Reliability of the North Star Ambulatory Assessment in a multicentric setting
Mazzone, E.S, Messina, S, Vasco, G, Main, M, Eagle, M, D’Amico, A, Doglio, L, Politano, L, Cavallaro, F, Frosini, S, Bello, L, Magri, F, Corlatti, A, Zucchini, E, Brancalion, B, Rossi, F, Ferretti, M, Motta, M.G, Cecio, M.R, Berardinelli, A, Alfieri, P, Mongini, T, Pini, A, Astrea, G, Battini, R, Comi, G, Pegoraro, E, Morandi, L, Pane, M, Angelini, C, Bruno, C, Villanova, M, Vita, G, Donati, M.A, Bertini, E, Mercuri, E
Published in Neuromuscular disorders : NMD (01.07.2009)
Published in Neuromuscular disorders : NMD (01.07.2009)
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Journal Article
Interim analysis of the phase 3 CHERISH study evaluating nusinersen in patients with later-onset spinal muscular atrophy (SMA): Primary and descriptive secondary endpoints
Mercuri, E, Finkel, R, Kirschner, J, Chiriboga, C.A, Kuntz, N, Darras, B, Shieh, P.B, Saito, K, De Vivo, D.C, Mazzone, E.S, Montes, J, Yang, Q, Zhong, Z.J, Gheuens, S, Bennett, C.F, Schneider, E, Farwell, W
Published in European journal of paediatric neurology (01.06.2017)
Published in European journal of paediatric neurology (01.06.2017)
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Journal Article
T.P.11
Pane, M, Mazzone, E.S, Fanelli, L, Sanctis, R. De, Palermo, C, Sivo, S, D’Amico, A, Messina, S, Politano, L, Battini, E, Pedemonte, M, Pegoraro, E, Berardinelli, A.L, D’Angelo, G, Pini, A, Baranello, G, Mercuri, E
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
T.P.37
Mazzone, E.S, Mayhew, A, Main, M, Montes, J, Ramsey, D, Scoto, M, Pane, M, Bushby, K, Finkel, R, Muntoni, F, Mercuri, E
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
T.P.4
Mazzone, E.S, Pane, M, Sivo, S, Palermo, C, Sormani, M.P, Messina, S, D’Amico, A, Vita, G.L, Fanelli, L, Berardinelli, A, Donati, M.A, Baranello, G, Battini, R, Pegoraro, E, Politano, L, Bruno, C, Comi, G.P, Bertini, E, Mercuri, E
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
S.P.4 Functional changes in Duchenne muscular dystrophy: A 24 month longitudinal cohort study
Mazzone, E.S, Pane, M, Scalise, R, Sormani, M.P, Torrente, Y, Berardinelli, A, Messina, S, Cavallaro, F, Amico, A. D, Doglio, L, Bruno, C, Politano, L, Frosini, S, Battini, R, Bello, L, Pegoraro, E, Bonfiglio, S, Comi, G, Pini, A, de Sanctis, R, Bianco, F, Vasco, G, Mongini, T, Donati, M.A, Previtali, S, Napolitano, S, Vita, G, Bertini, E, Mercuri, E
Published in Neuromuscular disorders : NMD (01.10.2012)
Published in Neuromuscular disorders : NMD (01.10.2012)
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Journal Article
M.P.2.01 Reliability of the north star ambulatory assessment in a multicentric setting
Mazzone, E.S, Messina, S, Vasco, G, Main, M, Eagle, M, D’Amico, A, Bruno, C, Politano, L, Berardinelli, A, Mongini, T, Pini, A, Battini, R, Comi, G, Pegoraro, E, Morandi, L, Villanova, M, Vita, G, Bertini, E, Mercuri, E
Published in Neuromuscular disorders : NMD (01.09.2009)
Published in Neuromuscular disorders : NMD (01.09.2009)
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Journal Article
T.P.37: Old measures and new analysis in non ambulant SMA patients
Mazzone, E.S., Mayhew, A., Main, M., Montes, J., Ramsey, D., Scoto, M., Pane, M., Bushby, K., Finkel, R., Muntoni, F., Mercuri, E.
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
T.P.11: Longitudinal assessment of Upper Limb function in DMD patients: 12 month changes
Pane, M., Mazzone, E.S., Fanelli, L., Sanctis, R. De, Palermo, C., Sivo, S., D’Amico, A., Messina, S., Politano, L., Battini, E., Pedemonte, M., Pegoraro, E., Berardinelli, A.L., D’Angelo, G., Pini, A., Baranello, G., Mercuri, E.
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
T.P.4: Long term natural history data in ambulant boys with Duchenne muscular dystrophy: 36 month changes
Mazzone, E.S., Pane, M., Sivo, S., Palermo, C., Sormani, M.P., Messina, S., D’Amico, A., Vita, G.L., Fanelli, L., Berardinelli, A., Donati, M.A., Baranello, G., Battini, R., Pegoraro, E., Politano, L., Bruno, C., Comi, G.P., Bertini, E., Mercuri, E.
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
S.P.4 Functional changes in Duchenne muscular dystrophy: A 24month longitudinal cohort study
Mazzone, E.S., Pane, M., Scalise, R., Sormani, M.P., Torrente, Y., Berardinelli, A., Messina, S., Cavallaro, F., ′Amico, A. D, Doglio, L., Bruno, C., Politano, L., Frosini, S., Battini, R., Bello, L., Pegoraro, E., Bonfiglio, S., Comi, G., Pini, A., de Sanctis, R., Bianco, F., Vasco, G., Mongini, T., Donati, M.A., Previtali, S., Napolitano, S., Vita, G., Bertini, E., Mercuri, E.
Published in Neuromuscular disorders : NMD (01.10.2012)
Published in Neuromuscular disorders : NMD (01.10.2012)
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Journal Article