A Randomized Trial of Factor VIII and Neutralizing Antibodies in Hemophilia A
Peyvandi, Flora, Mannucci, Pier M, Garagiola, Isabella, El-Beshlawy, Amal, Elalfy, Mohsen, Ramanan, Vijay, Eshghi, Peyman, Hanagavadi, Suresh, Varadarajan, Ramabadran, Karimi, Mehran, Manglani, Mamta V, Ross, Cecil, Young, Guy, Seth, Tulika, Apte, Shashikant, Nayak, Dinesh M, Santagostino, Elena, Mancuso, Maria Elisa, Sandoval Gonzalez, Adriana C, Mahlangu, Johnny N, Bonanad Boix, Santiago, Cerqueira, Monica, Ewing, Nadia P, Male, Christoph, Owaidah, Tarek, Soto Arellano, Veronica, Kobrinsky, Nathan L, Majumdar, Suvankar, Perez Garrido, Rosario, Sachdeva, Anupam, Simpson, Mindy, Thomas, Mathew, Zanon, Ezio, Antmen, Bulent, Kavakli, Kaan, Manco-Johnson, Marilyn J, Martinez, Monica, Marzouka, Esperanza, Mazzucconi, Maria G, Neme, Daniela, Palomo Bravo, Angeles, Paredes Aguilera, Rogelio, Prezotti, Alessandra, Schmitt, Klaus, Wicklund, Brian M, Zulfikar, Bulent, Rosendaal, Frits R
Published in The New England journal of medicine (26.05.2016)
Published in The New England journal of medicine (26.05.2016)
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Journal Article
Inhibitor incidence in an unselected cohort of previously untreated patients with severe haemophilia B: a PedNet study
Male, Christoph, Andersson, Nadine G, Rafowicz, Anne, Liesner, Ri, Kurnik, Karin, Fischer, Kathelijn, Platokouki, Helen, Santagostino, Elena, Chambost, Hervé, Nolan, Beatrice, Königs, Christoph, Kenet, Gili, Ljung, Rolf, Van den Berg, Marijke
Published in Haematologica (Roma) (01.01.2021)
Published in Haematologica (Roma) (01.01.2021)
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Journal Article
Efficacy and tolerability of the ketogenic diet versus high‐dose adrenocorticotropic hormone for infantile spasms: A single‐center parallel‐cohort randomized controlled trial
Dressler, Anastasia, Benninger, Franz, Trimmel‐Schwahofer, Petra, Gröppel, Gudrun, Porsche, Barbara, Abraham, Klaus, Mühlebner, Angelika, Samueli, Sharon, Male, Christoph, Feucht, Martha
Published in Epilepsia (Copenhagen) (01.03.2019)
Published in Epilepsia (Copenhagen) (01.03.2019)
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Journal Article
Genetic determinants of VWF clearance and FVIII binding modify FVIII pharmacokinetics in pediatric hemophilia A patients
Swystun, Laura L., Ogiwara, Kenichi, Rawley, Orla, Brown, Christine, Georgescu, Ilinca, Hopman, Wilma, Labarque, Veerle, Male, Christoph, Thom, Katharina, Blanchette, Victor S., Carcao, Manuel D., Lillicrap, David
Published in Blood (12.09.2019)
Published in Blood (12.09.2019)
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Journal Article
Distinct characteristics of antibody responses against factor VIII in healthy individuals and in different cohorts of hemophilia A patients
Whelan, Shawn F.J., Hofbauer, Christoph J., Horling, Frank M., Allacher, Peter, Wolfsegger, Martin J., Oldenburg, Johannes, Male, Christoph, Windyga, Jerzy, Tiede, Andreas, Schwarz, Hans Peter, Scheiflinger, Friedrich, Reipert, Birgit M.
