Brain conditioning is instrumental for successful microglia reconstitution following hematopoietic stem cell transplantation
Capotondo, Alessia, Milazzo, Rita, Politi, Letterio Salvatore, Quattrini, Angelo, Palini, Alessio, Plati, Tiziana, Merella, Stefania, Nonis, Alessandro, di Serio, Clelia, Montini, Eugenio, Naldini, Luigi, Biffi, Alessandra
Published in Proceedings of the National Academy of Sciences - PNAS (11.09.2012)
Published in Proceedings of the National Academy of Sciences - PNAS (11.09.2012)
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Therapeutic efficacy of intracerebral hematopoietic stem cell gene therapy in an Alzheimer’s disease mouse model
Milazzo, Rita, Montepeloso, Annita, Kumar, Rajesh, Ferro, Francesca, Cavalca, Eleonora, Rigoni, Pietro, Cabras, Paolo, Ciervo, Yuri, Das, Sabyasachi, Capotondo, Alessia, Pellin, Danilo, Peviani, Marco, Biffi, Alessandra
Published in Nature communications (13.09.2024)
Published in Nature communications (13.09.2024)
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An innovative hematopoietic stem cell gene therapy approach benefits CLN1 disease in the mouse model
Peviani, Marco, Das, Sabyasachi, Patel, Janki, Jno‐Charles, Odella, Kumar, Rajesh, Zguro, Ana, Mathews, Tyler D, Cabras, Paolo, Milazzo, Rita, Cavalca, Eleonora, Poletti, Valentina, Biffi, Alessandra
Published in EMBO molecular medicine (11.04.2023)
Published in EMBO molecular medicine (11.04.2023)
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Biodegradable polymeric nanoparticles administered in the cerebrospinal fluid: Brain biodistribution, preferential internalization in microglia and implications for cell-selective drug release
Peviani, Marco, Capasso Palmiero, Umberto, Cecere, Francesca, Milazzo, Rita, Moscatelli, Davide, Biffi, Alessandra
Published in Biomaterials (01.07.2019)
Published in Biomaterials (01.07.2019)
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An empowered, clinically viable hematopoietic stem cell gene therapy for the treatment of multisystemic mucopolysaccharidosis type II
Das, Sabyasachi, Rruga, Fatlum, Montepeloso, Annita, Dimartino, Agnese, Spadini, Silvia, Corre, Guillaume, Patel, Janki, Cavalca, Eleonora, Ferro, Francesca, Gatti, Alessandra, Milazzo, Rita, Galy, Anne, Politi, Letterio S., Rizzardi, Gian Paolo, Vallanti, Giuliana, Poletti, Valentina, Biffi, Alessandra
Published in Molecular therapy (06.03.2024)
Published in Molecular therapy (06.03.2024)
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Intracerebroventricular delivery of hematopoietic progenitors results in rapid and robust engraftment of microglia-like cells
Capotondo, Alessia, Milazzo, Rita, Garcia-Manteiga, Jose M, Cavalca, Eleonora, Montepeloso, Annita, Garrison, Brian S, Peviani, Marco, Rossi, Derrick J, Biffi, Alessandra
Published in Science advances (01.12.2017)
Published in Science advances (01.12.2017)
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Journal Article
An innovative hematopoietic stem cell gene therapy approach benefits CLN1 disease in the mouse model
Peviani, Marco, Das, Sabyasachi, Patel, Janki, Jno-Charles, Odella, Kumar, Rajesh, Zguro, Ana, Mathews, Tyler D, Milazzo, Rita, Cavalca, Eleonora, Poletti, Valentina, Biffi, Alessandra
Published in bioRxiv (04.03.2022)
Published in bioRxiv (04.03.2022)
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Paper
COMPOSITIONS AND METHODS FOR TREATING DISEASES AND DISORDERS OF THE CENTRAL NERVOUS SYSTEM
MOSCATELLI, Davide, BIFFI, Alessandra, CAPOTONDO, Alessia, MILAZZO, Rita, PEVIANI, Marco
Year of Publication 19.04.2018
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Year of Publication 19.04.2018
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