Long-term safety and tolerability of ProSavin, a lentiviral vector-based gene therapy for Parkinson's disease: a dose escalation, open-label, phase 1/2 trial
Palfi, Stéphane, Prof, Gurruchaga, Jean Marc, MD, Ralph, G Scott, PhD, Lepetit, Helene, PhD, Lavisse, Sonia, PhD, Buttery, Philip C, PhD, Watts, Colin, PhD, Miskin, James, PhD, Kelleher, Michelle, PhD, Deeley, Sarah, MSc, Iwamuro, Hirokazu, MD, Lefaucheur, Jean Pascal, MD, Thiriez, Claire, MD, Fenelon, Gilles, MD, Lucas, Cherry, BA, Brugières, Pierre, MD, Gabriel, Inanna, MD, Abhay, Kou, MD, Drouot, Xavier, MD, Tani, Naoki, MD, Kas, Aurelie, MD, Ghaleh, Bijan, Prof, Le Corvoisier, Philippe, MD, Dolphin, Patrice, MSc, Breen, David P, MRCP, Mason, Sarah, BSc, Guzman, Natalie Valle, MSc, Mazarakis, Nicholas D, Prof, Radcliffe, Pippa A, PhD, Harrop, Richard, PhD, Kingsman, Susan M, PhD, Rascol, Olivier, Prof, Naylor, Stuart, PhD, Barker, Roger A, Prof, Hantraye, Philippe, PhD, Remy, Philippe, Prof, Cesaro, Pierre, Prof, Mitrophanous, Kyriacos A, PhD
Published in The Lancet (British edition) (29.03.2014)
Published in The Lancet (British edition) (29.03.2014)
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Lentiviral Vector Gene Transfer of Endostatin/Angiostatin for Macular Degeneration (GEM) Study
Campochiaro, Peter A, Lauer, Andreas K, Sohn, Elliott H, Mir, Tahreem A, Naylor, Stuart, Anderton, Matthew C, Kelleher, Michelle, Harrop, Richard, Ellis, Scott, Mitrophanous, Kyriacos A
Published in Human gene therapy (01.01.2017)
Published in Human gene therapy (01.01.2017)
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Separate elements of episodic memory subserved by distinct hippocampal-prefrontal connections
Barker, Gareth R I, Banks, Paul J, Scott, Hannah, Ralph, G Scott, Mitrophanous, Kyriacos A, Wong, Liang-Fong, Bashir, Zafar I, Uney, James B, Warburton, E Clea
Published in Nature neuroscience (01.02.2017)
Published in Nature neuroscience (01.02.2017)
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EIAV-based retinal gene therapy in the shaker1 mouse model for usher syndrome type 1B: development of UshStat
Zallocchi, Marisa, Binley, Katie, Lad, Yatish, Ellis, Scott, Widdowson, Peter, Iqball, Sharifah, Scripps, Vicky, Kelleher, Michelle, Loader, Julie, Miskin, James, Peng, You-Wei, Wang, Wei-Min, Cheung, Linda, Delimont, Duane, Mitrophanous, Kyriacos A, Cosgrove, Dominic
Published in PloS one (01.04.2014)
Published in PloS one (01.04.2014)
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Long-Term Follow-Up of a Phase I/II Study of ProSavin, a Lentiviral Vector Gene Therapy for Parkinson's Disease
Palfi, Stéphane, Gurruchaga, Jean Marc, Lepetit, Hélène, Howard, Katy, Ralph, G Scott, Mason, Sarah, Gouello, Gaëtane, Domenech, Philippe, Buttery, Philip C, Hantraye, Philippe, Tuckwell, Nicola J, Barker, Roger A, Mitrophanous, Kyriacos A
Published in Human gene therapy. Clinical development (01.09.2018)
Published in Human gene therapy. Clinical development (01.09.2018)
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Journal Article
Silencing mutant SOD1 using RNAi protects against neurodegeneration and extends survival in an ALS model
Ralph, G Scott, Azzouz, Mimoun, Radcliffe, Pippa A, Day, Denise M, Carthy, Janine M, Leroux, Marie A, Lee, Debbie C P, Wong, Liang-Fong, Bilsland, Lynsey G, Greensmith, Linda, Kingsman, Susan M, Mitrophanous, Kyriacos A, Mazarakis, Nicholas D
