Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study
Smith, Edward C., Conklin, Laurie S., Hoffman, Eric P., Clemens, Paula R., Mah, Jean K., Finkel, Richard S., Guglieri, Michela, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M., Webster, Richard, Castro, Diana, Kuntz, Nancy L., Kerchner, Laurie, Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Jaros, Mark, Shale, Phil, Gordish-Dressman, Heather, Hagerty, Laura, Dang, Utkarsh J., Damsker, Jesse M., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., McDonald, Craig M.
Published in PLoS medicine (01.09.2020)
Published in PLoS medicine (01.09.2020)
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Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function
Hoffman, Eric P, Schwartz, Benjamin D, Mengle-Gaw, Laurel J, Smith, Edward C, Castro, Diana, Mah, Jean K, McDonald, Craig M, Kuntz, Nancy L, Finkel, Richard S, Guglieri, Michela, Bushby, Katharine, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M, Webster, Richard, Smith, Andrea L, Morgenroth, Lauren P, Arrieta, Adrienne, Shimony, Maya, Siener, Catherine, Jaros, Mark, Shale, Phil, McCall, John M, Nagaraju, Kanneboyina, van den Anker, John, Conklin, Laurie S, Cnaan, Avital, Gordish-Dressman, Heather, Damsker, Jesse M, Clemens, Paula R
Published in Neurology (24.09.2019)
Published in Neurology (24.09.2019)
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Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial
Guglieri, Michela, Clemens, Paula R, Perlman, Seth J, Smith, Edward C, Horrocks, Iain, Finkel, Richard S, Mah, Jean K, Deconinck, Nicolas, Goemans, Nathalie, Haberlova, Jana, Straub, Volker, Mengle-Gaw, Laurel J, Schwartz, Benjamin D, Harper, Amy D, Shieh, Perry B, De Waele, Liesbeth, Castro, Diana, Yang, Michelle L, Ryan, Monique M, McDonald, Craig M, Tulinius, Mar, Webster, Richard, McMillan, Hugh J, Kuntz, Nancy L, Rao, Vashmi K, Baranello, Giovanni, Spinty, Stefan, Childs, Anne-Marie, Sbrocchi, Annie M, Selby, Kathryn A, Monduy, Migvis, Nevo, Yoram, Vilchez-Padilla, Juan J, Nascimento-Osorio, Andres, Niks, Erik H, de Groot, Imelda JM, Katsalouli, Marina, James, Meredith K, van den Anker, Johannes, Damsker, Jesse M, Ahmet, Alexandra, Ward, Leanne M, Jaros, Mark, Shale, Phil, Dang, Utkarsh J, Hoffman, Eric P
Published in Archives of neurology (Chicago) (01.10.2022)
Published in Archives of neurology (Chicago) (01.10.2022)
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Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug
Conklin, Laurie S., Damsker, Jesse M., Hoffman, Eric P., Jusko, William J., Mavroudis, Panteleimon D., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., Smith, Edward C., Mah, Jean K., Guglieri, Michela, Nevo, Yoram, Kuntz, Nancy, McDonald, Craig M., Tulinius, Mar, Ryan, Monique M., Webster, Richard, Castro, Diana, Finkel, Richard S., Smith, Andrea L., Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Jaros, Mark, Shale, Phil, McCall, John M., Hathout, Yetrib, Nagaraju, Kanneboyina, van den Anker, John, Ward, Leanne M., Ahmet, Alexandra, Cornish, Michaelyn R., Clemens, Paula R.
Published in Pharmacological research (01.10.2018)
Published in Pharmacological research (01.10.2018)
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Efficacy and safety of tacrolimus in patients with rheumatoid arthritis: A double‐blind trial
Yocum, David E., Furst, Daniel E., Kaine, Jeffrey L., Baldassare, Andrew R., Stevenson, Jon T., Borton, Mary Ann, Mengle‐Gaw, Laurel J., Schwartz, Benjamin D., Wisemandle, Wayne, Mekki, Qais A.
