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Safety and efficacy of eculizumab in anti-acetylcholine receptor antibody-positive refractory generalised myasthenia gravis (REGAIN): a phase 3, randomised, double-blind, placebo-controlled, multicentre study

by Utsugisawa, Kimiaki, Kissel, John T, O'Brien, Fanny, Lamont, Phillipa, Roberts, Leslie, De Mey, Katrien, Tilkin, Petra, Alves de Siqueira Carvalho, Alzira, Paiva, Gabriel, Prando, Natalia, Souza, Iandra, Campbell, Natasha, Blackmore, Derrick, Autzen, Anne Mette, Harrison, Tuula, Moutarde, Julie, Le Masson, Gwendal, Wilson, Amy, Fricke, Karin, Horvath, Melinda, Matolcsi, Judit, Szabadosne, Brigitta, Vecsei, Laszlo, Konyane, Monika, Troili, Fernanda, Di Pasquale, Antonella, Filla, Alessandro, Campanella, Angela, Inghilleri, Maurizio, Fionda, Laura, Gabriele, Maria, Salvatore Caramma, Andrea, Kanzaki, Akiko, Jingu, Maki, Yoshimura, Shunsuke, Kobashikawa, Tomomi, Yamashita, Yumi, Kawamura, Tomohiro, Higuchi, Eriko, Osakada, Kaori, Hisahara, Shin, Suzuki, Shuichiro, Ogasawara, Junichi, Shinozaki, Hirokazu, Gibson, Tamar, Keijzers, Maria Johanna, Kim, Byung-Jo, Ra, HyeJin, Kim, Byoung Joon, Lee, JiEun, Kim, Seung Min, Kim, Yool-hee, Lee, Hyung Seok, Yarmoschuk, Asya, Nesterova, Yulia, Fernandez-Fournier, Mireya, Hietala, Albert, Andersson, Blanka, Boz, Cavit, Erdem-Ozdamar, Sevim, Terzi, Murat, Gollogly, Jakit, Smalley, Nicole, Silvestri, Nicholas, Loor, John, Pascuzzi, Robert, Snook, Riley, Carter, Cynthia, Levine-Weinberg, Mark, Simpson, Ericka, Kaur, Harpreet, Crabtree, Brigid, Taber, Sandra, Gilchrist, James, Darnell, Taylor, Goyal, Neelam, Sakamuri, Sarada, Jones, Floyd, Alsharabati, Mohammad, Butters, Janelle, Goyal, Namita, Garcia, Sonia, Echevarria, Laura, Pulley, Michael, Shabbir, Yasmeen, Gutmann, Laurie, Gutmann, Ludwig, Hafer-Macko, Charlene, Chopra, Manisha, Kaufman, Jacob, McClain, Terry, Harvey, Brittany, Huynh, Kristin, Droker, Brian, Weiss, Michael, Downing, Sharon, Bernitsas, Evanthia, Kumar Sriwastava, Shitiz, Jia, Kelly, Patwa, Huned
Published in Lancet neurology (01.12.2017)

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Long‐term safety and efficacy of eculizumab in generalized myasthenia gravis