Published in Blood (07.02.2013)
Published in Blood (07.02.2013)
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Journal Article
Affinity of FVIII-specific antibodies reveals major differences between neutralizing and nonneutralizing antibodies in humans
Hofbauer, Christoph J., Whelan, ShawnF.J., Hirschler, Maria, Allacher, Peter, Horling, Frank M., Lawo, John-Philip, Oldenburg, Johannes, Tiede, Andreas, Male, Christoph, Windyga, Jerzy, Greinacher, Andreas, Knöbl, Paul N., Schrenk, Gerald, Koehn, Jadranka, Scheiflinger, Friedrich, Reipert, Birgit M.
Published in Blood (12.02.2015)
Published in Blood (12.02.2015)
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Journal Article
Evaluation of bone mineral density and bone turnover in children on anticoagulation
Thom, Katharina, Patsch, Janina Maria, Haufler, Florentina, Pees, Christiane, Albinni, Sulaima, Weber, Michael, Male, Christoph, Raimann, Adalbert
Published in Frontiers in endocrinology (Lausanne) (01.08.2023)
Published in Frontiers in endocrinology (Lausanne) (01.08.2023)
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Journal Article
Ketogenic Diet in the Treatment of Super-Refractory Status Epilepticus at a Pediatric Intensive Care Unit: A Single-Center Experience
Breu, Markus, Häfele, Chiara, Glatter, Sarah, Trimmel-Schwahofer, Petra, Golej, Johann, Male, Christoph, Feucht, Martha, Dressler, Anastasia
Published in Frontiers in neurology (03.06.2021)
Published in Frontiers in neurology (03.06.2021)
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Journal Article
Exploratory evaluation of pharmacodynamics, pharmacokinetics and safety of rivaroxaban in children and adolescents: an EINSTEIN-Jr phase I study
Kubitza, Dagmar, Willmann, Stefan, Becka, Michael, Thelen, Kirstin, Young, Guy, Brandão, Leonardo R, Monagle, Paul, Male, Christoph, Chan, Anthony, Kennet, Gili, Martinelli, Ida, Saracco, Paola, Lensing, Anthonie W A
Published in Thrombosis journal (04.12.2018)
Published in Thrombosis journal (04.12.2018)
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Journal Article
Safety and Efficacy of Recombinant Fusion Protein Linking Coagulation Factor IX with Albumin (rIX-FP) in Previously Untreated Patients with Hemophilia B
Lemons, Richard, Wang, Michael, Curtin, Julie, Lepatan, Lynda Mae, Male, Christoph, Peyvandi, Flora, von Depka Prondzinski, Mario, Wang, Rongrong, McKeand, William, Seifert, Wilfried, Oldenburg, Johannes
Published in TH open : companion journal to thrombosis and haemostasis (01.01.2024)
Published in TH open : companion journal to thrombosis and haemostasis (01.01.2024)
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Journal Article
Influence of Age, Heart Failure and ACE Inhibitor Treatment on Plasma Renin Activity in Children: Insights from a Systematic Review and the European LENA Project
Steichert, Melina, Cawello, Willi, Bajcetic, Milica, Breur, Johannes M P J, Dalinghaus, Michiel, Male, Christoph, de Wildt, Saskia N, Läer, Stephanie
Published in Frontiers in bioscience (Landmark. Print) (12.12.2023)
Published in Frontiers in bioscience (Landmark. Print) (12.12.2023)
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Journal Article
Rivaroxaban versus standard anticoagulation for acute venous thromboembolism in childhood. Design of the EINSTEIN-Jr phase III study
Lensing, Anthonie W A, Male, Christoph, Young, Guy, Kubitza, Dagmar, Kenet, Gili, Patricia Massicotte, M, Chan, Anthony, Molinari, Angelo C, Nowak-Goettl, Ulrike, Pap, Ákos F, Adalbo, Ivet, Smith, William T, Mason, Amy, Thelen, Kirstin, Berkowitz, Scott D, Crowther, Mark, Schmidt, Stephan, Price, Victoria, Prins, Martin H, Monagle, Paul
Published in Thrombosis journal (21.12.2018)
Published in Thrombosis journal (21.12.2018)
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Journal Article
Enalapril and Enalaprilat Pharmacokinetics in Children with Heart Failure Due to Dilated Cardiomyopathy and Congestive Heart Failure after Administration of an Orodispersible Enalapril Minitablet (LENA-Studies)
Laeer, Stephanie, Cawello, Willi, Burckhardt, Bjoern B., Ablonczy, László, Bajcetic, Milica, Breur, Johannes M. P. J., Dalinghaus, Michiel, Male, Christoph, de Wildt, Saskia N., Breitkreutz, Jörg, Faisal, Muhammed, Keatley-Clarke, Anne, Klingmann, Ingrid, Lagler, Florian B.
