Characterization of the interplay between DNA repair and CRISPR/Cas9-induced DNA lesions at an endogenous locus
Bothmer, Anne, Phadke, Tanushree, Barrera, Luis A, Margulies, Carrie M, Lee, Christina S, Buquicchio, Frank, Moss, Sean, Abdulkerim, Hayat S, Selleck, William, Jayaram, Hariharan, Myer, Vic E, Cotta-Ramusino, Cecilia
Published in Nature communications (09.01.2017)
Published in Nature communications (09.01.2017)
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Journal Article
Multiplexed DNA repair assays for multiple lesions and multiple doses via transcription inhibition and transcriptional mutagenesis
Nagel, Zachary D., Margulies, Carrie M., Chaim, Isaac A., McRee, Siobhan K., Mazzucato, Patrizia, Ahmad, Anwaar, Abo, Ryan P., Butty, Vincent L., Forget, Anthony L., Samson, Leona D.
Published in Proceedings of the National Academy of Sciences - PNAS (06.05.2014)
Published in Proceedings of the National Academy of Sciences - PNAS (06.05.2014)
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Journal Article
A highly efficient transgene knock-in technology in clinically relevant cell types
Allen, Alexander G, Khan, Samia Q, Margulies, Carrie M, Viswanathan, Ramya, Lele, Swarali, Blaha, Laura, Scott, Sean N, Izzo, Kaitlyn M, Gerew, Alexandra, Pattali, Rithu, Cochran, Nadire R, Holland, Carl S, Zhao, Amy H, Sherman, Stephen E, Jaskolka, Michael C, Wu, Meng, Wilson, Aaron C, Sun, Xiaoqi, Ciulla, Dawn M, Zhang, Deric, Nelson, Jacqueline D, Zhang, Peisheng, Mazzucato, Patrizia, Huang, Yan, Giannoukos, Georgia, Marco, Eugenio, Nehil, Michael, Follit, John A, Chang, Kai-Hsin, Shearman, Mark S, Wilson, Christopher J, Zuris, John A
Published in Nature biotechnology (01.03.2024)
Published in Nature biotechnology (01.03.2024)
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Journal Article
Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome
Vavassori, Valentina, Mercuri, Elisabetta, Marcovecchio, Genni E, Castiello, Maria C, Schiroli, Giulia, Albano, Luisa, Margulies, Carrie, Buquicchio, Frank, Fontana, Elena, Beretta, Stefano, Merelli, Ivan, Cappelleri, Andrea, Rancoita, Paola MV, Lougaris, Vassilios, Plebani, Alessandro, Kanariou, Maria, Lankester, Arjan, Ferrua, Francesca, Scanziani, Eugenio, Cotta‐Ramusino, Cecilia, Villa, Anna, Naldini, Luigi, Genovese, Pietro
Published in EMBO molecular medicine (05.03.2021)
Published in EMBO molecular medicine (05.03.2021)
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Journal Article
ALKBH7 drives a tissue and sex-specific necrotic cell death response following alkylation-induced damage
Jordan, Jennifer J, Chhim, Sophea, Margulies, Carrie M, Allocca, Mariacarmela, Bronson, Roderick T, Klungland, Arne, Samson, Leona D, Fu, Dragony
Published in Cell death & disease (20.07.2017)
Published in Cell death & disease (20.07.2017)
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Journal Article
Expanding CRISPR Genome Editing Strategies in Hematopoietic Stem and Progenitor Cells for the Treatment of Hematologic Diseases
deDreuzy, Edouard, Chalishazar, Aditi, Heath, Jack, Margulies, Carrie M, Labella, John, Viswanathan, Ramya, Loveluck, Katherine, Chang, KaiHsin, Jayaram, Hariharan, Zuris, John A, Myer, Vic E, Albright, Charlie, Cotta-Ramusino, Cecilia, Gori, Jennifer L
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Journal Article
필수 유전자 녹-인에 의한 선택
MONETTI CLAUDIO, MCAULIFFE CONOR BRIAN, ZURIS JOHN ANTHONY, TOMISHIMA MARK JAMES, SOH CHEW LI, MARGULIES CARRIE MARIE, TONGE PETER
Year of Publication 03.03.2023
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Year of Publication 03.03.2023
Patent
SYSTEMS AND METHODS FOR TREATING HYPER-IGM SYNDROME
GENOVESE, Pietro, COTTA-RAMUSINO, Cecillia, MARGULIES, Carrie, M, NALDINI, Luigi
Year of Publication 11.09.2024
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Year of Publication 11.09.2024
Patent