Diagnosis of Cystic Fibrosis: Consensus Guidelines from the Cystic Fibrosis Foundation
Farrell, Philip M., MD, PhD, White, Terry B., PhD, Ren, Clement L., MD, Hempstead, Sarah E., MS, Accurso, Frank, MD, Derichs, Nico, MD, Howenstine, Michelle, MD, McColley, Susanna A., MD, Rock, Michael, MD, Rosenfeld, Margaret, MD, MPH, Sermet-Gaudelus, Isabelle, MD, PhD, Southern, Kevin W., MBChB, PhD, Marshall, Bruce C., MD, Sosnay, Patrick R., MD
Published in The Journal of pediatrics (01.02.2017)
Published in The Journal of pediatrics (01.02.2017)
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Journal Article
Clinical Significance of Microbial Infection and Adaptation in Cystic Fibrosis
Hauser, Alan R, Jain, Manu, Bar-Meir, Maskit, McColley, Susanna A
Published in Clinical Microbiology Reviews (01.01.2011)
Published in Clinical Microbiology Reviews (01.01.2011)
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A Phase 3 Open-Label Study of Elexacaftor/Tezacaftor/Ivacaftor in Children 6 through 11 Years of Age with Cystic Fibrosis and at Least One F508del Allele
Zemanick, Edith T, Taylor-Cousar, Jennifer L, Davies, Jane, Gibson, Ronald L, Mall, Marcus A, McKone, Edward F, McNally, Paul, Ramsey, Bonnie W, Rayment, Jonathan H, Rowe, Steven M, Tullis, Elizabeth, Ahluwalia, Neil, Chu, Chenghao, Ho, Thang, Moskowitz, Samuel M, Noel, Sabrina, Tian, Simon, Waltz, David, Weinstock, Tanya G, Xuan, Fengjuan, Wainwright, Claire E, McColley, Susanna A
Published in American journal of respiratory and critical care medicine (15.06.2021)
Published in American journal of respiratory and critical care medicine (15.06.2021)
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A CFTR corrector (lumacaftor) and a CFTR potentiator (ivacaftor) for treatment of patients with cystic fibrosis who have a phe508del CFTR mutation: a phase 2 randomised controlled trial
Boyle, Michael P, Bell, Scott C, Konstan, Michael W, McColley, Susanna A, Rowe, Steven M, Rietschel, Ernst, Huang, Xiaohong, Waltz, David, Patel, Naimish R, Rodman, David
Published in The lancet respiratory medicine (01.07.2014)
Published in The lancet respiratory medicine (01.07.2014)
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Airway microbiota across age and disease spectrum in cystic fibrosis
Zemanick, Edith T, Wagner, Brandie D, Robertson, Charles E, Ahrens, Richard C, Chmiel, James F, Clancy, John P, Gibson, Ronald L, Harris, William T, Kurland, Geoffrey, Laguna, Theresa A, McColley, Susanna A, McCoy, Karen, Retsch-Bogart, George, Sobush, Kurtis T, Zeitlin, Pamela L, Stevens, Mark J, Accurso, Frank J, Sagel, Scott D, Harris, J Kirk
Published in The European respiratory journal (01.11.2017)
Published in The European respiratory journal (01.11.2017)
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Efficacy and safety of ivacaftor in patients with cystic fibrosis who have an Arg117His-CFTR mutation: a double-blind, randomised controlled trial
Moss, Richard B, Flume, Patrick A, Elborn, J Stuart, Cooke, Jon, Rowe, Steven M, McColley, Susanna A, Rubenstein, Ronald C, Higgins, Mark
Published in The lancet respiratory medicine (01.07.2015)
Published in The lancet respiratory medicine (01.07.2015)
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Journal Article
Lumacaftor–Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508del CFTR
Wainwright, Claire E, Elborn, J. Stuart, Ramsey, Bonnie W, Marigowda, Gautham, Huang, Xiaohong, Cipolli, Marco, Colombo, Carla, Davies, Jane C, De Boeck, Kris, Flume, Patrick A, Konstan, Michael W, McColley, Susanna A, McCoy, Karen, McKone, Edward F, Munck, Anne, Ratjen, Felix, Rowe, Steven M, Waltz, David, Boyle, Michael P
Published in The New England journal of medicine (16.07.2015)
Published in The New England journal of medicine (16.07.2015)
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Phase 3 Open-Label Clinical Trial of Elexacaftor/Tezacaftor/Ivacaftor in Children Aged 2-5 Years with Cystic Fibrosis and at Least One F508del Allele
Goralski, Jennifer L, Hoppe, Jordana E, Mall, Marcus A, McColley, Susanna A, McKone, Edward, Ramsey, Bonnie, Rayment, Jonathan H, Robinson, Phil, Stehling, Florian, Taylor-Cousar, Jennifer L, Tullis, Elizabeth, Ahluwalia, Neil, Chin, Anna, Chu, Chenghao, Lu, Mengdi, Niu, Tao, Weinstock, Tanya, Ratjen, Felix, Rosenfeld, Margaret
Published in American journal of respiratory and critical care medicine (01.07.2023)
Published in American journal of respiratory and critical care medicine (01.07.2023)
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Journal Article
Soft, skin-interfaced sweat stickers for cystic fibrosis diagnosis and management
Ray, Tyler R, Ivanovic, Maja, Curtis, Paul M, Franklin, Daniel, Guventurk, Kerem, Jeang, William J, Chafetz, Joseph, Gaertner, Hannah, Young, Grace, Rebollo, Steve, Model, Jeffrey B, Lee, Stephen P, Ciraldo, John, Reeder, Jonathan T, Hourlier-Fargette, Aurélie, Bandodkar, Amay J, Choi, Jungil, Aranyosi, Alexander J, Ghaffari, Roozbeh, McColley, Susanna A, Haymond, Shannon, Rogers, John A
Published in Science translational medicine (31.03.2021)
Published in Science translational medicine (31.03.2021)
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Detection of disease‐causing CFTR variants in state newborn screening programs
McGarry, Meghan E., Ren, Clement L., Wu, Runyu, Farrell, Philip M., McColley, Susanna A.
Published in Pediatric pulmonology (01.02.2023)
Published in Pediatric pulmonology (01.02.2023)
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Journal Article
Minorities Are Underrepresented in Clinical Trials of Pharmaceutical Agents for Cystic Fibrosis
McGarry, Meghan E, McColley, Susanna A
Published in Annals of the American Thoracic Society (01.10.2016)
Published in Annals of the American Thoracic Society (01.10.2016)
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