Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR
Cehajic-Kapetanovic, Jasmina, Xue, Kanmin, Martinez-Fernandez de la Camara, Cristina, Nanda, Anika, Davies, Alexandra, Wood, Laura J., Salvetti, Anna Paola, Fischer, M. Dominik, Aylward, James W., Barnard, Alun R., Jolly, Jasleen K., Luo, Edmond, Lujan, Brandon J., Ong, Tuyen, Girach, Aniz, Black, Graeme C. M., Gregori, Ninel Z., Davis, Janet L., Rosa, Potyra R., Lotery, Andrew J., Lam, Byron L., Stanga, Paulo E., MacLaren, Robert E.
Published in Nature medicine (01.03.2020)
Published in Nature medicine (01.03.2020)
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Journal Article
Retinal gene therapy in X-linked retinitis pigmentosa caused by mutations in RPGR: Results at 6 months in a first in human clinical trial
Cehajic-Kapetanovic, Jasmina, Xue, Kanmin, de la Camara, Cristina Martinez-Fernandez, Nanda, Anika, Davies, Alexandra, Wood, Laura J, Salvetti, Anna Paola, Fischer, M Dominik, Aylward, James W, Barnard, Alun R, Jolly, Jasleen K, Luo, Edmond, Lujan, Brandon J, Ong, Tuyen, Girach, Aniz, Black, Graeme CM, Gregori, Ninel Z, Davis, Janet L, Rosa, Potyra R, Lotery, Andrew J, Lam, Byron L, Stanga, Paulo E, MacLaren, Robert E
Published in Nature medicine (24.02.2020)
Published in Nature medicine (24.02.2020)
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Journal Article