Slowing late infantile Batten disease by direct brain parenchymal administration of a rh.10 adeno-associated virus expressing CLN2
Sondhi, Dolan, Kaminsky, Stephen M, Hackett, Neil R, Pagovich, Odelya E, Rosenberg, Jonathan B, De, Bishnu P, Chen, Alvin, Van de Graaf, Benjamin, Mezey, Jason G, Mammen, Grace W, Mancenido, Denesy, Xu, Fang, Kosofsky, Barry, Yohay, Kaleb, Worgall, Stefan, Kaner, Robert J, Souwedaine, Mark, Greenwald, Bruce M, Kaplitt, Michael, Dyke, Jonathan P, Ballon, Douglas J, Heier, Linda A, Kiss, Szilard, Crystal, Ronald G
Published in Science translational medicine (02.12.2020)
Published in Science translational medicine (02.12.2020)
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