Sirolimus is effective in relapsed/refractory autoimmune cytopenias: results of a prospective multi-institutional trial
Bride, Karen L., Vincent, Tiffaney, Smith-Whitley, Kim, Lambert, Michele P., Bleesing, Jack J., Seif, Alix E., Manno, Catherine S., Casper, James, Grupp, Stephan A., Teachey, David T.
Published in Blood (07.01.2016)
Published in Blood (07.01.2016)
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Journal Article
The Growth of Regional Children's Campuses and Academic Departments of Pediatrics
Steiner, Michael J., Moya, Fernando, Liles, Bethany L., Jaskolka, Michael, Pino, Joseph, Hurtado, Christine Waasdorp, Manno, Catherine S., Davis, Stephanie D.
Published in The Journal of pediatrics (01.09.2024)
Published in The Journal of pediatrics (01.09.2024)
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Journal Article
Leadership Development Program Outcomes
Davies, H. Dele, Degnon, Laura E., Donavan, Sarah K., Wilmott, Robert W., Manno, Catherine S.
Published in The Journal of pediatrics (01.11.2022)
Published in The Journal of pediatrics (01.11.2022)
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Journal Article
Guidelines for assessing appropriateness of pediatric transfusion
Roseff, Susan D., Luban, Naomi L.C., Manno, Catherine S.
Published in Transfusion (Philadelphia, Pa.) (01.11.2002)
Published in Transfusion (Philadelphia, Pa.) (01.11.2002)
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Journal Article
CD8 + T-cell responses to adeno-associated virus capsid in humans
High, Katherine A, Mingozzi, Federico, Maus, Marcela V, Hui, Daniel J, Sabatino, Denise E, Murphy, Samuel L, Rasko, John E J, Ragni, Margaret V, Manno, Catherine S, Sommer, Jurg, Jiang, Haiyan, Pierce, Glenn F, Ertl, Hildegund C J
Published in Nature medicine (01.04.2007)
Published in Nature medicine (01.04.2007)
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Journal Article
Dose of Prophylactic Platelet Transfusions and Prevention of Hemorrhage
Slichter, Sherrill J, Kaufman, Richard M, Assmann, Susan F, McCullough, Jeffrey, Triulzi, Darrell J, Strauss, Ronald G, Gernsheimer, Terry B, Ness, Paul M, Brecher, Mark E, Josephson, Cassandra D, Konkle, Barbara A, Woodson, Robert D, Ortel, Thomas L, Hillyer, Christopher D, Skerrett, Donna L, McCrae, Keith R, Sloan, Steven R, Uhl, Lynne, George, James N, Aquino, Victor M, Manno, Catherine S, McFarland, Janice G, Hess, John R, Leissinger, Cindy, Granger, Suzanne
Published in The New England journal of medicine (18.02.2010)
Published in The New England journal of medicine (18.02.2010)
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Journal Article
Associations between intracranial haemorrhage and prescribed prophylaxis in a large cohort of haemophilia patients in the United States
Witmer, Char, Presley, Rodney, Kulkarni, Roshni, Michael Soucie, J., Manno, Catherine S., Raffini, Leslie
Published in British journal of haematology (01.01.2011)
Published in British journal of haematology (01.01.2011)
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Journal Article
Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response
High, Katherine A, Manno, Catherine S, Pierce, Glenn F, Arruda, Valder R, Glader, Bertil, Ragni, Margaret, Rasko, John J E, Ozelo, Margareth C, Hoots, Keith, Blatt, Philip, Konkle, Barbara, Dake, Michael, Kaye, Robin, Razavi, Mahmood, Zajko, Albert, Zehnder, James, Rustagi, Pradip, Nakai, Hiroyuki, Chew, Amy, Leonard, Debra, Wright, J Fraser, Lessard, Ruth R, Sommer, Jürg M, Tigges, Michael, Sabatino, Denise, Luk, Alvin, Jiang, Haiyan, Mingozzi, Federico, Couto, Linda, Ertl, Hildegund C, Kay, Mark A
Published in Nature medicine (01.03.2006)
Published in Nature medicine (01.03.2006)
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Journal Article
Characteristics of Hospitalized Children With SARS-CoV-2 in the New York City Metropolitan Area
Verma, Sourabh, Lumba, Rishi, Dapul, Heda M, Gold-von Simson, Gabrielle, Phoon, Colin K, Lighter, Jennifer L, Farkas, Jonathan S, Vinci, Alexandra, Noor, Asif, Raabe, Vanessa N, Rhee, David, Rigaud, Mona, Mally, Pradeep V, Randis, Tara M, Dreyer, Benard, Ratner, Adam J, Manno, Catherine S, Chopra, Arun
Published in Hospital pediatrics (01.01.2021)
Published in Hospital pediatrics (01.01.2021)
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Journal Article
Evidence of Multiyear Factor IX Expression by AAV-Mediated Gene Transfer to Skeletal Muscle in an Individual with Severe Hemophilia B
Jiang, Haiyan, Pierce, Glenn F, Ozelo, Margareth C, de Paula, Erich V, Vargas, Joseph A, Smith, Peter, Sommer, Jürg, Luk, Alvin, Manno, Catherine S, High, Katherine A, Arruda, Valder R
Published in Molecular therapy (01.09.2006)
Published in Molecular therapy (01.09.2006)
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Journal Article
AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B
Manno, Catherine S., Chew, Amy J., Hutchison, Sylvia, Larson, Peter J., Herzog, Roland W., Arruda, Valder R., Tai, Shing Jen, Ragni, Margaret V., Thompson, Arthur, Ozelo, Margareth, Couto, Linda B., Leonard, Debra G.B., Johnson, Frederick A., McClelland, Alan, Scallan, Ciaran, Skarsgard, Erik, Flake, Alan W., Kay, Mark A., High, Katherine A., Glader, Bertil
Published in Blood (15.04.2003)
Published in Blood (15.04.2003)
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Journal Article
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
High, Katherine A, Kay, Mark A, Manno, Catherine S, Ragni, Margaret V, Larson, Peter J, Couto, Linda B, McClelland, Alan, Glader, Bertil, Chew, Amy J, J Tai, Shing, Herzog, Roland W, Arruda, Valder, Johnson, Fred, Scallan, Ciaran, Skarsgard, Erik, Flake, Alan W
Published in Nature genetics (01.03.2000)
Published in Nature genetics (01.03.2000)
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Journal Article
Unmasking Evans syndrome: T-cell phenotype and apoptotic response reveal autoimmune lymphoproliferative syndrome (ALPS)
Teachey, David T., Manno, Catherine S., Axsom, Kelly M., Andrews, Timothy, Choi, John K., Greenbaum, Barbara H., McMann, Joseph M., Sullivan, Kathleen E., Travis, Susan F., Grupp, Stephan A.
Published in Blood (15.03.2005)
Published in Blood (15.03.2005)
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Journal Article
Rapamycin improves lymphoproliferative disease in murine autoimmune lymphoproliferative syndrome (ALPS)
Teachey, David T., Obzut, Dana A., Axsom, Kelly, Choi, John K., Goldsmith, Kelly C., Hall, Junior, Hulitt, Jessica, Manno, Catherine S., Maris, John M., Rhodin, Nicholas, Sullivan, Kathleen E., Brown, Valerie I., Grupp, Stephan A.
Published in Blood (15.09.2006)
Published in Blood (15.09.2006)
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