52 An open-label extension (EXT) study of lumacaftor/ivacaftor (LUM/IVA) therapy in patients (pts) aged 6–11 years (yrs) with cystic fibrosis (CF) homozygous for F508del-CFTR
Chilvers, M, Tian, S, Marigowda, G, Bsharat, M, Hug, C, Solomon, M, Black, P, Rosenfeld, M, Sawicki, G.S, Hoppe, J
Published in Journal of cystic fibrosis (01.06.2017)
Published in Journal of cystic fibrosis (01.06.2017)
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WS13.4 Efficacy and safety of lumacaftor/ivacaftor (LUM/IVA) in patients (pts) aged 6–11 years (yrs) with cystic fibrosis (CF) homozygous for F508del-CFTR : a randomized placebo (PBO)-controlled phase 3 trial
Ratjen, F, Tian, S, Marigowda, G, Hug, C, Huang, X, Stanojevic, S, Milla, C.E, Robinson, P, Waltz, D, Davies, J.C
Published in Journal of cystic fibrosis (01.06.2017)
Published in Journal of cystic fibrosis (01.06.2017)
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WS04.2 Improvement in inflammatory biomarkers in patients (pts) with cystic fibrosis (CF) homozygous for the F508del-CFTR mutation treated with lumacaftor (LUM) and ivacaftor (IVA)
Sullivan, J.C, Accurso, F.J, Marigowda, G, Beusmans, J, Geho, D, Zhang, E, Moss, R.B, Waltz, D
Published in Journal of cystic fibrosis (01.06.2016)
Published in Journal of cystic fibrosis (01.06.2016)
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55 Lumacaftor/ivacaftor (LUM/IVA) in patients (pts) with cystic fibrosis (CF) and advanced lung disease homozygous for F508del-CFTR : a 24-week open-label study
Taylor-Cousar, J, Jain, M, Barto, T.L, Haddad, T, Atkinson, J, Tian, S, Tang, R, Marigowda, G, Waltz, D, Pilewski, J
Published in Journal of cystic fibrosis (01.06.2017)
Published in Journal of cystic fibrosis (01.06.2017)
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WS01.3 Lumacaftor in combination with ivacaftor in patients with cystic fibrosis who are homozygous for the F508del-CFTR mutation
Elborn, J.S, Ramsey, B, Boyle, M.P, Wainwright, C, Konstan, M, Huang, X, Marigowda, G, Waltz, D
Published in Journal of cystic fibrosis (01.06.2015)
Published in Journal of cystic fibrosis (01.06.2015)
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143 Lumacaftor/ivacaftor combination therapy in CF patients homozygous for F508del-CFTR with severe lung dysfunction
Elborn, J.S, Ramsey, B, Boyle, M.P, Wainwright, C, Konstan, M, Huang, X, Marigowda, G, Waltz, D
Published in Journal of cystic fibrosis (01.06.2015)
Published in Journal of cystic fibrosis (01.06.2015)
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Elexacaftor–Tezacaftor–Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele
Middleton, Peter G, Mall, Marcus A, Dřevínek, Pavel, Lands, Larry C, McKone, Edward F, Polineni, Deepika, Ramsey, Bonnie W, Taylor-Cousar, Jennifer L, Tullis, Elizabeth, Vermeulen, François, Marigowda, Gautham, McKee, Charlotte M, Moskowitz, Samuel M, Nair, Nitin, Savage, Jessica, Simard, Christopher, Tian, Simon, Waltz, David, Xuan, Fengjuan, Rowe, Steven M, Jain, Raksha
Published in The New England journal of medicine (07.11.2019)
Published in The New England journal of medicine (07.11.2019)
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Lumacaftor–Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508del CFTR
Wainwright, Claire E, Elborn, J. Stuart, Ramsey, Bonnie W, Marigowda, Gautham, Huang, Xiaohong, Cipolli, Marco, Colombo, Carla, Davies, Jane C, De Boeck, Kris, Flume, Patrick A, Konstan, Michael W, McColley, Susanna A, McCoy, Karen, McKone, Edward F, Munck, Anne, Ratjen, Felix, Rowe, Steven M, Waltz, David, Boyle, Michael P
Published in The New England journal of medicine (16.07.2015)
Published in The New England journal of medicine (16.07.2015)
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S96 An open-label extension (ext) study of lumacaftor/ivacaftor (lum/iva) therapy in patients aged 6 to 11 years with cystic fibrosis (cf) homozygous for f508del-cftr
Chilvers, M, Tian, S, Marigowda, G, Bsharat, M, Hug, C, Solomon, M, Black, P, Rosenfeld, M, Sawicki, G, Hoppe, J
Published in Thorax (01.12.2017)
Published in Thorax (01.12.2017)
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S93 Effect of lumacaftor/ivacaftor on total, bronchiectasis, and air trapping computed tomography (ct) scores in children homozygous for f508del-cftr: exploratory imaging substudy
Brody, AS, Nagle, S, Hug, C, Marigowda, G, Waltz, D, Goldin, J, Ratjen, F, Wang, L
Published in Thorax (01.12.2017)
Published in Thorax (01.12.2017)
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WS01.5 A 2-part, phase 3 single-arm study to evaluate the safety and pharmacokinetics (PK) of lumacaftor/ivacaftor (LUM/IVA) combination therapy in patients (pts) aged 2 to 5 years with cystic fibrosis (CF) homozygous for the F508del-CFTR mutation
Mcnamara, J., Mccolley, S.A., Owen, C.A., Liu, F., Tian, S., Waltz, D., Marigowda, G., Sawicki, G.S.
Published in Journal of cystic fibrosis (01.06.2018)
Published in Journal of cystic fibrosis (01.06.2018)
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P254 Feasibility of ultrashort echo time (ute) mri to evaluate the effect of lumacaftor/ivacaftor therapy in children with cystic fibrosis (cf) homozygous for f508del
Nagle, S, Brody, AS, Woods, J, Johnson, KM, Wang, L, Marigowda, G, Waltz, D, Goldin, J, Ratjen, F, Hug, C
Published in Thorax (01.12.2017)
Published in Thorax (01.12.2017)
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Journal Article
Diminished Lipoxin Biosynthesis in Severe Asthma
Levy, Bruce D, Bonnans, Caroline, Silverman, Eric S, Palmer, Lyle J, Marigowda, Gautham, Israel, Elliot, Severe Asthma Research Program, National Heart, Lung, and Blood Institute
Published in American journal of respiratory and critical care medicine (01.10.2005)
Published in American journal of respiratory and critical care medicine (01.10.2005)
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