TMPRSS6 as a Therapeutic Target for Disorders of Erythropoiesis and Iron Homeostasis
Ganz, Tomas, Nemeth, Elizabeta, Rivella, Stefano, Goldberg, Paul, Dibble, Andrew R., McCaleb, Michael L., Guo, Shuling, Monia, Brett P., Barrett, Terrance D.
Published in Advances in therapy (01.04.2023)
Published in Advances in therapy (01.04.2023)
Get full text
Journal Article
IL-4 Receptor Alpha Signaling through Macrophages Differentially Regulates Liver Fibrosis Progression and Reversal
Weng, Shih-Yen, Wang, Xiaoyu, Vijayan, Santosh, Tang, Yilang, Kim, Yong Ook, Padberg, Kornelius, Regen, Tommy, Molokanova, Olena, Chen, Tao, Bopp, Tobias, Schild, Hansjörg, Brombacher, Frank, Crosby, Jeff R., McCaleb, Michael L., Waisman, Ari, Bockamp, Ernesto, Schuppan, Detlef
Published in EBioMedicine (01.03.2018)
Published in EBioMedicine (01.03.2018)
Get full text
Journal Article
Peripheral reduction of FGFR4 with antisense oligonucleotides increases metabolic rate and lowers adiposity in diet-induced obese mice
Yu, Xing Xian, Watts, Lynnetta M, Manchem, Vara Prasad, Chakravarty, Kaushik, Monia, Brett P, McCaleb, Michael L, Bhanot, Sanjay
Published in PloS one (29.07.2013)
Published in PloS one (29.07.2013)
Get full text
Journal Article
New Potent Antihyperglycemic Agents in db/db Mice: Synthesis and Structure−Activity Relationship Studies of (4-Substituted benzyl)(trifluoromethyl)pyrazoles and -pyrazolones
Kees, Kenneth L, Fitzgerald, John J, Steiner, Kurt E, Mattes, James F, Mihan, Brenda, Tosi, Theresa, Mondoro, Diane, McCaleb, Michael L
Published in Journal of medicinal chemistry (27.09.1996)
Published in Journal of medicinal chemistry (27.09.1996)
Get full text
Journal Article
Allele-Specific Inhibition of Rhodopsin With an Antisense Oligonucleotide Slows Photoreceptor Cell Degeneration
Murray, Susan F, Jazayeri, Ali, Matthes, Michael T, Yasumura, Douglas, Yang, Haidong, Peralta, Raechel, Watt, Andy, Freier, Sue, Hung, Gene, Adamson, Peter S, Guo, Shuling, Monia, Brett P, LaVail, Matthew M, McCaleb, Michael L
Published in Investigative ophthalmology & visual science (01.10.2015)
Published in Investigative ophthalmology & visual science (01.10.2015)
Get full text
Journal Article
In vivo reduction of hepatitis B virus antigenemia and viremia by antisense oligonucleotides
Billioud, Gaetan, Kruse, Robert L, Carrillo, Melissa, Whitten-Bauer, Christina, Gao, Dacao, Kim, Aneeza, Chen, Leon, McCaleb, Michael L, Crosby, Jeffrey R, Hamatake, Robert, Hong, Zhi, Garaigorta, Urtzi, Swayze, Eric, Bissig, Karl-Dimiter, Wieland, Stefan
Published in Journal of hepatology (01.04.2016)
Published in Journal of hepatology (01.04.2016)
Get full text
Journal Article
Antisense oligonucleotide treatment ameliorates alpha-1 antitrypsin-related liver disease in mice
Guo, Shuling, Booten, Sheri L, Aghajan, Mariam, Hung, Gene, Zhao, Chenguang, Blomenkamp, Keith, Gattis, Danielle, Watt, Andrew, Freier, Susan M, Teckman, Jeffery H, McCaleb, Michael L, Monia, Brett P
Published in The Journal of clinical investigation (01.01.2014)
Published in The Journal of clinical investigation (01.01.2014)
Get full text
Journal Article
Reduction in ocular complement factor B protein in mice and monkeys by systemic administration of factor B antisense oligonucleotide
