Antisense oligonucleotide-induced exon skipping restores dystrophin expression in vitro in a canine model of DMD
MCCLOREY, G, MOULTON, H. M, IVERSEN, P. L, FLETCHER, S, WILTON, S. D
Published in Gene therapy (01.10.2006)
Published in Gene therapy (01.10.2006)
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Cell-penetrating peptide-morpholino conjugates alter pre-mRNA splicing of DMD (Duchenne muscular dystrophy) and inhibit murine coronavirus replication in vivo
Moulton, H M, Fletcher, S, Neuman, B W, McClorey, G, Stein, D A, Abes, S, Wilton, S D, Buchmeier, M J, Lebleu, B, Iversen, P L
Published in Biochemical Society transactions (01.08.2007)
Published in Biochemical Society transactions (01.08.2007)
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WVE-210201, an investigational stereopure oligonucleotide therapy for Duchenne muscular dystrophy, induces Exon 51 skipping and dystrophin protein restoration
Wood, M., Zhang, J., Bowman, K., Butler, D., Rinaldi, C., McClorey, G., Frank-Kamenetsky, M., Iwamoto, N., Kothari, N., Lu, G., Mathieu, S., Meena, M., Menon, S., Shimizu, M., Standley, S., Yang, H., Zhong, Z., Francis, C., Vargeese, C.
Published in Neuromuscular disorders : NMD (01.10.2017)
Published in Neuromuscular disorders : NMD (01.10.2017)
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Journal Article
P1 Peptide-conjugated phosphodiamidate morpholino treatment in mdx mice: cardiac dystrophin restoration and function
Blain, A, Greally, E, McCLorey, G, Godfrey, C, Laval, S.H, Gait, M, Wood, M, MacGowan, G, Straub, V
Published in Neuromuscular disorders : NMD (01.03.2014)
Published in Neuromuscular disorders : NMD (01.03.2014)
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Journal Article
The physiological consequences of different levels of dystrophin following antisense based exon-skipping in the mdx mouse
Muses, S, Godfrey, C, McClorey, G, Wells, K, Coursindel, T, Terry, R, Betts, C, Cappellari, O, Hammond, S, O'Donovan, E, Hildyard, J, El Andaloussi, S, Gait, M, Wood, M, Wells, D
Published in NEUROMUSCULAR DISORDERS (2015)
Published in NEUROMUSCULAR DISORDERS (2015)
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Conference Proceeding
P4.58 Antisense oligonucleotide correction of splice error in cultured ISCU myopathy muscle cells
Sanaker, P.S, Toompuu, M, McClorey, G, Bindoff, L.A
Published in Neuromuscular disorders : NMD (01.10.2010)
Published in Neuromuscular disorders : NMD (01.10.2010)
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Journal Article
Induced dystrophin exon skipping in human muscle explants
McClorey, G., Fall, A.M., Moulton, H.M., Iversen, P.L., Rasko, J.E., Ryan, M., Fletcher, S., Wilton, S.D.
Published in Neuromuscular disorders : NMD (01.10.2006)
Published in Neuromuscular disorders : NMD (01.10.2006)
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P04 Advancing the potential of peptide-PMO compounds in exon skipping therapy for DMD
Godfrey, C, McClorey, G, Coursindel, T, Betts, C, Hammond, S, El Andaloussi, S, Gait, M, Wood, M
Published in Neuromuscular disorders : NMD (01.03.2012)
Published in Neuromuscular disorders : NMD (01.03.2012)
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How much dystrophin is enough: the physiological consequences of different levels of dystrophin in the mdx mouse
Godfrey, Caroline, Muses, Sofia, McClorey, Graham, Wells, Kim E, Coursindel, Thibault, Terry, Rebecca L, Betts, Corinne, Hammond, Suzan, O'Donovan, Liz, Hildyard, John, El Andaloussi, Samir, Gait, Michael J, Wood, Matthew J, Wells, Dominic J
Published in Human molecular genetics (01.08.2015)
Published in Human molecular genetics (01.08.2015)
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Engineered extracellular vesicle decoy receptor-mediated modulation of the IL6 trans-signalling pathway in muscle
Conceição, Mariana, Forcina, Laura, Wiklander, Oscar P.B., Gupta, Dhanu, Nordin, Joel Z., Vrellaku, Besarte, McClorey, Graham, Mäger, Imre, Gӧrgens, André, Lundin, Per, Musarò, Antonio, Wood, Matthew J.A., Andaloussi, Samir EL, Roberts, Thomas C.
