Modeling Glutaric Aciduria Type I in human neuroblastoma cells recapitulates neuronal damage that can be rescued by gene replacement
Mateu-Bosch, A., Segur-Bailach, E., García-Villoria, J., Gea-Sorlí, S., Ruiz, I., del Rey, J., Camps, J., Guitart-Mampel, M., Garrabou, G., Tort, F., Ribes, A., Fillat, C.
Published in Gene therapy (01.01.2024)
Published in Gene therapy (01.01.2024)
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