Development of a Modified Prognostic Index for Adult Patients with Acute Lymphoblastic Leukemia
Chapchap, Eduardo Cerello, Oliveira, Ana Luisa, Joaquim de Carvalho, Maria Eduarda Alonso, Morgades, Mireia, Mauad, Vitor AQ, Borducchi, Davimar Miranda Maciel, Santos, Fabio P. S., Ribera, Jordi, Kerbauy, Fabio R., Ribera, Josep-Maria, Hamerschlak, Nelson
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Oral Monotherapy with Iptacopan, a Proximal Complement Inhibitor of Factor B, Has Superior Efficacy to Intravenous Terminal Complement Inhibition with Standard of Care Eculizumab or Ravulizumab and Favorable Safety in Patients with Paroxysmal Nocturnal Hemoglobinuria and Residual Anemia: Results from the Randomized, Active-Comparator-Controlled, Open-Label, Multicenter, Phase III Apply-PNH Study
Peffault de Latour, Regis, Roeth, Alexander, Kulasekararaj, Austin, Scheinberg, Phillip, Ueda, Yasutaka, de Castro, Carlos M, Di Bona, Eros, Schrezenmeier, Hubert, Langemeijer, Saskia MC, Barcellini, Wilma, Tavitian, Suzanne, Panse, Jens, Schafhausen, Philippe, Mauad, Vitor AQ, Kerloeguen, Cecile, Levitch, Rafael, Kumar, Rakesh, Thorburn, Christine, Maitra, Samopriyo, Dahlke, Marion, Risitano, Antonio M
Published in Blood (06.12.2022)
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Published in Blood (06.12.2022)
Journal Article
Oral Monotherapy with Iptacopan, a Proximal Complement Inhibitor of Factor B, Has Superior Efficacy to Intravenous Terminal Complement Inhibition with Standard of Care Eculizumab or Ravulizumab and Favorable Safety in Patients with Paroxysmal Nocturnal Hemoglobinuria and Residual Anemia: Results from the Randomized, Active-Comparator-Controlled, Open-Label, Multicenter, Phase III Apply-PNH Study
Peffault de Latour, Regis, Roeth, Alexander, Kulasekararaj, Austin, Scheinberg, Phillip, Ueda, Yasutaka, de Castro, Carlos M, Di Bona, Eros, Schrezenmeier, Hubert, Langemeijer, Saskia MC, Barcellini, Wilma, Tavitian, Suzanne, Panse, Jens, Schafhausen, Philippe, Mauad, Vitor AQ, Kerloeguen, Cecile, Levitch, Rafael, Kumar, Rakesh, Thorburn, Christine, Maitra, Samopriyo, Dahlke, Marion, Risitano, Antonio M
Published in Blood (06.12.2022)
Published in Blood (06.12.2022)
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Factor B Inhibition with Oral Iptacopan Monotherapy Demonstrates Sustained Long-Term Efficacy and Safety in Anti-C5-Treated Patients (pts) with Paroxysmal Nocturnal Hemoglobinuria (PNH) and Persistent Anemia: Final 48-Week Results from the Multicenter, Phase III APPLY-PNH Trial
Risitano, Antonio M, Kulasekararaj, Austin, Roeth, Alexander, Scheinberg, Phillip, Ueda, Yasutaka, de Castro, Carlos, Di Bona, Eros, Griffin, Morag, Langemeijer, Saskia MC, Schrezenmeier, Hubert, Barcellini, Wilma, Mauad, Vitor AQ, Panse, Jens, Schafhausen, Philippe, Tavitian, Suzanne, Beggiato, Eloise, Gaya, Anna, Huang, Wei-Han, Kitawaki, Toshio, Kutlar, Abdullah, Maciejewski, Jaroslaw P., Notaro, Rosario, Pullarkat, Vinod, Schubert, Jörg, Terriou, Louis, Uchiyama, Michihiro, Sicre De Fontbrune, Flore, Frieri, Camilla, Alashkar, Ferras, Gandhi, Shreyans, Kumar, Rakesh, Thorburn, Christine, Maitra, Samopriyo, Solar-Yohay, Susan, Lawniczek, Tomasz, Dahlke, Marion, Peffault De Latour, Régis
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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POSTER: MDS-273 Oral Iptacopan Monotherapy Increases Paroxysmal Nocturnal Hemoglobinuria (PNH) Red Blood Cell Clone Size Via Control of Intra- and Extravascular Hemolysis in Anti-C5-Treated PNH Patients With Anemia
