How Slow RNA Polymerase II Elongation Favors Alternative Exon Skipping
Dujardin, Gwendal, Lafaille, Celina, de la Mata, Manuel, Marasco, Luciano E., Muñoz, Manuel J., Le Jossic-Corcos, Catherine, Corcos, Laurent, Kornblihtt, Alberto R.
Published in Molecular cell (22.05.2014)
Published in Molecular cell (22.05.2014)
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Journal Article
The physiology of alternative splicing
Marasco, Luciano E, Kornblihtt, Alberto R
Published in Nature reviews. Molecular cell biology (01.04.2023)
Published in Nature reviews. Molecular cell biology (01.04.2023)
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Journal Article
Physiological tissue-specific and age-related reduction of mouse TDP-43 levels is regulated by epigenetic modifications
Pacetti, Miriam, De Conti, Laura, Marasco, Luciano E, Romano, Maurizio, Rashid, Mohammad M, Nubiè, Martina, Baralle, Francisco E, Baralle, Marco
Published in Disease models & mechanisms (01.04.2022)
Published in Disease models & mechanisms (01.04.2022)
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Journal Article
Counteracting chromatin effects of a splicing-correcting antisense oligonucleotide improves its therapeutic efficacy in spinal muscular atrophy
Marasco, Luciano E., Dujardin, Gwendal, Sousa-Luís, Rui, Liu, Ying Hsiu, Stigliano, Jose N., Nomakuchi, Tomoki, Proudfoot, Nick J., Krainer, Adrian R., Kornblihtt, Alberto R.
Published in Cell (09.06.2022)
Published in Cell (09.06.2022)
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Journal Article
Nuclear role for human Argonaute-1 as an estrogen-dependent transcription coactivator
Gómez Acuña, Luciana I, Nazer, Ezequiel, Rodríguez-Seguí, Santiago A, Pozzi, Berta, Buggiano, Valeria, Marasco, Luciano E, Agirre, Eneritz, He, Cody, Alló, Mariano, Kornblihtt, Alberto R
Published in The Journal of cell biology (07.09.2020)
Published in The Journal of cell biology (07.09.2020)
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Journal Article
Design and evaluation of an incoherent feed-forward loop for an arsenic biosensor based on standard iGEM parts
Barone, Federico, Dorr, Francisco, Marasco, Luciano E, Mildiner, Sebastián, Patop, Inés L, Sosa, Santiago, Vattino, Lucas G, Vignale, Federico A, Altszyler, Edgar, Basanta, Benjamin, Carlotto, Nicolás, Gasulla, Javier, Giménez, Manuel, Grande, Alicia, Nieto Moreno, Nicolás, Bonomi, Hernán R, Nadra, Alejandro D
Published in Synthetic biology (Oxford University Press) (01.01.2017)
Published in Synthetic biology (Oxford University Press) (01.01.2017)
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Journal Article
COMPOSITIONS FOR TREATMENT OF SPINAL MUSCULAR ATROPHY
MARASCO, Luciano E, KORNBLIHTT, Alberto R, KRAINER, Adrian, STIGLIANO, Jose
Year of Publication 28.09.2023
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Year of Publication 28.09.2023
Patent
COMPOSITIONS FOR TREATMENT OF SPINAL MUSCULAR ATROPHY
MARASCO, Luciano E, KORNBLIHTT, Alberto R, KRAINER, Adrian, STIGLIANO, Jose
Year of Publication 17.05.2023
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Year of Publication 17.05.2023
Patent
Compositions for treatment of spinal muscular atrophy
MARASCO, Luciano E, KORNBLIHTT, Alberto R, KRAINER, Adrian, STIGLIANO, Jose
Year of Publication 02.03.2023
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Year of Publication 02.03.2023
Patent
COMPOSITIONS FOR TREATMENT OF SPINAL MUSCULAR ATROPHY
MARASCO, Luciano E, KORNBLIHTT, Alberto R, KRAINER, Adrian, STIGLIANO, Jose
Year of Publication 20.01.2022
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Year of Publication 20.01.2022
Patent
COMPOSITIONS FOR TREATMENT OF SPINAL MUSCULAR ATROPHY
STIGLIANO, JOSE, KRAINER, ADRIAN, MARASCO, LUCIANO E, KORNBLIHTT, ALBERTO R
Year of Publication 20.01.2022
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Year of Publication 20.01.2022
Patent
Composiciones para el tratamiento de la atrofia muscular espinal
MARASCO, Luciano E, KORNBLIHTT, Alberto R, KRAINER, Adrian, STIGLIANO, Jose
Year of Publication 10.07.2023
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Year of Publication 10.07.2023
Patent
COMPOSITIONS FOR TREATMENT OF SPINAL MUSCULAR ATROPHY
MARASCO Luciano E, KRAINER Adrian, KORNBLIHTT Alberto R, STIGLIANO Jose
Year of Publication 09.06.2023
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Year of Publication 09.06.2023
Patent
Towards a combined therapy for spinal muscular atrophy based on opposing effects of an antisense oligonucleotide on chromatin and splicing
Marasco, Luciano E, Dujardin, Gwendal, Sousa-Luis, Rui, Liu, Ying Hsiu, Stigliano, Jose, Nomakuchi, Tomoki, Proudfoot, Nicholas R, Krainer, Adrian, Kornblihtt, Alberto R
Published in bioRxiv (24.09.2021)
Published in bioRxiv (24.09.2021)
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Paper
COMPOSICIONES PARA TRATAMIENTO DE ATROFIA MUSCULAR ESPINAL
KRAINER, ADRIAN, MARASCO, LUCIANO E, KORNBLIHTT, ALBERTO R, STIGLIANO, JOS
Year of Publication 19.10.2022
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Year of Publication 19.10.2022
Patent