THE 6-minute walk test and other endpoints in Duchenne muscular dystrophy: Longitudinal natural history observations over 48 weeks from a multicenter study
Mcdonald, Craig M., Henricson, Erik K., Abresch, R. Ted, Florence, Julaine M., Eagle, Michelle, Gappmaier, Eduard, Glanzman, Allan M., Spiegel, Robert, Barth, Jay, Elfring, Gary, Reha, Allen, Peltz, Stuart
Published in Muscle & nerve (01.09.2013)
Published in Muscle & nerve (01.09.2013)
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Journal Article
The 6-minute walk test and other clinical endpoints in duchenne muscular dystrophy: Reliability, concurrent validity, and minimal clinically important differences from a multicenter study
McDonald, Craig M., Henricson, Erik K., Abresch, R. Ted, Florence, Julaine, Eagle, Michelle, Gappmaier, Eduard, Glanzman, Allan M., Spiegel, Robert, Barth, Jay, Elfring, Gary, Reha, Allen, Peltz, Stuart W.
Published in Muscle & nerve (01.09.2013)
Published in Muscle & nerve (01.09.2013)
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Journal Article
Genetic modifiers of ambulation in the cooperative international Neuromuscular research group Duchenne natural history study
Bello, Luca, Kesari, Akanchha, Gordish-Dressman, Heather, Cnaan, Avital, Morgenroth, Lauren P., Punetha, Jaya, Duong, Tina, Henricson, Erik K., Pegoraro, Elena, McDonald, Craig M., Hoffman, Eric P.
Published in Annals of neurology (01.04.2015)
Published in Annals of neurology (01.04.2015)
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Journal Article
Efficacy of idebenone on respiratory function in patients with Duchenne muscular dystrophy not using glucocorticoids (DELOS): a double-blind randomised placebo-controlled phase 3 trial
Buyse, Gunnar M, Prof, Voit, Thomas, Prof, Schara, Ulrike, Prof, Straathof, Chiara S M, MD, D'Angelo, M Grazia, MD, Bernert, Günther, MD, Cuisset, Jean-Marie, MD, Finkel, Richard S, Prof, Goemans, Nathalie, MD, McDonald, Craig M, Prof, Rummey, Christian, PhD, Meier, Thomas, PhD
Published in The Lancet (British edition) (02.05.2015)
Published in The Lancet (British edition) (02.05.2015)
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Journal Article
The 6-minute walk test as a new outcome measure in Duchenne muscular dystrophy
McDonald, Craig M., Henricson, Erik K., Han, Jay J., Abresch, R. Ted, Nicorici, Alina, Elfring, Gary L., Atkinson, Leone, Reha, Allen, Hirawat, Samit, Miller, Langdon L.
Published in Muscle & nerve (01.04.2010)
Published in Muscle & nerve (01.04.2010)
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Journal Article
Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials
McDonald, Craig M, Signorovitch, James, Mercuri, Eugenio, Niks, Erik H, Wong, Brenda, Fillbrunn, Mirko, Sajeev, Gautam, Yim, Erica, Dieye, Ibrahima, Miller, Debra, Ward, Susan J, Goemans, Nathalie
Published in PloS one (03.06.2024)
Published in PloS one (03.06.2024)
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Journal Article
Gait Characterization in Duchenne Muscular Dystrophy (DMD) Using a Single-Sensor Accelerometer: Classical Machine Learning and Deep Learning Approaches
Ramli, Albara Ah, Liu, Xin, Berndt, Kelly, Goude, Erica, Hou, Jiahui, Kaethler, Lynea B, Liu, Rex, Lopez, Amanda, Nicorici, Alina, Owens, Corey, Rodriguez, David, Wang, Jane, Zhang, Huanle, Aranki, Daniel, McDonald, Craig M, Henricson, Erik K
Published in Sensors (Basel, Switzerland) (01.02.2024)
Published in Sensors (Basel, Switzerland) (01.02.2024)
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Journal Article
Mexiletine for muscle cramps in amyotrophic lateral sclerosis: A randomized, double‐blind crossover trial
Oskarsson, Björn, Moore, Dan, Mozaffar, Tahseen, Ravits, John, Wiedau‐Pazos, Martina, Parziale, Nicholas, Joyce, Nanette C., Mandeville, Ross, Goyal, Namita, Cudkowicz, Merit E., Weiss, Michael, Miller, Robert G., McDonald, Craig M.