Published in Pharmaceutics (30.05.2022)
Published in Pharmaceutics (30.05.2022)
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Journal Article
SARS-CoV-2 Associated Pediatric Inflammatory Multisystem Syndrome With a High Prevalence of Myocarditis – A Multicenter Evaluation of Clinical and Laboratory Characteristics, Treatment and Outcome
Thom, Katharina, Kahl, Beatrice, Wagner, Thomas, van Egmond-Fröhlich, Andreas, Krainz, Mathias, Frischer, Thomas, Leeb, Iris, Schuster, Christine, Ehringer-Schetitska, Doris, Minkov, Milen, Male, Christoph, Michel-Behnke, Ina
Published in Frontiers in pediatrics (10.06.2022)
Published in Frontiers in pediatrics (10.06.2022)
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Journal Article
Recommendations to Enhance Pediatric Cardiovascular Drug Development: Report of a Multi‐Stakeholder Think Tank
Torok, Rachel D., Li, Jennifer S., Kannankeril, Prince J., Atz, Andrew M., Bishai, Raafat, Bolotin, Ellen, Breitenstein, Stefanie, Chen, Cathy, Diacovo, Thomas, Feltes, Timothy, Furlong, Patricia, Hanna, Michael, Graham, Eric M., Hsu, Daphne, Ivy, D. Dunbar, Murphy, Dianne, Kammerman, Lisa A., Kearns, Gregory, Lawrence, John, Lebeaut, Brigitte, Li, Danshi, Male, Christoph, McCrindle, Brian, Mugnier, Pierre, Newburger, Jane W., Pearson, Gail D., Peiris, Vasum, Percival, Lisa, Pina, Miriam, Portman, Ronald, Shaddy, Robert, Stockbridge, Norman L., Temple, Robert, Hill, Kevin D.
Published in Journal of the American Heart Association (20.02.2018)
Published in Journal of the American Heart Association (20.02.2018)
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Journal Article
Evaluation of bone health in pediatric patients with chronic anticoagulation pharmacotherapy
Raimann, Adalbert, Patsch, Janina, Weber, Michael, Haufler, Florentina, Pees, Christiane, Albinni, Sulaima, Male, Christoph, Thom, Katharina
Published in Bone Reports (01.04.2021)
Published in Bone Reports (01.04.2021)
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Journal Article
Orodispersible minitablets of enalapril for use in children with heart failure (LENA): Rationale and protocol for a multicentre pharmacokinetic bridging study and follow-up safety study
Bajcetic, Milica, de Wildt, Saskia N, Dalinghaus, Michiel, Breitkreutz, Jörg, Klingmann, Ingrid, Lagler, Florian B, Keatley-Clarke, Anne, Breur, Johannes MPJ, Male, Christoph, Jovanovic, Ida, Szatmári, Andras, Ablonczy, László, Burckhardt, Bjoern B, Cawello, Willi, Kleine, Karl, Obarcanin, Emina, Spatenkova, Lucie, Swoboda, Vanessa, van der Meulen, Marijke, Wagner, Peter, Walsh, Jennifer, Läer, Stephanie
Published in Contemporary clinical trials communications (01.09.2019)
Published in Contemporary clinical trials communications (01.09.2019)
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