by Illa, Isabel, Wang, Jing Jing, Garcia, Alejandra Dalila, de Koning, Kathy, Stevens, Olivier, Pozo, Marina, Souza Duca, Luciana, Guerreiro, Alexandre, Carrara, Fernanda, Siddiqi, Zaeem, Kurkova, Barbora, Pitha, Jiri, Wolfova, Marcela, Pedersen, Jane, Oksaranta, Olli, Jakab, Gedeonne, Antonini, Giovanni, Di Pasquale, Antonella, Costabile, Teresa, Marsili, Angela, Bonanno, Silvia, Camera, Giorgia, Pasanisi, Maria, Gabriele, Maria, Uzawa, Akiyuki, Matsushita, Takuya, Kikutake, Keiko, Nakamura, Yumiko, Samukawa, Makoto, Mitazaki, Teiichiro, Yoshimura, Shunsuke, Tsurumaru, Masako, Makamori, Masayuki, Takahashi, Masanori, Hasuike, Tomoya, Kobayashi, Hisako, Osakada, Kaori, Imai, Tomihiro, Tsuda, Emiko, Murahara, Takashi, Suzuki, Shuichiro, Uwasa, Kaori, Min, Ju-Hong, Koh, Da Yoon, Kwon, JuYoung, Hwang, Ji Ye, Kim, Miri, Jung, JinWoo, Shin, Ha Young, Shin, Miju, Lazaro, Ana, Diez Tejedor, Exuperio, Salvado, Maria, Mazuela, Gonzalo, Diaz-Manera, Jordi, Piehl, Fredrik, Hietala, Albert, Sengun, Ihsan, Bekircan‐Kurt, Can Ebru, Orsel, Gulsah, Semiz, Cansu, Veske, Adife, Gollogly, Jakit, Sokratous, Giannis, Sohail, Faisal, Arndt, Heike, Amato, Anthony, Salajegheh, Mohammed, Patrick, Kara, Bravver, Elena, Cunningham, Scott, Schommer, Clara, Carnes, Donna, Bodkin, Cynthia, Carter, Cynthia, Jeffery, Dennis, Chelnick, Sharon, Marburger, Tessa, Gilchrist, James, Andoin, Angela, Seelback, Jenna, Bhavaraju-Sanka, Ratna, Alsharabati, Mohammad, Lu, Liang, Rosenfeld, Jeffrey, Pulley, Michael, Shah, Jaimin, Gutmann, Ludwig, Pasnoor, Mamatha, Jenci, Nicole, Locheke, Jerry, Fondaw, Alex, Sharma, Khema, Steele, Julie, Chopra, Manisha, Katzin, Lara, Beydoun, Said, Waheed, Waqar, Distad, Jane, Robeson, Kimberly
Published in Muscle & nerve (01.07.2019)

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Eculizumab in refractory generalized myasthenia gravis previously treated with rituximab: subgroup analysis of REGAIN and its extension study

by Nowak, Richard J., Mozaffar, Tahseen, Wilken, Miguel, Saba, Juliet, Bettini, Mariela, De Bleecker, Jan, Van den Abeele, Guy, Mahieu, Délphine, Stevens, Olivier, Geraldo, Jordana Gonçalves, Pozo, Marina, Volpe, Luciana Renata Cubas, Ferreira, Luciana, Cassia Santos, Aline, Andrade, Ana Carolina Amaral, Carrara, Fernanda, Junkerova, Jana, Krogh, Susanne, Autzen, Anne Mette Ostergaard, Erälinna, Juha‐Pekka, Oksaranta, Olli, Szabadosne, Brigitta, Antonini, Giovanni, Puorro, Giorgia, Lopergolo, Diego, Onesti, Emanuela, Frasca, Vittorio, Kanzaki, Akiko, Shimpo, Misa, Morikawa, Miyuki, Shiraishi, Hirokazu, Asada, Shizuka, Amamoto, Shoko, Takada, Kazumi, Suzuki, Yasushi, Akiyama, Tetsuya, Narikawa, Koichi, Fukuda, Yusuke, Sato, Miwako, Nakamori, Masayuki, Yamamoto, Daisuke, Ishiyama, Naoko, Lee, Chang Nyoung, Choi, Mi Song, Jeong, Ha‐Neul, Lee, Hyung Seok, Hwang, Eun Bi, Visser, Marianne, Casasnovas, Carlos, Aguilo, Maria Antonia Alberti, Tejedor, Exuperio Diez, Rivera, Francisco Javier Rodriguez, Fernandez‐Fournier, Mireya, Sastre, Maria, Carbonell, Josep Gamez, Piehl, Fredrik, Hietala, Albert, Sengun, Ihsan, Orsel, Gulsah, Semiz, Cansu, Cavdar, Tugce Kirbas, Sohail, Faisal, Arndt, Heike, Salajegheh, Mohammed, Bravver, Elena, Plevka, Sarah, Guptill, Jeffrey, Hobson‐Webb, Lisa, Pascuzzi, Robert, Mosmiller, Betsy, Ventura, Nicholas, Carter, Cynthia, Sattar, Nadia, Daniels, Kevin, Jeffery, Dennis, Khoury, Julie, Dimitrova, Diana, Seelbach, Jenna, Paulose, Shirley, Bhavaraju‐Sanka, Ratna, Jones, Floyd, Roy, Gulmohor, Mathew, Veena, Echevarria, Laura, Shabbir, Yasmeen, Barohn, Richard, Glenn, Melanie, Johns, Kathryn, Naunton, Kerry, Bilsker, Martin, Karam, Chafic, Vu, Tuan, Gong, Hui, Karimi, Sanaz, Akhter, Salma, Strom, Susan, Bertorini, Tulio, Henderson, Kendrick, Wheeler, Lauren, Nye, Joan
Published in Muscle & nerve (01.12.2021)

