An engineered U1 small nuclear RNA rescues splicing‐defective coagulation F7 gene expression in mice
Balestra, D., Faella, A., Margaritis, P., Cavallari, N., Pagani, F., Bernardi, F., Arruda, V. R., Pinotti, M.
Published in Journal of thrombosis and haemostasis (01.02.2014)
Published in Journal of thrombosis and haemostasis (01.02.2014)
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Journal Article
An engineered U1 small nuclear RNA rescues splicing defective coagulation F7 gene expression in mice
Balestra, D, Faella, A, Margaritis, P, Cavallari, N, Pagani, F, Bernardi, F, Arruda, V R, Pinotti, M
Published in Journal of thrombosis and haemostasis (01.02.2014)
Published in Journal of thrombosis and haemostasis (01.02.2014)
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Journal Article
One amino acid in mouse activated factor VII defines its endothelial protein C receptor (EPCR) binding and modulates its EPCR‐dependent hemostatic activity in vivo
Pavani, G., Zintner, S. M., Ivanciu, L., Small, J. C., Stafford, K. A., Szeto, J. H., Margaritis, P.
Published in Journal of thrombosis and haemostasis (01.03.2017)
Published in Journal of thrombosis and haemostasis (01.03.2017)
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Journal Article
Gene therapy in haemophilia - going for cure?
MARGARITIS, P., HIGH, K. A.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2010)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2010)
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Journal Article
A viable mouse model of factor X deficiency provides evidence for maternal transfer of factor X
Tai, S J, Herzog, R W, Margaritis, P, Arruda, V R, Chu, K, Golden, J A, Labosky, P A, High, K A
Published in Journal of thrombosis and haemostasis (01.02.2008)
Published in Journal of thrombosis and haemostasis (01.02.2008)
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Journal Article
A novel missense mutation responsible for factor VII deficiency in research Beagle colonies
CALLAN, M. B., ALJAMALI, M. N., MARGARITIS, P., GRIOT‐WENK, M. E., POLLAK, E. S., WERNER, P., GIGER, U., HIGH, K. A.
Published in Journal of thrombosis and haemostasis (01.12.2006)
Published in Journal of thrombosis and haemostasis (01.12.2006)
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Journal Article
Optimized Production of High-Titer Recombinant Adeno-Associated Virus in Roller Bottles
Liu, Y.-L, Wagner, K, Robinson, N, Sabatino, D, Margaritis, P, Xiao, W, Herzog, R.W
Published in BioTechniques (01.01.2003)
Published in BioTechniques (01.01.2003)
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Journal Article
Prevention of spontaneous bleeding in dogs with haemophilia A and haemophilia B
NICHOLS, T. C., RAYMER, R. A., FRANCK, H. W. G., MERRICKS, E. P., BELLINGER, D. A., DeFRIESS, N., MARGARITIS, P., ARRUDA, V. R., KAY, M. A., HIGH, K. A.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2010)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2010)
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Journal Article
Novel therapeutic approach for hemophilia using gene delivery of an engineered secreted activated Factor VII
Margaritis, Paris, Arruda, Valder R., Aljamali, Majed, Camire, Rodney M., Schlachterman, Alexander, High, Katherine A.
Published in The Journal of clinical investigation (01.04.2004)
Published in The Journal of clinical investigation (01.04.2004)
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Journal Article
ORIGINAL ARTICLE: A novel missense mutation responsible for factor VII deficiency in research Beagle colonies
Callan, M B, Aljamali, M N, Margaritis, P, Griot-Wenk, ME, Pollak, E S, Werner, P, Giger, U, High, KA
Published in Journal of thrombosis and haemostasis (01.12.2006)
Published in Journal of thrombosis and haemostasis (01.12.2006)
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Journal Article
In vivo detection of hemorrhage rate in dog models of hemophilia and VWD and at human femoral arteriotomy by ARFI ultrasound
Scola, M. R., Baggesen, L. M., Behler, R. H., Nichols, T. C., Hongtu Zhu, Caughey, M. C., Merricks, E. P., Raymer, R. A., Margaritis, P., High, K. A., Gallippi, C. M.
Published in 2011 IEEE International Ultrasonics Symposium (01.10.2011)
Published in 2011 IEEE International Ultrasonics Symposium (01.10.2011)
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