SMA – THERAPY: P.262 Value of onasemnogene abeparvovec in spinal muscular atrophy type 1: improvements in motor function, ventilation-free survival, and hospitalizations
Dabbous, O., Reyna, S., Feltner, D., Ogrinc, F., Menier, M., Ouyang, H., Droege, M., Bischof, M., LaMarca, N., Arunji, R.
Published in Neuromuscular disorders : NMD (01.10.2020)
Published in Neuromuscular disorders : NMD (01.10.2020)
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Journal Article
SMA – THERAPY
Dabbous, O., Reyna, S., Feltner, D., Ogrinc, F., Menier, M., Ouyang, H., Droege, M., Bischof, M., LaMarca, N., Arunji, R.
Published in Neuromuscular disorders : NMD (01.10.2020)
Published in Neuromuscular disorders : NMD (01.10.2020)
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Journal Article
SMA - TREATMENT: EP.290 Newborn screening (NBS) for spinal muscular atrophy (SMA) in the United States (US): Early findings from the RESTORE registry
Servais, L., De Vivo, D., Kirschner, J., Mercuri, E., Muntoni, F., Tizzano, E., Roy, S., Saito, K., Menier, M., LaMarca, N., Anderson, F., Dabbous, O., Finkel, R.
Published in Neuromuscular disorders : NMD (01.10.2021)
Published in Neuromuscular disorders : NMD (01.10.2021)
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Journal Article
SMA - TREATMENT
Servais, L., De Vivo, D., Kirschner, J., Mercuri, E., Muntoni, F., Tizzano, E., Roy, S., Saito, K., Menier, M., LaMarca, N., Anderson, F., Dabbous, O., Finkel, R.
Published in Neuromuscular disorders : NMD (01.10.2021)
Published in Neuromuscular disorders : NMD (01.10.2021)
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Journal Article
SMA - TREATMENT: EP.289 Routine practices in use of onasemnogene abeparvovec (OA) in older patients with spinal muscular atrophy (SMA): Early findings from RESTORE
Servais, L., De Vivo, D., Kirschner, J., Mercuri, E., Muntoni, F., Tizzano, E., Roy, S., Saito, K., Menier, M., LaMarca, N., Anderson, F., Dabbous, O., Finkel, R.
Published in Neuromuscular disorders : NMD (01.10.2021)
Published in Neuromuscular disorders : NMD (01.10.2021)
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Journal Article
SMA - TREATMENT
Servais, L., De Vivo, D., Kirschner, J., Mercuri, E., Muntoni, F., Tizzano, E., Roy, S., Saito, K., Menier, M., LaMarca, N., Anderson, F., Dabbous, O., Finkel, R.
Published in Neuromuscular disorders : NMD (01.10.2021)
Published in Neuromuscular disorders : NMD (01.10.2021)
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Journal Article
SMA THERAPIES I: P.182Early diagnosis and speed to effect in infant-onset spinal muscular atrophy
Dabbous, O., Droege, M., Feltner, D., Novack, A., Menier, M., Ryman, D., Sproule, D.
Published in Neuromuscular disorders : NMD (01.10.2018)
Published in Neuromuscular disorders : NMD (01.10.2018)
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Journal Article
SMA THERAPIES I
Dabbous, O., Droege, M., Feltner, D., Novack, A., Menier, M., Ryman, D., Sproule, D.
Published in Neuromuscular disorders : NMD (01.10.2018)
Published in Neuromuscular disorders : NMD (01.10.2018)
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Journal Article
PSY18 - RAPID IMPROVEMENTS IN MOTOR FUNCTION IN SPINAL MUSCULAR ATROPHY TYPE 1 FOLLOWING AVXS-101 GENE REPLACEMENT THERAPY
Dabbous, O., Droege, M., Feltner, D., Novack, A., Menier, M., Ryman, D., Sproule, D.M.
Published in Value in health (01.10.2018)
Published in Value in health (01.10.2018)
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Journal Article
P.209Event-free survival and motor milestone achievement following onasemnogene abeparvovec and nusinersen interventions contrasted to natural history for spinal muscular atrophy t1 (SMA1) patients
Dabbous, O., Sproule, D., Feltner, D., Ogrinc, F., Menier, M., Droege, M., Maru, B., Khan, F., Arjunji, R.
