Live-imaging of revertant and therapeutically restored dystrophin in the Dmd EGFP-mdx mouse model for Duchenne muscular dystrophy
Petkova, M V, Stantzou, A, Morin, A, Petrova, O, Morales-Gonzalez, S, Seifert, F, Bellec-Dyevre, J, Manoliu, T, Goyenvalle, A, Garcia, L, Richard, I, Laplace-Builhé, C, Schuelke, M, Amthor, H
Published in Neuropathology and applied neurobiology (01.10.2020)
Published in Neuropathology and applied neurobiology (01.10.2020)
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Journal Article
Live‐imaging of revertant and therapeutically restored dystrophin in the DmdEGFP‐mdx mouse model for Duchenne muscular dystrophy
Petkova, M. V., Stantzou, A., Morin, A., Petrova, O., Morales‐Gonzalez, S., Seifert, F., Bellec‐Dyevre, J., Manoliu, T., Goyenvalle, A., Garcia, L., Richard, I., Laplace‐Builhé, C., Schuelke, M., Amthor, H.
Published in Neuropathology and applied neurobiology (01.10.2020)
Published in Neuropathology and applied neurobiology (01.10.2020)
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Journal Article
Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle
Morin, Adrien, Stantzou, Amalia, Petrova, Olga N, Hildyard, John, Tensorer, Thomas, Matouk, Meriem, Petkova, Mina V, Richard, Isabelle, Manoliu, Tudor, Goyenvalle, Aurélie, Falcone, Sestina, Schuelke, Markus, Laplace-Builhé, Corinne, Piercy, Richard J, Garcia, Luis, Amthor, Helge
Published in Proceedings of the National Academy of Sciences - PNAS (10.01.2023)
Published in Proceedings of the National Academy of Sciences - PNAS (10.01.2023)
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DMD – ANIMAL MODELS: EP.77 Subcellular organization of skeletal muscle dystrophin is restored by tricyclo-DNA mediated exon skipping in the DmdEGFP-mdx mouse model
Morin, A., Petrova, O., Petkova, M., Tensorer, T., Manoliu, T., Richard, I., Garcia, L., Schuelke, M., Laplace-Builhé, C., Goyenvalle, A., Stantzou, A., Amthor, H.
Published in Neuromuscular disorders : NMD (01.10.2021)
Published in Neuromuscular disorders : NMD (01.10.2021)
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Journal Article
DMD – ANIMAL MODELS
Morin, A., Petrova, O., Petkova, M., Tensorer, T., Manoliu, T., Richard, I., Garcia, L., Schuelke, M., Laplace-Builhé, C., Goyenvalle, A., Stantzou, A., Amthor, H.
Published in Neuromuscular disorders : NMD (01.10.2021)
Published in Neuromuscular disorders : NMD (01.10.2021)
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Journal Article