Published in Nature medicine (01.04.2005)
Published in Nature medicine (01.04.2005)
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Dopamine gene therapy for Parkinson's disease in a nonhuman primate without associated dyskinesia
Jarraya, Béchir, Boulet, Sabrina, Ralph, G Scott, Jan, Caroline, Bonvento, Gilles, Azzouz, Mimoun, Miskin, James E, Shin, Masahiro, Delzescaux, Thierry, Drouot, Xavier, Hérard, Anne-Sophie, Day, Denise M, Brouillet, Emmanuel, Kingsman, Susan M, Hantraye, Philippe, Mitrophanous, Kyriacos A, Mazarakis, Nicholas D, Palfi, Stéphane
Published in Science translational medicine (14.10.2009)
Published in Science translational medicine (14.10.2009)
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Lentiviral delivered aflibercept OXB-203 for treatment of neovascular AMD
Iqball, Sharifah, Beck, Daniel K., Devarajan, Gayathri, Khoo, Cheen P., O’Connor, Deirdre M., Ellis, Scott, Guzman, Efrain, Mitrophanous, Kyriacos A., Lad, Yatish
Published in Molecular therapy. Methods & clinical development (14.09.2023)
Published in Molecular therapy. Methods & clinical development (14.09.2023)
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Efficient production of germline transgenic chickens using lentiviral vectors
McGrew, Michael J, Sherman, Adrian, Ellard, Fiona M, Lillico, Simon G, Gilhooley, Hazel J, Kingsman, Alan J, Mitrophanous, Kyriacos A, Sang, Helen
Published in EMBO reports (01.07.2004)
Published in EMBO reports (01.07.2004)
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Lentivector-mediated SMN replacement in a mouse model of spinal muscular atrophy
Azzouz, Mimoun, Le, Thanh, Ralph, G Scott, Walmsley, Lucy, Monani, Umrao R, Lee, Debbie C P, Wilkes, Fraser, Mitrophanous, Kyriacos A, Kingsman, Susan M, Burghes, Arthur H M, Mazarakis, Nicholas D
Published in The Journal of clinical investigation (01.12.2004)
Published in The Journal of clinical investigation (01.12.2004)
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Journal Article
Lentivirus-mediated gene transfer to the central nervous system: therapeutic and research applications
Wong, Liang-Fong, Goodhead, Lucy, Prat, Christine, Mitrophanous, Kyriacos A, Kingsman, Susan M, Mazarakis, Nicholas D
Published in Human gene therapy (01.01.2006)
Published in Human gene therapy (01.01.2006)
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Multicistronic Lentiviral Vector-Mediated Striatal Gene Transfer of Aromatic L-Amino Acid Decarboxylase, Tyrosine Hydroxylase, and GTP Cyclohydrolase I Induces Sustained Transgene Expression, Dopamine Production, and Functional Improvement in a Rat Model of Parkinson's Disease
Azzouz, Mimoun, Martin-Rendon, Enca, Barber, Robert D, Mitrophanous, Kyriacos A, Carter, Emma E, Rohll, Jonathan B, Kingsman, Susan M, Kingsman, Alan J, Mazarakis, Nicholas D
Published in The Journal of neuroscience (01.12.2002)
Published in The Journal of neuroscience (01.12.2002)
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Transduction Patterns of Pseudotyped Lentiviral Vectors in the Nervous System
Wong, Liang-Fong, Azzouz, Mimoun, Walmsley, Lucy E, Askham, Zoe, Wilkes, Fraser J, Mitrophanous, Kyriacos A, Kingsman, Susan M, Mazarakis, Nicholas D
Published in Molecular therapy (01.01.2004)