Risitano, Antonio M., Röth, Alexander, Kulasekararaj, Austin, Scheinberg, Phillip, Ueda, Yasutaka, de Castro, Carlos, Di Bona, Eros, Griffin, Morag, Langemeijer, Saskia MC, Schrezenmeier, Hubert, Barcellini, Wilma, Mauad, Vitor AQ, Panse, Jens, Schafhausen, Philippe, Tavitian, Suzanne, Beggiato, Eloise, Gaya, Anna, Huang, Wei-Han, Kitawaki, Toshio, Kutlar, Abdullah, Maciejewski, Jaroslaw, Notaro, Rosario, Pullarkat, Vinod, Schubert, Jörg, Terriou, Louis, Uchiyama, Michihiro, de Fontbrune, Flore Sicre, Marano, Luana, Alashkar, Ferras, Gandhi, Shreyans, Kerloeguen, Cécile, Kumar, Rakesh, Thorburn, Christine, Maitra, Samopriyo, Dahlke, Marion, de Latour, Régis Peffault
Published in Clinical lymphoma, myeloma and leukemia (01.09.2023)
Published in Clinical lymphoma, myeloma and leukemia (01.09.2023)
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Journal Article
MDS-273 Oral Iptacopan Monotherapy Increases Paroxysmal Nocturnal Hemoglobinuria (PNH) Red Blood Cell Clone Size Via Control of Intra- and Extravascular Hemolysis in Anti-C5-Treated PNH Patients With Anemia
Risitano, Antonio M., Röth, Alexander, Kulasekararaj, Austin, Scheinberg, Phillip, Ueda, Yasutaka, de Castro, Carlos, Di Bona, Eros, Griffin, Morag, Langemeijer, Saskia MC, Schrezenmeier, Hubert, Barcellini, Wilma, Mauad, Vitor AQ, Panse, Jens, Schafhausen, Philippe, Tavitian, Suzanne, Beggiato, Eloise, Gaya, Anna, Huang, Wei-Han, Kitawaki, Toshio, Kutlar, Abdullah, Maciejewski, Jaroslaw, Notaro, Rosario, Pullarkat, Vinod, Schubert, Jörg, Terriou, Louis, Uchiyama, Michihiro, de Fontbrune, Flore Sicre, Marano, Luana, Alashkar, Ferras, Gandhi, Shreyans, Kerloeguen, Cécile, Kumar, Rakesh, Thorburn, Christine, Maitra, Samopriyo, Dahlke, Marion, de Latour, Régis Peffault
Published in Clinical lymphoma, myeloma and leukemia (01.09.2023)
Published in Clinical lymphoma, myeloma and leukemia (01.09.2023)
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S182: ORAL IPTACOPAN MONOTHERAPY INCREASES PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH) RED BLOOD CELL CLONE SIZE VIA CONTROL OF INTRA‐ AND EXTRAVASCULAR HEMOLYSIS IN ANTI‐C5‐TREATED PNH PATIENTS WITH ANEMIA
Risitano, Antonio Maria, Röth, Alexander, Kulasekararaj, Austin, Scheinberg, Phillip, Ueda, Yasutaka, Castro, Carlos, Bona, Eros DI, Griffin, Morag, Langemeijer, Saskia, Schrezenmeier, Hubert, Barcellini, Wilma, Mauad, Vitor Aq, Panse, Jens, Schafhausen, Philippe, Tavitian, Suzanne, Beggiato, Eloise, Gaya, Anna, Huang, Wei‐Han, Kitawaki, Toshio, Kutlar, Abdullah, Maciejewski, Jaroslaw P, Notaro, Rosario, Pullarkat, Vinod, Schubert, Jörg, Terriou, Louis, Uchiyama, Michihiro, Fontbrune, Flore Sicre, Marano, Luana, Alashkar, Ferras, Gandhi, Shreyans, Kerloëguen, Cécile, Kumar, Rakesh, Thorburn, Christine, Maitra, Samopriyo, Dahlke, Marion, Latour, Régis Peffault
Published in HemaSphere (08.08.2023)
Published in HemaSphere (08.08.2023)
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Oral Iptacopan Monotherapy in Paroxysmal Nocturnal Hemoglobinuria
Peffault de Latour, Régis, Röth, Alexander, Kulasekararaj, Austin G., Han, Bing, Scheinberg, Phillip, Maciejewski, Jaroslaw P., Ueda, Yasutaka, de Castro, Carlos M., Di Bona, Eros, Fu, Rong, Zhang, Li, Griffin, Morag, Langemeijer, Saskia M.C., Panse, Jens, Schrezenmeier, Hubert, Barcellini, Wilma, Mauad, Vitor A.Q., Schafhausen, Philippe, Tavitian, Suzanne, Beggiato, Eloise, Chew, Lee Ping, Gaya, Anna, Huang, Wei-Han, Jang, Jun Ho, Kitawaki, Toshio, Kutlar, Abdullah, Notaro, Rosario, Pullarkat, Vinod, Schubert, Jörg, Terriou, Louis, Uchiyama, Michihiro, Wong Lee Lee, Lily, Yap, Eng-Soo, Sicre de Fontbrune, Flore, Marano, Luana, Alashkar, Ferras, Gandhi, Shreyans, Trikha, Roochi, Yang, Chen, Liu, Hui, Kelly, Richard J., Höchsmann, Britta, Kerloeguen, Cécile, Banerjee, Partha, Levitch, Rafael, Kumar, Rakesh, Wang, Zhixin, Thorburn, Christine, Maitra, Samopriyo, Li, Shujie, Verles, Aurelie, Dahlke, Marion, Risitano, Antonio M.
Published in The New England journal of medicine (14.03.2024)
Published in The New England journal of medicine (14.03.2024)
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