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Long-term efficacy and safety of eculizumab in Japanese patients with generalized myasthenia gravis: A subgroup analysis of the REGAIN open-label extension study

by Suzuki, Hidekazu, Fujita, Kenji P., Rugiero, Marcelo, Bettini, Mariela, Garcia, Alejandra Dalila, Smetcoren, Charlotte, Van Daele, Sien, Verjans, Sarah, Melo, Ana Paula, Rocha, Rosana, Gonçalves Geraldo, Jordana, Otavio Maia Gonçalves, Luiz, Renata Cubas Volpe, Luciana, Amaral Andrade, Ana Carolina, Cavalcante Lino, Valeria, Carrara, Fernanda, Siddiqi, Zaeem, Phan, Cecile, Junkerova, Jana, Zapletalova, Olga, Wolfova, Marcela, Eriksson, Jaana, Matolcsi, Judit, Garibaldi, Matteo, Saccà, Francesco, Mantegazza, Renato, Bonanno, Silvia, Camera, Giorgia, Pasanisi, Maria, Matsuse, Dai, Nakamura, Yumiko, Futono, Kazumi, Morikawa, Miyuki, Miyawaki, Eriko, Motomura, Masakatsu, Maeda, Yasuko, Takada, Kazumi, Akiyama, Tetsuya, Fukuda, Yusuke, Sato, Miwako, Kawamura, Tomohiro, Kobayashi, Hisako, Tsuda, Emiko, Hayashi, Takashi, Murahara, Takashi, Suzuki, Shuichiro, Noshiro, Mayuko, Yasuda, Ikuko, Homedes-Pedret, Christian, Julia Palacios, Natalia, Diez Tejedor, Exuperio, Rodriguez de Rivera, Francisco Javier, Cortes Vicente, Elena, Querol Gutierrez, Luis Antonio, Bjarbo, Lena, Meherremova, Arzu, Balkan, Bengu, Ugur, Muzeyyen, Aydinlik, Seda, Cavus, Hakan, Kutlu, Ayse, Veske, Adife, Sokratous, Giannis, Shah, Amna, Arndt, Heike, Wolfe, Gil, Patrick, Kara, Forshew, Dallas, Bravver, Elena, Hobson-Webb, Lisa, Beck, Kate, Pascuzzi, Robert, Kincaid, John, Kelley, Andrea, Ho, Doreen, Scala, Stephanie, Herbert, Carol, Weiner, Elaine, Marburger, Tessa, Dimitrova, Diana, Seelback, Jenna, Alsharabati, Mohammad, Nozaki, Kenkichi, Minton, Brian, Rosenfeld, Jeffrey, Shah, Jaimin, Smith, Lisa, Jerath, Nivedita, Swenson, Andrea, Dimachkie, Mazen, Wang, Yunxia, Johns, Kathryn, Hafer-Macko, Charlene, Young, Valerie, Sheldon, Danielle, Katzin, Lara, Droker, Brian, Lin, Frank, Pokala, Krishna, Weiss, Michael
Published in Journal of the neurological sciences (15.12.2019)

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Response to eculizumab in patients with myasthenia gravis recently treated with chronic IVIg: a subgroup analysis of REGAIN and its open-label extension study