Published in Molecular therapy (01.01.2004)
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Transduction of photoreceptors with equine infectious anemia virus lentiviral vectors: safety and biodistribution of StarGen for Stargardt disease
Binley, Katie, Widdowson, Peter, Loader, Julie, Kelleher, Michelle, Iqball, Sharifah, Ferrige, Georgina, de Belin, Jackie, Carlucci, Marie, Angell-Manning, Diana, Hurst, Felicity, Ellis, Scott, Miskin, James, Fernandes, Alcides, Wong, Paul, Allikmets, Rando, Bergstrom, Christopher, Aaberg, Thomas, Yan, Jiong, Kong, Jian, Gouras, Peter, Prefontaine, Annick, Vezina, Mark, Bussieres, Martin, Naylor, Stuart, Mitrophanous, Kyriacos A
Published in Investigative ophthalmology & visual science (12.06.2013)
Published in Investigative ophthalmology & visual science (12.06.2013)
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Safety and Efficacy of OXB-202, a Genetically Engineered Tissue Therapy for the Prevention of Rejection in High-Risk Corneal Transplant Patients
Fouladi, Naghmeh, Parker, Maria, Kennedy, Vicky, Binley, Katie, McCloskey, Laura, Loader, Julie, Kelleher, Michelle, Mitrophanous, Kyriacos A, Stout, J Timothy, Ellis, Scott
Published in Human gene therapy (01.06.2018)
Published in Human gene therapy (01.06.2018)
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Development of a replication-competent lentivirus assay for dendritic cell-targeting lentiviral vectors
Farley, Daniel C, McCloskey, Laura, Thorne, Barbara A, Tareen, Semih U, Nicolai, Christopher J, Campbell, David J, Bannister, Richard, Stewart, Hannah J, Pearson, Laura Je, Moyer, Bentley J, Robbins, Scott H, Zielinski, Leah, Kim, Tae, Radcliffe, Pippa A, Mitrophanous, Kyriacos A, Gombotz, Wayne R, Miskin, James E, Kelley-Clarke, Brenna
Published in Molecular therapy. Methods & clinical development (01.01.2015)
Published in Molecular therapy. Methods & clinical development (01.01.2015)
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VEGF delivery with retrogradely transported lentivector prolongs survival in a mouse ALS model
Azzouz, Mimoun, Mazarakis, Nicholas D, Ralph, G. Scott, Storkebaum, Erik, Walmsley, Lucy E, Mitrophanous, Kyriacos A, Kingsman, Susan M, Carmeliet, Peter
Published in Nature (27.05.2004)
Published in Nature (27.05.2004)
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Long-term replacement of a mutated nonfunctional CNS gene: reversal of hypothalamic diabetes insipidus using an EIAV-based lentiviral vector expressing arginine vasopressin
Bienemann, Alison S, Martin-Rendon, Enca, Cosgrave, Anna S, Glover, Colin P.J, Wong, Liang-Fong, Kingsman, Susan M, Mitrophanous, Kyriacos A, Mazarakis, Nicholas D, Uney, James B
Published in Molecular therapy (01.05.2003)
Published in Molecular therapy (01.05.2003)
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Suppression of neovascularization of donor corneas by transduction with equine infectious anemia virus-based lentiviral vectors expressing endostatin and angiostatin
Parker, Maria, Bellec, Jessica, McFarland, Trevor, Scripps, Vicky, Appukuttan, Binoy, Hartzell, Matt, Yeager, Austen, Hady, Thomas, Mitrophanous, Kyriacos A, Stout, Tim, Ellis, Scott
Published in Human gene therapy (01.05.2014)
Published in Human gene therapy (01.05.2014)
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