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Río, Paula, Navarro, Susana, Wang, Wei, Sánchez-Domínguez, Rebeca, Pujol, Roser M, Segovia, José C, Bogliolo, Massimo, Merino, Eva, Wu, Ning, Salgado, Rocío, Lamana, María L, Yañez, Rosa M, Casado, José A, Giménez, Yari, Román-Rodríguez, Francisco J, Álvarez, Lara, Alberquilla, Omaira, Raimbault, Anna, Guenechea, Guillermo, Lozano, M Luz, Cerrato, Laura, Hernando, Miriam, Gálvez, Eva, Hladun, Raquel, Giralt, Irina, Barquinero, Jordi, Galy, Anne, García de Andoín, Nagore, López, Ricardo, Catalá, Albert, Schwartz, Jonathan D, Surrallés, Jordi, Soulier, Jean, Schmidt, Manfred, Díaz de Heredia, Cristina, Sevilla, Julián, Bueren, Juan A
Published in Nature medicine (01.09.2019)
Published in Nature medicine (01.09.2019)
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Generation of dyskeratosis congenita-like hematopoietic stem cells through the stable inhibition of DKC1
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Development of lentiviral vectors with optimized transcriptional activity for the gene therapy of patients with Fanconi anemia
González-Murillo, Africa, Lozano, M Luz, Alvarez, Lara, Jacome, Ariana, Almarza, Elena, Navarro, Susana, Segovia, José C, Hanenberg, Helmut, Guenechea, Guillermo, Bueren, Juan A, Río, Paula
Published in Human gene therapy (01.05.2010)
Published in Human gene therapy (01.05.2010)
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Brief Report: Impaired Cell Reprogramming in Nonhomologous End Joining Deficient Cells
Molina‐Estevez, F. Javier, Lozano, M. Luz, Navarro, Susana, Torres, Yaima, Grabundzija, Ivana, Ivics, Zoltan, Samper, Enrique, Bueren, Juan A., Guenechea, Guillermo
Published in Stem cells (Dayton, Ohio) (01.08.2013)
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Lentiviral-mediated Genetic Correction of Hematopoietic and Mesenchymal Progenitor Cells From Fanconi Anemia Patients
Jacome, Ariana, Navarro, Susana, Río, Paula, Yañez, Rosa M, González-Murillo, Africa, Luz Lozano, M, Lamana, Maria Luisa, Sevilla, Julian, Olive, Teresa, Diaz-Heredia, Cristina, Badell, Isabel, Estella, Jesus, Madero, Luis, Guenechea, Guillermo, Casado, José, Segovia, Jose C, Bueren, Juan A
Published in Molecular therapy (01.06.2009)
Published in Molecular therapy (01.06.2009)
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Lentiviral vector integration sites in human NOD/SCID repopulating cells
Laufs, Stephanie, Guenechea, Guillermo, Gonzalez-Murillo, Africa, Zsuzsanna Nagy, K., Luz Lozano, M., del Val, Coral, Jonnakuty, Sunitha, Hotz-Wagenblatt, Agnes, Jens Zeller, W., Bueren, Juan A., Fruehauf, Stefan
Published in The journal of gene medicine (01.10.2006)
Published in The journal of gene medicine (01.10.2006)
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Posterior reversible leukoencephalopathy syndrome induced by L-asparaginase in a teenage female diagnosed with acute lymphoblastic leukemia
Titos-Arcos, José C, León-Villar, Josefa, Amigo-Lozano, M Luz, Muiña-Juárez, Begoña
Published in Revista de neurologiá (01.01.2011)
Published in Revista de neurologiá (01.01.2011)
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Gene Therapy for Lad-I Immunodeficiency: Preclinical Evaluation of HSC Transduction Under Optimized GMP-Conditions
Almarza, Elena, Mesa-Núñez, Cristina, Damián, Carlos, Fernández-García, María, Díez-Cabezas, Begoña, Lozano, M Luz, Rio, Paula, Yañez, Rosa M, Law, Ken, Beard, Brian C, Schwartz, Jonathan D, Bueren, Juan A.
Published in Blood (13.11.2019)
Published in Blood (13.11.2019)
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Lentiviral-Mediated Gene Therapy in Fanconi Anemia-A Mice Reveals Long-Term Engraftment and Continuous Turnover of Corrected HSCs
Molina-Estevez, F Javier, Nowrouzi, Ali, Lozano, M Luz, Galy, Anne, Charrier, Sabine, von Kalle, Christof, Guenechea, Guillermo, Bueren, Juan A, Schmidt, Manfred
Published in Current gene therapy (01.01.2015)
Published in Current gene therapy (01.01.2015)
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Optimization of lentiviral vectors for the gene therapy of fanconi anemia
Gonzalez-Murillo, Africa, Lozano, M. Luz, Molina-Estevez, Javier, Almarza, Elena, Aldea, Montserrat, Alvarez, Lara, Guenechea, Guillermo, Bueren, Juan A., Rio, Paula
Published in Blood cells, molecules, & diseases (01.03.2008)
Published in Blood cells, molecules, & diseases (01.03.2008)
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Síndrome de leucoencefalopatía posterior reversible inducida por L-asparaginasa en una adolescente diagnosticada de leucemia linfoblástica aguda
Titos Arcos, José Carlos, León Villar, Josefa, Amigo Lozano, María Luz, Muiña Juárez, Begoña
Published in Revista de neurologiá (2011)
Published in Revista de neurologiá (2011)
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Generation of Dyskeratosis Congenita-like Hematopoietic Stem Cells through the Stable Inhibition of DKC1
Carrascoso-Rubio, Carlos, Zittersteijn, Hidde A, Pintado-Berninches, Laura, Fernández-Varas, Beatriz, M. Luz Lozano, Manguan-Garcia, Cristina, Sastre, Leandro, Bueren, Juan A, Perona, Rosario, Guenechea, Guillermo
Published in Stem Cell Research & Therapy (05.01.2021)
Published in Stem Cell Research & Therapy (05.01.2021)
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