Jerry R
Published in Journal of neuromuscular diseases (2019)
Published in Journal of neuromuscular diseases (2019)
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Journal Article
High Healthcare Resource Use in Hospitalized Patients with a Diagnosis of Spinal Muscular Atrophy Type 1 (SMA1): Retrospective Analysis of the Kids’ Inpatient Database (KID)
Cardenas, Jessica, Menier, Melissa, Heitzer, Marjet D., Sproule, Douglas M.
Published in PharmacoEconomics - open (01.06.2019)
Published in PharmacoEconomics - open (01.06.2019)
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Journal Article
A convex urostomy pouch with adhesive border: a patient survey
McPhail, Jacqueline, Nichols, Thom, Menier, Melissa
Published in British journal of nursing (Mark Allen Publishing) (11.12.2014)
Published in British journal of nursing (Mark Allen Publishing) (11.12.2014)
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