Grossman, Tamar R, Carrer, Michele, Shen, Lijiang, Johnson, Robert B, Hettrick, Lisa A, Henry, Scott P, Monia, Brett P, McCaleb, Michael L
Published in Molecular vision (10.08.2017)
Get full text
Published in Molecular vision (10.08.2017)
Journal Article
Inhibition of the alternative complement pathway by antisense oligonucleotides targeting complement factor B improves lupus nephritis in mice
Grossman, Tamar R, Hettrick, Lisa A, Johnson, Robert B, Hung, Gene, Peralta, Raechel, Watt, Andrew, Henry, Scott P, Adamson, Peter, Monia, Brett P, McCaleb, Michael L
Published in Immunobiology (1979) (01.06.2016)
Published in Immunobiology (1979) (01.06.2016)
Get full text
Journal Article
593 Antisense Oligonucleotide Reduction of Mutant Alpha-1 Antitrypsin Protein for the Treatment of Alpha-1 Antitrypsin Liver Disease
Guo, Shuling, Freier, Susan M, Booten, Sheri L, Watt, Andrew, Peralta, Raechel Q, Blomenkamp, Keith S, Teckman, Jeffrey, Monia, Brett P, McCaleb, Michael L
Published in Gastroenterology (New York, N.Y. 1943) (01.05.2012)
Published in Gastroenterology (New York, N.Y. 1943) (01.05.2012)
Get full text
Journal Article
Studies on New Acidic Azoles as Glucose-Lowering Agents in Obese, Diabetic db/db Mice
Kees, Kenneth L, Caggiano, Thomas J, Steiner, Kurt E, Fitzgerald, John J, Kates, Michael J, Christos, Thomas E, Kulishoff, John M, Moore, Robin D, McCaleb, Michael L
Published in Journal of medicinal chemistry (01.02.1995)
Published in Journal of medicinal chemistry (01.02.1995)
Get full text
Journal Article
Clinical Trial Design for Alpha-1 Antitrypsin Deficiency: A Model for Rare Diseases
Wanner, Adam, Groft, Stephen C, Teagarden, J Russell, Krischer, Jeffrey, Davis, Barry R, Coffey, Christopher S, Hickam, David H, Teckman, Jeffrey, Nelson, David R, McCaleb, Michael L, Loomba, Rohit, Strange, Charlie, Sandhaus, Robert A, Brantly, Mark, Edelman, Jonathan M, Farrugia, Albert
Published in Chronic obstructive pulmonary diseases (28.04.2015)
Published in Chronic obstructive pulmonary diseases (28.04.2015)
Get full text
Journal Article
Identification of a Novel Hypothalamic Neuropeptide Y Receptor Associated with Feeding Behavior
Yinghe Hu, Brian T. Bloomquist, Linda J. Cornfield, Lynn B. DeCarr, Jaime R. Flores-Riveros, Lizbeth Friedman, Peiling Jiang, Lore Lewis-Higgins, Yola Sadlowski, Jean Schaefer, Nelson Velazquez, Michael L. McCaleb
Published in The Journal of biological chemistry (18.10.1996)
Published in The Journal of biological chemistry (18.10.1996)
Get full text
Journal Article
Synthesis and antihyperglycemic activity of novel 5-(naphthalenylsulfonyl)-2,4-thiazolidinediones
Zask, Arie, Jirkovsky, Ivo, Nowicki, James W, McCaleb, Michael L
Published in Journal of medicinal chemistry (01.05.1990)
Published in Journal of medicinal chemistry (01.05.1990)
Get full text
Journal Article
Antihyperglycemic activity of novel substituted 3H-1,2,3,5-oxathiadiazole 2-oxides
Ellingboe, John W, Alessi, Thomas R, Dolak, Terence M, Nguyen, Thomas T, Tomer, John D, Guzzo, Frieda, Bagli, Jehan F, McCaleb, Michael L
Published in Journal of medicinal chemistry (01.04.1992)
Published in Journal of medicinal chemistry (01.04.1992)
Get full text
Journal Article