Published in Biomaterials (01.01.2021)
Published in Biomaterials (01.01.2021)
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P7 Profile of circadianly regulated metabolic genes in dystrophic heart
Betts, CA, van Westering, TLE, Bowerman, M, McClorey, G, Meijboom, K, Wood, MJA
Published in Heart (British Cardiac Society) (01.03.2018)
Published in Heart (British Cardiac Society) (01.03.2018)
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Journal Article
Self-Assembly into Nanoparticles Is Essential for Receptor Mediated Uptake of Therapeutic Antisense Oligonucleotides
Ezzat, Kariem, Aoki, Yoshitsugu, Koo, Taeyoung, McClorey, Graham, Benner, Leif, Coenen-Stass, Anna, O’Donovan, Liz, Lehto, Taavi, Garcia-Guerra, Antonio, Nordin, Joel, Saleh, Amer F, Behlke, Mark, Morris, John, Goyenvalle, Aurelie, Dugovic, Branislav, Leumann, Christian, Gordon, Siamon, Gait, Michael J, El−Andaloussi, Samir, Wood, Matthew JA
Published in Nano letters (08.07.2015)
Published in Nano letters (08.07.2015)
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Journal Article
P.193 Phosphoryl guanidine-containing backbone modifications enhance exon skipping, dystrophin restoration and survival in a severe mouse model for DMD
Hu, X., Kandasamy, P., McClorey, G., Shimizu, M., Kothari, N., Iwamoto, N., Byrne, M., Liu, F., Longo, K., Oieni, J., Shivalila, C., Rinaldi, C., Yang, H., Wood, M., Vargeese, C.
Published in Neuromuscular disorders : NMD (01.10.2022)
Published in Neuromuscular disorders : NMD (01.10.2022)
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Journal Article
D43 - Profile of circadianly regulated metabolic genes in dystrophic heart
Betts, C.A., van Westering, T.L.E., Bowerman, M., McClorey, G., Meijboom, K., Wood, M.J.A.
Published in Neuromuscular disorders : NMD (01.04.2018)
Published in Neuromuscular disorders : NMD (01.04.2018)
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Journal Article
Profile of circadianly regulated metabolic genes in dystrophic heart
Betts, C.A., van Westering, T.L.E., Bowerman, M., McClorey, G., Meijboom, K., Wood, M.J.A.
Published in Neuromuscular disorders : NMD (01.04.2018)
Published in Neuromuscular disorders : NMD (01.04.2018)
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Journal Article
Multi-level omics analysis in a murine model of dystrophin loss and therapeutic restoration
Roberts, Thomas C, Johansson, Henrik J, McClorey, Graham, Godfrey, Caroline, Blomberg, K Emelie M, Coursindel, Thibault, Gait, Michael J, Smith, C I Edvard, Lehtiö, Janne, El Andaloussi, Samir, Wood, Matthew J A
Published in Human molecular genetics (01.12.2015)
Published in Human molecular genetics (01.12.2015)
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Journal Article
Preclinical studies of WVE-210201, an investigational stereopure antisense oligonucleotide in development for the treatment of patients with duchenne muscular dystrophy (DMD)
Panzara, M., Zhang, J., Rinaldi, C., McClorey, G., Bowman, K., Butler, D., Dodart, J., Frank-Kamenetsky, M., Iwamoto, N., Kothari, N., Lu, G., Mathieu, S., M, M., Melkonian, M., Menon, S., Standley, S., Yang, H., Zhong, Z., Wood, M., Vargeese, C.
Published in Journal of the neurological sciences (15.10.2017)
Published in Journal of the neurological sciences (15.10.2017)
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P.402 - WVE-210201, an investigational stereopure oligonucleotide therapy for Duchenne muscular dystrophy, induces Exon 51 skipping and dystrophin protein restoration
Wood, M., Zhang, J., Bowman, K., Butler, D., Rinaldi, C., McClorey, G., Frank-Kamenetsky, M., Iwamoto, N., Kothari, N., Lu, G., Mathieu, S., Meena, M., Menon, S., Shimizu, M., Standley, S., Yang, H., Zhong, Z., Francis, C., Vargeese, C.
Published in Neuromuscular disorders : NMD (01.10.2017)
Published in Neuromuscular disorders : NMD (01.10.2017)
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DMD CLINICAL THERAPIES II: P.127Identification of potent, muscle-targeting investigational stereo-pure oligonucleotides for exon 53 DMD therapy
Durbin, A., Shivalila, C., Kothari, N., Rinaldi, C., McClorey, G., Antonijevic, I., Byrne, M., Davis II, J., Guo, L., Iwamoto, N., Liu, F., Longo, K., Lu, G., Nadella, P., Purcell-Estabrook, E., Standley, S., Zhong, Z., Zhang, J., Wood, M., Vargeese, C.
Published in Neuromuscular disorders : NMD (01.10.2018)
Published in Neuromuscular disorders : NMD (01.10.2018)
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