Improved CRISPR genome editing using small highly active and specific engineered RNA-guided nucleases
Schmidt, Moritz J., Gupta, Ashish, Bednarski, Christien, Gehrig-Giannini, Stefanie, Richter, Florian, Pitzler, Christian, Gamalinda, Michael, Galonska, Christina, Takeuchi, Ryo, Wang, Kui, Reiss, Caroline, Dehne, Kerstin, Lukason, Michael J., Noma, Akiko, Park-Windhol, Cindy, Allocca, Mariacarmela, Kantardzhieva, Albena, Sane, Shailendra, Kosakowska, Karolina, Cafferty, Brian, Tebbe, Jan, Spencer, Sarah J., Munzer, Scott, Cheng, Christopher J., Scaria, Abraham, Scharenberg, Andrew M., Cohnen, André, Coco, Wayne M.
Published in Nature communications (09.07.2021)
Published in Nature communications (09.07.2021)
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Addendum to: Improved CRISPR genome editing using small highly active and specific engineered RNA-guided nucleases
Schmidt, Moritz J., Gupta, Ashish, Bednarski, Christien, Gehrig-Giannini, Stefanie, Richter, Florian, Pitzler, Christian, Gamalinda, Michael, Galonska, Christina, Takeuchi, Ryo, Wang, Kui, Reiss, Caroline, Dehne, Kerstin, Lukason, Michael J., Noma, Akiko, Park-Windhol, Cindy, Allocca, Mariacarmela, Kantardzhieva, Albena, Sane, Shailendra, Kosakowska, Karolina, Cafferty, Brian, Tebbe, Jan, Spencer, Sarah J., Munzer, Scott, Cheng, Christopher J., Scaria, Abraham, Scharenberg, Andrew M., Cohnen, André, Coco, Wayne M.
Published in Nature communications (13.06.2023)
Published in Nature communications (13.06.2023)
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Preexisting Immunity and Low Expression in Primates Highlight Translational Challenges for Liver-directed AAV8-mediated Gene Therapy
Hurlbut, Gregory D, Ziegler, Robin J, Nietupski, Jennifer B, Foley, Joseph W, Woodworth, Lisa A, Meyers, Elizabeth, Bercury, Scott D, Pande, Nilesh N, Souza, David W, Bree, Mark P, Lukason, Michael J, Marshall, John, Cheng, Seng H, Scheule, Ronald K
Published in Molecular therapy (01.11.2010)
Published in Molecular therapy (01.11.2010)
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Rationally designed AAV2 and AAVrh8R capsids provide improved transduction in the retina and brain
Sullivan, Jennifer A., Stanek, Lisa M., Lukason, Michael J., Bu, Jie, Osmond, Shayla R., Barry, Elizabeth A., O’Riordan, Catherine R., Shihabuddin, Lamya S., Cheng, Seng H., Scaria, Abraham
Published in Gene therapy (01.06.2018)
Published in Gene therapy (01.06.2018)
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Optimization of formulations and conditions for the aerosol delivery of functional cationic lipid:DNA complexes
Eastman, S J, Tousignant, J D, Lukason, M J, Murray, H, Siegel, C S, Constantino, P, Harris, D J, Cheng, S H, Scheule, R K
Published in Human gene therapy (10.02.1997)
Published in Human gene therapy (10.02.1997)
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Adenoviral Vector Expressing ICP47 Inhibits Adenovirus-Specific Cytotoxic T Lymphocytes in Nonhuman Primates
Scaria, Abraham, Sullivan, Jennifer A., St. George, Judith A., Kaplan, Johanne M., Lukason, Michael J., Morris, James E., Plog, Malinda, Nicolette, Charles, Gregory, Richard J., Wadsworth, Samuel C.
Published in Molecular therapy (01.11.2000)
Published in Molecular therapy (01.11.2000)
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A concentrated and stable aerosol formulation of cationic lipid:DNA complexes giving high-level gene expression in mouse lung
Eastman, S J, Lukason, M J, Tousignant, J D, Murray, H, Lane, M D, St George, J A, Akita, G Y, Cherry, M, Cheng, S H, Scheule, R K
Published in Human gene therapy (10.04.1997)
Published in Human gene therapy (10.04.1997)
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