A phase 2/3 randomized clinical trial followed by an open-label extension to evaluate the effectiveness of elamipretide in Barth syndrome, a genetic disorder of mitochondrial cardiolipin metabolism
Reid Thompson, W, Hornby, Brittany, Manuel, Ryan, Bradley, Elena, Laux, Janice, Carr, Jim, Vernon, Hilary J
Published in Genetics in medicine (01.03.2021)
Published in Genetics in medicine (01.03.2021)
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Journal Article
Natural history comparison study to assess the efficacy of elamipretide in patients with Barth syndrome
Hornby, Brittany, Thompson, William Reid, Almuqbil, Mohammed, Manuel, Ryan, Abbruscato, Anthony, Carr, Jim, Vernon, Hilary J
Published in Orphanet journal of rare diseases (02.09.2022)
Published in Orphanet journal of rare diseases (02.09.2022)
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Journal Article
Research Productivity as Performance Dynamics of PISA among Southeast Asian Countries
Guido, Ryan Manuel D., Mangali, Glen R.
Published in 2022 IEEE 14th International Conference on Humanoid, Nanotechnology, Information Technology, Communication and Control, Environment, and Management (HNICEM) (01.12.2022)
Published in 2022 IEEE 14th International Conference on Humanoid, Nanotechnology, Information Technology, Communication and Control, Environment, and Management (HNICEM) (01.12.2022)
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Conference Proceeding
Exploring Spratly Islands in using VIIRS Boat Detection Satellite Image Analytics
Guido, Ryan Manuel D., Santos, Gian Paulo A.
Published in 2022 IEEE 14th International Conference on Humanoid, Nanotechnology, Information Technology, Communication and Control, Environment, and Management (HNICEM) (01.12.2022)
Published in 2022 IEEE 14th International Conference on Humanoid, Nanotechnology, Information Technology, Communication and Control, Environment, and Management (HNICEM) (01.12.2022)
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Conference Proceeding
Business Technology and Innovation Research among Southeast Asian Countries: Examining Philippine Performance in Technoinnovation Research
Crisostomo, Leonila C., Guido, Ryan Manuel D., Villanueva, Mykl A.
Published in 2022 IEEE 14th International Conference on Humanoid, Nanotechnology, Information Technology, Communication and Control, Environment, and Management (HNICEM) (01.12.2022)
Published in 2022 IEEE 14th International Conference on Humanoid, Nanotechnology, Information Technology, Communication and Control, Environment, and Management (HNICEM) (01.12.2022)
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Conference Proceeding
ELAMIPRETIDE IMPROVES FUNCTIONAL ASSESSMENTS WHEN COMPARED TO THE NATURAL HISTORY PROGRESSION OF CARDIOMYOPATHY-RELATED DISEASE SYMPTOMATOLOGY IN PATIENTS WITH BARTH SYNDROME: A TAZPOWER ANALYSIS
Thompson, W. Reid, Manuel, Ryan, Abbruscato, Anthony, Carr, Jim, Hornby, Brittany, Vernon, Hilary
Published in Journal of the American College of Cardiology (11.05.2021)
Published in Journal of the American College of Cardiology (11.05.2021)
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Journal Article
ELAMIPRETIDE IN PATIENTS WITH BARTH SYNDROME: A RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED CLINICAL TRIAL FOLLOWED BY 36-WEEK OPEN-LABEL EXTENSION
Thompson, Reid, Manuel, Ryan, Aiudi, Anthony, Jones, John J., Carr, Jim, Hornby, Brittany, Vernon, Hilary
Published in Journal of the American College of Cardiology (24.03.2020)
Published in Journal of the American College of Cardiology (24.03.2020)
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Journal Article
Long-term efficacy and safety of elamipretide in patients with Barth syndrome: 168-week open-label extension results of TAZPOWER
Thompson, William R., Manuel, Ryan, Abbruscato, Anthony, Carr, Jim, Campbell, John, Hornby, Brittany, Vaz, Frédéric M., Vernon, Hilary J.
Published in Genetics in medicine (01.07.2024)
Published in Genetics in medicine (01.07.2024)
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Journal Article
Elamipretide Prevents the Natural History Progression of Cardiomyopathy-Related Disease Symptomatology in Patients with Barth Syndrome: A Tazpower Analysis
Thompson, William Reid, Manuel, Ryan, Jones, John J., Carr, Jim, Hornby, Brittany, Vernon, Hilary J.
Published in Journal of cardiac failure (01.10.2020)
Published in Journal of cardiac failure (01.10.2020)
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Journal Article
Quality of life in Barth syndrome
Kim, Alexander Y., Vernon, Hilary, Manuel, Ryan, Almuqbil, Mohammed, Hornby, Brittany
Published in Therapeutic advances in rare disease (01.01.2022)
Published in Therapeutic advances in rare disease (01.01.2022)
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Journal Article
Investigations of Recently Discovered Supernova Remnants’ Spectral Plot: AT2019fya, SN2019fjp, SN2019fcc, SN2019fbv, SN2019ffi, and SN2019fce
Raquel, Bjorn Jasper R., Bantaculo, Agnes C., Llemit, Shane Carlo B., Custodio, Eldrin P., Guido, Ryan Manuel D.
Published in International letters of chemistry, physics and astronomy (22.12.2020)
Published in International letters of chemistry, physics and astronomy (22.12.2020)
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Journal Article
Night-time Human Mobility during Pandemic in the Philippines as Observed by VIIRS Satellite
Guido, Ryan Manuel
Published in 2022 IEEE 14th International Conference on Humanoid, Nanotechnology, Information Technology, Communication and Control, Environment, and Management (HNICEM) (01.12.2022)
Published in 2022 IEEE 14th International Conference on Humanoid, Nanotechnology, Information Technology, Communication and Control, Environment, and Management (HNICEM) (01.12.2022)
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Conference Proceeding