Published in Neuromuscular disorders : NMD (01.10.2019)
Published in Neuromuscular disorders : NMD (01.10.2019)
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P.357Type I spinal muscular atrophy patients treated with AVXS-101 have greater health outcome improvements and lower use of ventilatory support, hospitalization, and associated costs contrasted to those treated with nusinersen
Arjunji, R., Dean, R., Jensen, I., Miller, B., Menier, M., Sproule, D., Feltner, D., Droege, M., Khan, F., Dabbous, O.
Published in Neuromuscular disorders : NMD (01.10.2019)
Published in Neuromuscular disorders : NMD (01.10.2019)
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Journal Article
PRO2 THE VALUE OF ONASEMNOGENE ABEPARVOVEC GENE-REPLACEMENT THERAPY IN IMPROVING SURVIVAL AND MOTOR FUNCTION AND DECREASING VENTILATORY SUPPORT AND HOSPITALIZATION CONTRASTED TO NATURAL HISTORY FOR SPINAL MUSCULAR ATROPHY TYPE 1
Dabbous, O., Sproule, D.M., Feltner, D.E., Ogrinc, F.G., Menier, M., Droege, M., Maru, B., Khan, F., Arjunji, R.
Published in Value in health (01.11.2019)
Published in Value in health (01.11.2019)
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Journal Article
SMA – THERAPY
Chand, D., Finkel, R., Mercuri, E., Masson, R., Parsons, J., Kleyn, A., Menier, M., Montgomery, K., Sproule, D., Reyna, S., Feltner, D., Tauscher-Wisniewki, S., Mendell, J.
Published in Neuromuscular disorders : NMD (01.10.2020)
Published in Neuromuscular disorders : NMD (01.10.2020)
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Journal Article
SMA – THERAPY: P.256 Intravenous (IV) onasemnogene abeparvovec for spinal muscular atrophy (SMA): integrated safety report
Chand, D., Finkel, R., Mercuri, E., Masson, R., Parsons, J., Kleyn, A., Menier, M., Montgomery, K., Sproule, D., Reyna, S., Feltner, D., Tauscher-Wisniewki, S., Mendell, J.
Published in Neuromuscular disorders : NMD (01.10.2020)
Published in Neuromuscular disorders : NMD (01.10.2020)
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Journal Article
SMA - TREATMENT
Servais, L., Day, J., De Vivo, D., Mercuri, E., Muntoni, F., Shieh, P., Tizzano, E., Desguerre, I., Saito, K., Menier, M., LaMarca, N., Anderson, F., Dabbous, O., Finkel, R.
Published in Neuromuscular disorders : NMD (01.10.2021)
Published in Neuromuscular disorders : NMD (01.10.2021)
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Journal Article
SMA - TREATMENT: EP.291 Real-world treatment patterns and outcomes in patients with spinal muscular atrophy (SMA): Updated findings from the RESTORE Registry
Servais, L., Day, J., De Vivo, D., Mercuri, E., Muntoni, F., Shieh, P., Tizzano, E., Desguerre, I., Saito, K., Menier, M., LaMarca, N., Anderson, F., Dabbous, O., Finkel, R.
Published in Neuromuscular disorders : NMD (01.10.2021)
Published in Neuromuscular disorders : NMD (01.10.2021)
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Journal Article
PBI10 TYPE I SPINAL MUSCULAR ATROPHY PATIENTS TREATED WITH AVXS-101 HAVE LOWER USE OF VENTILATORY SUPPORT, HOSPITALIZATION, AND ASSOCIATED COSTS COMPARED TO THOSE TREATED WITH NUSINERSEN
Arjunji, R., Dean, R., Jensen, I.S., Miller, B., Menier, M., Sproule, D.M., Feltner, D.E., Droege, M., Khan, F., Dabbous, O.
Published in Value in health (01.05.2019)
Published in Value in health (01.05.2019)
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Journal Article