Complement System Response to Adeno-Associated Virus Vector Gene Therapy
Kropf, Elizabeth, Markusic, David M, Majowicz, Anna, Mingozzi, Federico, Kuranda, Klaudia
Published in Human gene therapy (01.07.2024)
Published in Human gene therapy (01.07.2024)
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Journal Article
Immune Response Mechanisms against AAV Vectors in Animal Models
Martino, Ashley T., Markusic, David M.
Published in Molecular therapy. Methods & clinical development (12.06.2020)
Published in Molecular therapy. Methods & clinical development (12.06.2020)
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Journal Article
Manipulating the microbiome to enhance oral tolerance in food allergy
Gonzalez-Visiedo, Miguel, Kulis, Michael D., Markusic, David M.
Published in Cellular immunology (01.12.2022)
Published in Cellular immunology (01.12.2022)
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Journal Article
Liver induced transgene tolerance with AAV vectors
Keeler, Geoffrey D., Markusic, David M., Hoffman, Brad E.
Published in Cellular immunology (01.08.2019)
Published in Cellular immunology (01.08.2019)
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Journal Article
Editorial: Immunogenicity and toxicity of AAV gene therapy
Bradbury, Allison, Markusic, David, Muhuri, Manish, Ou, Li
Published in Frontiers in immunology (22.06.2023)
Published in Frontiers in immunology (22.06.2023)
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Journal Article
Gene Therapy-Induced Antigen-Specific Tregs Inhibit Neuro-inflammation and Reverse Disease in a Mouse Model of Multiple Sclerosis
Keeler, Geoffrey D., Kumar, Sandeep, Palaschak, Brett, Silverberg, Emily L., Markusic, David M., Jones, Noah T., Hoffman, Brad E.
Published in Molecular therapy (03.01.2018)
Published in Molecular therapy (03.01.2018)
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Journal Article
Type I IFN Sensing by cDCs and CD4+ T Cell Help Are Both Requisite for Cross-Priming of AAV Capsid-Specific CD8+ T Cells
Shirley, Jamie L., Keeler, Geoffrey D., Sherman, Alexandra, Zolotukhin, Irene, Markusic, David M., Hoffman, Brad E., Morel, Laurence M., Wallet, Mark A., Terhorst, Cox, Herzog, Roland W.
Published in Molecular therapy (04.03.2020)
Published in Molecular therapy (04.03.2020)
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Journal Article
The genome of self-complementary adeno-associated viral vectors increases Toll-like receptor 9–dependent innate immune responses in the liver
Martino, Ashley T., Suzuki, Masataka, Markusic, David M., Zolotukhin, Irene, Ryals, Renee C., Moghimi, Babak, Ertl, Hildegund C.J., Muruve, Daniel A., Lee, Brendan, Herzog, Roland W.
Published in Blood (16.06.2011)
Published in Blood (16.06.2011)
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Journal Article
Transient B cell depletion or improved transgene expression by codon optimization promote tolerance to factor VIII in gene therapy
Sack, Brandon K, Merchant, Sherin, Markusic, David M, Nathwani, Amit C, Davidoff, Andrew M, Byrne, Barry J, Herzog, Roland W
Published in PloS one (24.05.2012)
Published in PloS one (24.05.2012)
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Journal Article
Synergy between rapamycin and FLT3 ligand enhances plasmacytoid dendritic cell–dependent induction of CD4+CD25+FoxP3+ Treg
Biswas, Moanaro, Sarkar, Debalina, Kumar, Sandeep R.P., Nayak, Sushrusha, Rogers, Geoffrey L., Markusic, David M., Liao, Gongxian, Terhorst, Cox, Herzog, Roland W.
Published in Blood (07.05.2015)
Published in Blood (07.05.2015)
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Journal Article
Immunology of Gene and Cell Therapy
Markusic, David M., Martino, Ashley T., Porada, Christopher D., VandenDriessche, Thierry
Published in Molecular therapy (04.03.2020)
Published in Molecular therapy (04.03.2020)
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Journal Article
Development of a Clinical Candidate AAV3 Vector for Gene Therapy of Hemophilia B
Brown, Harrison C, Doering, Christopher B, Herzog, Roland W, Ling, Chen, Markusic, David M, Spencer, H Trent, Srivastava, Alok, Srivastava, Arun
Published in Human gene therapy (01.10.2020)
Published in Human gene therapy (01.10.2020)
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Journal Article
Engineered AAV vector minimizes in vivo targeting of transduced hepatocytes by capsid-specific CD8+ T cells
Martino, Ashley T., Basner-Tschakarjan, Etiena, Markusic, David M., Finn, Jonathan D., Hinderer, Christian, Zhou, Shangzhen, Ostrov, David A., Srivastava, Arun, Ertl, Hildegund C.J., Terhorst, Cox, High, Katherine A., Mingozzi, Federico, Herzog, Roland W.
Published in Blood (21.03.2013)
Published in Blood (21.03.2013)
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Journal Article
Viral Vector Based Immunotherapy for Peanut Allergy
Gonzalez-Visiedo, Miguel, Herzog, Roland W, Munoz-Melero, Maite, Blessinger, Sophia A, Cook-Mills, Joan M, Daniell, Henry, Markusic, David M
Published in Viruses (01.07.2024)
Published in Viruses (01.07.2024)
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Journal Article
Effective gene therapy for haemophilic mice with pathogenic factor IX antibodies
Markusic, David M., Hoffman, Brad E., Perrin, George Q., Nayak, Sushrusha, Wang, Xiaomei, LoDuca, Paul A., High, Katherine A., Herzog, Roland W.
Published in EMBO molecular medicine (01.11.2013)
Published in EMBO molecular medicine (01.11.2013)
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