Guidelines for the management of hemophilia
Srivastava, A., Brewer, A. K., Mauser-Bunschoten, E. P., Key, N. S., Kitchen, S., Llinas, A., Ludlam, C. A., Mahlangu, J. N., Mulder, K., Poon, M. C., Street, A.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2013)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2013)
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Journal Article
Emerging therapies for haemophilia ‐ Global perspective
Mahlangu, J., Cerquiera, M., Srivastava, A.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2018)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2018)
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Journal Article
Safety and pharmacokinetics of anti‐TFPI antibody (concizumab) in healthy volunteers and patients with hemophilia: a randomized first human dose trial
Chowdary, P., Lethagen, S., Friedrich, U., Brand, B., Hay, C., Abdul Karim, F., Klamroth, R., Knoebl, P., Laffan, M., Mahlangu, J., Miesbach, W., Dalsgaard Nielsen, J., Martín‐Salces, M., Angchaisuksiri, P.
Published in Journal of thrombosis and haemostasis (01.05.2015)
Published in Journal of thrombosis and haemostasis (01.05.2015)
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Journal Article
Recombinant factor VIII Fc fusion protein for the prevention and treatment of bleeding in children with severe hemophilia A
Young, G., Mahlangu, J., Kulkarni, R., Nolan, B., Liesner, R., Pasi, J., Barnes, C., Neelakantan, S., Gambino, G., Cristiano, L. M., Pierce, G. F., Allen, G.
Published in Journal of thrombosis and haemostasis (01.06.2015)
Published in Journal of thrombosis and haemostasis (01.06.2015)
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Journal Article
Improved joint health in subjects with severe haemophilia A treated prophylactically with recombinant factor VIII Fc fusion protein
Oldenburg, J., Kulkarni, R., Srivastava, A., Mahlangu, J. N., Blanchette, V. S., Tsao, E., Winding, B., Dumont, J., Jain, N.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2018)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2018)
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Journal Article
Long-term safety and efficacy of recombinant factor VIII Fc fusion protein (rFVIIIFc) in subjects with haemophilia A
Nolan, B., Mahlangu, J., Perry, D., Young, G., Liesner, R., Konkle, B., Rangarajan, S., Brown, S., Hanabusa, H., Pasi, K. J., Pabinger, I., Jackson, S., Cristiano, L. M., Li, X., Pierce, G. F., Allen, G.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2016)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2016)
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Journal Article
Evaluation of the utility of the ISTH-BAT in haemophilia carriers: a multinational study
James, P. D., Mahlangu, J., Bidlingmaier, C., Mingot-Castellano, M. E., Chitlur, M., Fogarty, P. F., Cuker, A., Mancuso, M. E., Holme, P. A., Grabell, J., Satkunam, N., Hopman, W. M., Mathew, P.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2016)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2016)
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Journal Article
Changes in health-related quality of life with treatment of longer-acting clotting factors: results in the A-LONG and B-LONG clinical studies
Wyrwich, K. W., Krishnan, S., Auguste, P., Poon, J.-L., von Maltzahn, R., Yu, R., Pierce, G. F., Mei, B., Mahlangu, J., von Mackensen, S.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2016)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2016)
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Journal Article
Recombinant B‐domain‐deleted porcine sequence factor VIII (r‐pFVIII) for the treatment of bleeding in patients with congenital haemophilia A and inhibitors
Mahlangu, J. N., Andreeva, T. A., Macfarlane, D. E., Walsh, C., Key, N. S.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2017)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2017)
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Journal Article
Recombinant factor VIII Fc fusion protein: extended‐interval dosing maintains low bleeding rates and correlates with von Willebrand factor levels
Shapiro, A. D., Ragni, M. V., Kulkarni, R., Oldenberg, J., Srivastava, A., Quon, D. V., Pasi, K. J., Hanabusa, H., Pabinger, I., Mahlangu, J., Fogarty, P., Lillicrap, D., Kulke, S., Potts, J., Neelakantan, S., Nestorov, I., Li, S., Dumont, J. A., Jiang, H., Brennan, A., Pierce, G. F.
Published in Journal of thrombosis and haemostasis (01.11.2014)
Published in Journal of thrombosis and haemostasis (01.11.2014)
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Journal Article
Pharmacokinetic modelling and validation of the half‐life extension needed to reduce the burden of infusions compared with standard factor VIII
Hermans, C., Mahlangu, J., Booth, J., Schütz, H., Santagostino, E., Young, G., Lee, H.‐Y., Steinitz‐Trost, K. N., Blanchette, V., Berntorp, E.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2018)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2018)
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Journal Article
Low‐factor consumption for major surgery in haemophilia B with long‐acting recombinant glycoPEGylated factor IX
Escobar, M. A., Tehranchi, R., Karim, F. A., Caliskan, U., Chowdary, P., Colberg, T., Giangrande, P., Giermasz, A., Mancuso, M. E., Serban, M., Tsay, W., Mahlangu, J. N.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2017)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2017)
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Journal Article
Changes in the amino acid sequence of the recombinant human factor VIIa analog, vatreptacog alfa, are associated with clinical immunogenicity
Mahlangu, J. N., Weldingh, K. N., Lentz, S. R., Kaicker, S., Karim, F. A., Matsushita, T., Recht, M., Tomczak, W., Windyga, J., Ehrenforth, S., Knobe, K., Weltermann, Ansgar, Paula, Erich, Cerqueira, Monica, Zupancic‐Salek, Silva, Katsarou, Olga, Economou, Marina, Nemes, Laszlo, Boda, Zoltan, Santagostino, Elena, Tagariello, Giuseppe, Hanabusa, Hideji, Fukutake, Katsuyuki, Shima, Midori, Serban, Margit, Elezovic, I., Savic, Aleksandar, Shen, Ming, Chuansumrit, Ampaiwan, Angchaisuksiri, Pantep, Kavakli, Kaan, Sasmaz, Ilgen, Madan, Bella, Giangrande, Paul, Kempton, Christine, Young, Guy, Quon, Doris, Ameri, Afshin, Kuriakose, Philip, Obzut, Dana, Wang, Michael, Ortiz, Idith
Published in Journal of thrombosis and haemostasis (01.11.2015)
Published in Journal of thrombosis and haemostasis (01.11.2015)
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Journal Article
Recombinant factor VIIa analog in the management of hemophilia with inhibitors: results from a multicenter, randomized, controlled trial of vatreptacog alfa
Lentz, S. R., Ehrenforth, S., Abdul Karim, F., Matsushita, T., Weldingh, K. N., Windyga, J., Mahlangu, J. N.
Published in Journal of thrombosis and haemostasis (01.08.2014)
Published in Journal of thrombosis and haemostasis (01.08.2014)
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Journal Article
Presentation and management of acute coronary syndromes among adult persons with haemophilia: results of an international, retrospective, 10-year survey
Fogarty, P. F., Mancuso, M. E., Kasthuri, R., Bidlingmaier, C., Chitlur, M., Gomez, K., Holme, P. A., James, P., Kruse-Jarres, R., Mahlangu, J., Mingot-Castellano, M. E., Soni, A.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.09.2015)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.09.2015)
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Journal Article
Gene and cell therapy in South Africa : current status and future prospects
Mahlangu, J.N., Bloom, K., Ely, A., Arbuthnot, P., Maepa, M.B., Pepper, M.S.
Published in South African medical journal (10.09.2019)
Published in South African medical journal (10.09.2019)
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Journal Article