Published in Arthritis and rheumatism (01.12.2003)
Published in Arthritis and rheumatism (01.12.2003)
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Tacrolimus in rheumatoid arthritis patients receiving concomitant methotrexate: A six-month, open-label study
KREMER, Joel M, HABROS, Joseph S, KOLBA, Karen S, KAINE, Jeffrey L, BORTON, Mary Ann, MENGLE-GAW, Laurel J, SCHWARTZ, Benjamin D, WISEMANDLE, Wayne, MEKKI, Qais A
Published in Arthritis and rheumatism (01.10.2003)
Published in Arthritis and rheumatism (01.10.2003)
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Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A 30-Month Nonrandomized Controlled Open-Label Extension Trial
Mah, Jean K, Clemens, Paula R, Guglieri, Michela, Smith, Edward C, Finkel, Richard S, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M, Webster, Richard, Castro, Diana, Kuntz, Nancy L, McDonald, Craig M, Damsker, Jesse M, Schwartz, Benjamin D, Mengle-Gaw, Laurel J, Jackowski, Stefan, Stimpson, Georgia, Ridout, Deborah A, Ayyar-Gupta, Vandana, Baranello, Giovanni, Manzur, Adnan Y, Muntoni, Francesco, Gordish-Dressman, Heather, Leinonen, Mika, Ward, Leanne M, Hoffman, Eric P, Dang, Utkarsh J
Published in JAMA network open (04.01.2022)
Published in JAMA network open (04.01.2022)
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Collagen-induced arthritis in the BB rat. Prevention of disease by treatment with CTLA-4-Ig
Knoerzer, D B, Karr, R W, Schwartz, B D, Mengle-Gaw, L J
Published in The Journal of clinical investigation (01.08.1995)
Published in The Journal of clinical investigation (01.08.1995)
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Tacrolimus in rheumatoid arthritis patients receiving concomitant methotrexate
Kremer, Joel M., Habros, Joseph S., Kolba, Karen S., Kaine, Jeffrey L., Borton, Mary Ann, Mengle‐Gaw, Laurel J., Schwartz, Benjamin D., Wisemandle, Wayne, Mekki, for the Tacrolimus‐Methotrexate Rheumatoid Arthritis Study Group, Qais A.
Published in Arthritis and rheumatism (01.10.2003)
Published in Arthritis and rheumatism (01.10.2003)
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METHODS OF CONVERTING A PATIENT'S TREATMENT REGIMEN FROM INTRAVENOUS ADMINISTRATION OF AN OPIOID TO ORAL CO-ADMINISTRATION OF MORPHINE AND OXYCODINE USING A DOSING ALGORITHM TO PROVIDE ANALGESIA
RICHARDS PATRICIA T, SCHWARTZ BENJAMIN D, MENGLE-GAW LAUREL J, STERN WARREN C
Year of Publication 28.05.2014
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Year of Publication 28.05.2014
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METHODS OF CONVERTING A PATIENT'S TREATMENT REGIMEN FROM INTRAVENOUS ADMINISTRATION OF AN OPIOID TO ORAL CO-ADMINISTRATION OF MORPHINE AND OXYCODONE USING A DOSING ALGORITHM TO PROVIDE ANALGESIA
MENGLE-GAW, LAUREL, J, SCHWARTZ, BENJAMIN, D, RICHARDS, PATRICIA, T, STERN, WARREN, C
Year of Publication 24.07.2013
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Year of Publication 24.07.2013
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Methods of converting a patient's treatment regimen from intravenous administration of an opioid to oral co-administration of morphine and oxycodone using a dosing algorithm to provide analgesia
RICHARDS, PATRICIA T, SCHWARTZ, BENJAMIN D, MENGLE-GAW, LAUREL J, STERN, WARREN C
Year of Publication 02.05.2013
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Year of Publication 02.05.2013
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Methods of converting a patient's treatment regimen from intravenous administration of an opioid to oral co-administration of morphine and oxycodone using a dosing algorithm to provide analgesia
RICHARDS PATRICIA T, SCHWARTZ BENJAMIN, MENGLE-GAW LAUREL J, STERN WARREN C
Year of Publication 17.07.2012
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Year of Publication 17.07.2012
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Methods of converting a patient's treatment regimen from intravenous administration of an opioid to oral co-administration of morphine and oxycodone using a dosing algorithm to provide analgesia
Richards, Patricia T, Stern, Warren C, Mengle-Gaw, Laurel J, Schwartz, Benjamin
Year of Publication 17.07.2012
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Year of Publication 17.07.2012
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METHODS OF CONVERTING A PATIENT'S TREATMENT REGIMEN FROM INTRAVENOUS ADMINISTRATION OF AN OPIOID TO ORAL CO-ADMINISTRATION OF MORPHINE AND OXYCODONE USING A DOSING ALGORITHM TO PROVIDE ANALGESIA
RICHARDS, PATRICIA T, SCHWARTZ, BENJAMIN D, MENGLE-GAW, LAUREL J, STERN, WARREN C
Year of Publication 22.03.2012
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Year of Publication 22.03.2012
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METHODS OF CONVERTING A PATIENT'S TREATMENT REGIMEN FROM INTRAVENOUS ADMINISTRATION OF AN OPIOID TO ORAL CO-ADMINISTRATION OF MORPHINE AND OXYCODONE USING A DOSING ALGORITHM TO PROVIDE ANALGESIA
MENGLE-GAW, LAUREL, J, SCHWARTZ, BENJAMIN, D, RICHARDS, PATRICIA, T, STERN, WARREN, C
Year of Publication 22.03.2012
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Year of Publication 22.03.2012
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Methods of Converting a Patient's Treatment Regimen from Intravenous Administration of an Opioid to Oral Co-Administration of Morphine and Oxycodone Using a Dosing Algorithm to Provide Analgesia
RICHARDS PATRICIA T, SCHWARTZ BENJAMIN, MENGLE-GAW LAUREL J, STERN WARREN C
Year of Publication 16.02.2012
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Year of Publication 16.02.2012
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