by Jacob, Saiju, Nowak, Richard J., Wiendl, Heinz, Fujita, Kenji P., O’Brien, Fanny, Howard, James F., Mazia, Claudio Gabriel, Wilken, Miguel, Saba, Juliet, de Koning, Kathy, De Mey, Katrien, Carvalho, Alzira Alves de Siqueira, Brockhausen, Igor Dias, Feder, David, Ambrosio, Daniel, César, Pamela, Melo, Ana Paula, Ribeiro, Renata Martins, Rocha, Rosana, Rosa, Bruno Bezerra, Veiga, Thabata, da Silva, Luiz Augusto, Gonçalves Geraldo, Jordana, Nagane, Yuriko, Kamegamori, Ikuko, Tsuda, Tomoko, Fujii, Yuko, Futono, Kazumi, Mizugami, Aya, Saito, Yuka, van der Kooi, Anneke, de Visser, Marianne, Gibson, Tamar, Kim, Seung Min, Jeong, JinWoo, Jung, Ha-Neul, Kim, Yool-hee, Lee, Hyung Seok, Shin, Ha Young, Hwang, Eun Bi, Shin, Miju, Carbonell, Josep Gamez, Sune, Pilar, Figueras, Maria Salvado, Gili, Gisela, Piehl, Fredrik, Bjarbo, Lena, Erdem-Ozdamar, Sevim, Bekircan-Kurt, Can Ebru, Acar, Nazire Pinar, Yilmaz, Ezgi, Orsel, Gulsah, Salajegheh, Mohammed, Roe, Kristen, Amato, Katherine, Toska, Shirli, Haar, Laura, McKinnon, Naya, Alcon, Karan, McKenna, Kaitlyn, Sattar, Nadia, Daniels, Kevin, Jeffery, Dennis, Mozaffar, Tahseen, Cash, Tiyonnoh, Roy, Gulmohor, Mathew, Veena, Maqsood, Fatima, Minton, Brian, Hafer-Macko, Charlene, Kwan, Justin, Callison, Karen, Young, Valerie, DiSanzo, Beth, Naunton, Kerry, Vu, Tuan, Katzin, Lara, McClain, Terry, Harvey, Brittany, Hart, Adam, Beydoun, Said, Chilingaryan, Amaiak, Doan, Victor, Droker, Brian, Gong, Hui, Karimi, Sanaz, Lin, Frank, Shah, Akshay, Akhter, Salma, Tandan, Rup, Waheed, Waqar, Lucy, Shannon, Bertorini, Tulio, Arnold, Thomas, Hendersen, Kendrick, Pillai, Rekha, Liu, Ye, Wheeler, Lauren, Hewlett, Jasmine, Vanderhook, Mollie
Published in Therapeutic advances in neurological disorders (2020)

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Consistent improvement with eculizumab across muscle groups in myasthenia gravis

by Mantegazza, Renato, Chaves, Marcelo, Vidal, Gonzalo, Mercelis, Rudy, Van Damme, Philip, Vandenbussche, Nicolas, Vynckier, Jan, Tilkin, Petra, Feder, David, Bezerra Rosa, Bruno, Paiva, Gabriel, Fernanda Butinhao, Cristiani, Paula Macagnan, Ana, Pinto, Graziela, Souza Bulle Oliveira, Acary, Annes, Marcelo, Cavalcante Lino, Valeria, Pinto, Wladimir, Assis, Natália, Fernandes, Patrícia, Narayan, Jeffrey, Blackmore, Derrick, Vohanka, Stanislav, Chmelikova, Magda, Toncrova, Stanislava, Kurkova, Barbora, Zapletalova, Olga, Pedersen, Jane, Erälinna, Juha‐Pekka, Harrison, Tuula, Rozsa, Csilla, Di Pasquale, Antonella, Garibaldi, Matteo, Gori, Maria, Marano, Enrico, Bonanno, Silvia, Camera, Giorgia, Pasanisi, Maria, Uzawa, Akiyuki, Kobayashi, Eri, Samukawa, Makoto, Suzuki, Hidekazu, Miyawaki, Eriko, Kobayashi, Hisako, Osakada, Kaori, Miyazaki, Teiichiro, Yoshimura, Shunsuke, Tsurumaru, Masako, Hisahara, Shin, Kawamata, Jun, Ishiyama, Yoko, Noshiro, Mayuko, Takeyama, Rumi, Lee, HyeLim, Lee, JiEun, Park, SangAe, Homedes‐Pedret, Christian, Diaz‐Manera, Jordi, Antonio Querol Gutiérrez, Luis, Lopez Ruiz, Pedro, Rodriguez de Rivera, Francisco Javier, Meherremova, Arzu, Pinar Acar, Nazire, Kazim Onar, Musa, Davies, Debbie, Wolfe, Gil, Sanjak, Mohammed, Massey, Janice, Kincaid, John, Chaudhry, Vinay, Vytopil, Michal, Jara, Jordan, Weiner, Elaine, McKinnon, Naya, McKenna, Kaitlyn, Kohlrus, Stephanie, Darnell, Taylor, Lokaitis, Barbara, Padilla, Patricia, Hopkins, Steve, Nozaki, Kenkichi, Mumfrey‐Thomas, Sandi, Woodall, Amy, Maqsood, Fatima, Minton, Brian, Garcia, Rebekah, Ross Berger, Alan, Shabbir, Yasmeen, Gutmann, Ludwig, Jenci, Nicole, Fondaw, Alex, Sharma, Khema, Steele, Julie, Hart, Adam, Waheed, Waqar, Weiss, Michael, Downing, Sharon, Arnold, Thomas, Hewlett, Jasmine, Dicapua, Daniel
Published in Annals of clinical and translational neurology (01.08.2020)

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