Published in Muscle & nerve (01.07.2018)
Published in Muscle & nerve (01.07.2018)
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Journal Article
Gait Event Detection and Travel Distance Using Waist-Worn Accelerometers across a Range of Speeds: Automated Approach
Ramli, Albara Ah, Liu, Xin, Berndt, Kelly, Chuah, Chen-Nee, Goude, Erica, Kaethler, Lynea B, Lopez, Amanda, Nicorici, Alina, Owens, Corey, Rodriguez, David, Wang, Jane, Aranki, Daniel, McDonald, Craig M, Henricson, Erik K
Published in Sensors (Basel, Switzerland) (09.02.2024)
Published in Sensors (Basel, Switzerland) (09.02.2024)
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Journal Article
Randomized phase 2 trial and open-label extension of domagrozumab in Duchenne muscular dystrophy
Wagner, Kathryn R., Abdel-Hamid, Hoda Z., Mah, Jean K., Campbell, Craig, Guglieri, Michela, Muntoni, Francesco, Takeshima, Yasuhiro, McDonald, Craig M., Kostera-Pruszczyk, Anna, Karachunski, Peter, Butterfield, Russell J., Mercuri, Eugenio, Fiorillo, Chiara, Bertini, Enrico S., Tian, Cuixia, Statland, Jeffery, Sadosky, Alesia B., Purohit, Vivek S., Sherlock, Sarah P., Palmer, Jeffrey P., Binks, Michael, Charnas, Lawrence, Marraffino, Shannon, Wong, Brenda L.
Published in Neuromuscular disorders : NMD (01.06.2020)
Published in Neuromuscular disorders : NMD (01.06.2020)
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Journal Article
Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD): Observations from a phase 2 trial
Muntoni, Francesco, Guglieri, Michela, Mah, Jean K., Wagner, Kathryn R., Brandsema, John F., Butterfield, Russell J., McDonald, Craig M., Mayhew, Anna G., Palmer, Jeffrey P., Marraffino, Shannon, Charnas, Lawrence, Mercuri, Eugenio
Published in PloS one (23.08.2022)
Published in PloS one (23.08.2022)
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Journal Article
First Regulatory Qualification of a Novel Digital Endpoint in Duchenne Muscular Dystrophy: A Multi-Stakeholder Perspective on the Impact for Patients and for Drug Development in Neuromuscular Diseases
Servais, Laurent, Camino, Eric, Clement, Aude, McDonald, Craig M., Lukawy, Jacek, Lowes, Linda P., Eggenspieler, Damien, Cerreta, Francesca, Strijbos, Paul
Published in Digital biomarkers (01.05.2021)
Published in Digital biomarkers (01.05.2021)
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Journal Article
Web Resource
Sleep Disordered Breathing in Children with Neuromuscular Disease
Chidambaram, Ambika G, Jhawar, Sanjay, McDonald, Craig M, Nandalike, Kiran
Published in Children (Basel) (01.10.2023)
Published in Children (Basel) (01.10.2023)
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Journal Article
Medical management of muscle weakness in Duchenne muscular dystrophy
Rivera, Sarah R, Jhamb, Sumit K, Abdel-Hamid, Hoda Z, Acsadi, Gyula, Brandsema, John, Ciafaloni, Emma, Darras, Basil T, Iannaccone, Susan T, Konersman, Chamindra G, Kuntz, Nancy L, McDonald, Craig M, Parsons, Julie A, Tesi Rocha, Carolina, Zaidman, Craig M, Butterfield, Russell J, Connolly, Anne M, Mathews, Katherine D
Published in PloS one (19.10.2020)
Published in PloS one (19.10.2020)
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Journal Article
Expression of SRP-9001 dystrophin and stabilization of motor function up to 2 years post-treatment with delandistrogene moxeparvovec gene therapy in individuals with Duchenne muscular dystrophy
Mendell, Jerry R, Shieh, Perry B, McDonald, Craig M, Sahenk, Zarife, Lehman, Kelly J, Lowes, Linda P, Reash, Natalie F, Iammarino, Megan A, Alfano, Lindsay N, Sabo, Brenna, Woods, Jeremy D, Skura, Christy L, Mao, Howard C, Staudt, Loretta A, Griffin, Danielle A, Lewis, Sarah, Wang, Shufang, Potter, Rachael A, Singh, Teji, Rodino-Klapac, Louise R
Published in Frontiers in cell and developmental biology (11.07.2023)
Published in Frontiers in cell and developmental biology (11.07.2023)
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Journal Article
Feasibility and Reproducibility of Echocardiographic Measures in Children with Muscular Dystrophies
Spurney, Christopher F., MD, McCaffrey, Francis M., MD, Cnaan, Avital, PhD, Morgenroth, Lauren P., MS, Ghelani, Sunil J., MD, Gordish-Dressman, Heather, MD, PhD, Arrieta, Adrienne, MS, Connolly, Anne M., MD, Lotze, Timothy E., MD, McDonald, Craig M., MD, Leshner, Robert T., MD, Clemens, Paula R., MD
Published in Journal of the American Society of Echocardiography (01.08.2015)
Published in Journal of the American Society of Echocardiography (01.08.2015)
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