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Published in NeuroImage (Orlando, Fla.) (01.11.2016)
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Published in Thorax (01.02.2021)
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S61 Onasemnogene abeparvovec gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): preliminary pulmonary and ventilatory findings from the phase 3 study (STR1VE)
Shell, R, Day, JW, Chiriboga, CA, Crawford, TO, Darras, BT, Finkel, RS, Connolly, AM, Iannaccone, ST, Kuntz, NL, Peña, LDM, Shieh, PB, Smith, EC, Kausar, I, Schultz, M, Feltner, DE, Ogrinc, FG, Macek, TA, Kernbauer, E, L’Italien, J, Sproule, DM, Kaspar, BK, Mendell, JR
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Published in Thorax (01.12.2019)
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B.01 AVXS-101 gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): pivotal phase 3 study (STR1VE) update
Day, JW, Chiriboga, CA, Crawford, TO, Darras, BT, Finkel, RS, Connolly, AM, Iannaccone, ST, Kuntz, NL, Pena, LD, Schultz, M, Shieh, PB, Smith, EC, Feltner, DE, Ogrinc, FG, Macek, TA, Kernbauer, E, Muehring, LM, L’Italien, J, Sproule, DM, Kaspar, BK, Mendell, JR
Published in Canadian journal of neurological sciences (01.06.2019)
Published in Canadian journal of neurological sciences (01.06.2019)
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A phase I study of the oral combination of CI-994, a putative histone deacetylase inhibitor, and capecitabine
Undevia, S. D., Kindler, H. L., Janisch, L., Olson, S. C., Schilsky, R. L., Vogelzang, N. J., Kimmel, K. A., Macek, T. A., Ratain, M. J.
Published in Annals of oncology (01.11.2004)
Published in Annals of oncology (01.11.2004)
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Dissociation of Protein Kinase-Mediated Regulation of Metabotropic Glutamate Receptor 7 (mGluR7) Interactions with Calmodulin and Regulation of mGluR7 Function
Sorensen, Scott D, Macek, Thomas A, Cai, Zhaohui, Saugstad, Julie A, Conn, P Jeffrey
Published in Molecular pharmacology (01.06.2002)
Published in Molecular pharmacology (01.06.2002)
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