Retinoblastoma protein represses transcription by recruiting a histone deacetylase
Harel-Bellan, A, Magnaghi-Jaulin, L, Groisman, R, Naguibneva, I, Robin, P, Lorain, S, Le Villain, J. P, Troalen, F, Trouche, D
Published in Nature (London) (05.02.1998)
Published in Nature (London) (05.02.1998)
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Journal Article
Gene therapy via trans-splicing for LMNA -related congenital muscular dystrophy (L-CMD)
Azibani, F, Arandel, L, Beuvin, M, Jollet, A, Prudhon, B, Lorain, S, Bertrand, A, Bonne, G
Published in Neuromuscular disorders : NMD (01.10.2015)
Published in Neuromuscular disorders : NMD (01.10.2015)
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Journal Article
P.20.8 AAV genome loss from dystrophic mouse muscles during AAV-U7snRNA-mediated exon skipping therapy
Hir, M. Le, Goyenvalle, A, Peccate, C, Précigout, G, Davies, K.E, Voit, T, Garcia, L, Lorain, S
Published in Neuromuscular disorders : NMD (01.10.2013)
Published in Neuromuscular disorders : NMD (01.10.2013)
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Journal Article
G.P.93
Maniangou, B, Cadot, B, Dorna, M, Holtzman, I, Pontoriero, M, Jollet, A, Mamchaoui, K, Lorain, S, Voit, T, Pietri-Rouxel, F, Benkhelifa-Ziyyat, S
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
P4.51 Correction of FKRP function via RNA trans -splicing
Farmer, S, Lorain, S, Thrasher, A, Garcia, L, Muntoni, F, Conti, F
Published in Neuromuscular disorders : NMD (01.10.2011)
Published in Neuromuscular disorders : NMD (01.10.2011)
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Journal Article
P04 Correction of FKRP function via RNA trans-splicing
Farmer, S, Lorain, S, Thrasher, A, Garcia, L, Muntoni, F, Conti, F
Published in Neuromuscular disorders : NMD (2011)
Published in Neuromuscular disorders : NMD (2011)
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Journal Article
O.14 Exon exchange approach to repair Duchenne dystrophin transcripts
Lorain, S, Peccate, C, Le Hir, M, Griffith, G, Voit, T, Garcia, L
Published in Neuromuscular disorders : NMD (01.10.2010)
Published in Neuromuscular disorders : NMD (01.10.2010)
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Journal Article
T.P.1.05 Trans-splicing approaches to repair Duchenne dystrophin transcripts
Lorain, S, Peccate, C, Griffith, G, Voit, T, Garcia, L
Published in Neuromuscular disorders : NMD (01.09.2009)
Published in Neuromuscular disorders : NMD (01.09.2009)
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Journal Article
DMD TREATMENT: P.334PPMO pre-treatment is beneficial for AAV-based gene therapy in Duchenne muscular dystrophy
Forand, A., Muchir, A., Mougenot, N., Sevoz-Couche, C., Peccate, C., Lemaitre, M., Wood, M., Lorain, S., Piétri-Rouxel, F.
Published in Neuromuscular disorders : NMD (01.10.2019)
Published in Neuromuscular disorders : NMD (01.10.2019)
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Journal Article
DMD TREATMENT
Forand, A., Muchir, A., Mougenot, N., Sevoz-Couche, C., Peccate, C., Lemaitre, M., Wood, M., Lorain, S., Piétri-Rouxel, F.
Published in Neuromuscular disorders : NMD (01.10.2019)
Published in Neuromuscular disorders : NMD (01.10.2019)
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Journal Article
G.P.314 - Gene therapy via trans-splicing for LMNA-related congenital muscular dystrophy (L-CMD)
Azibani, F., Arandel, L., Beuvin, M., Jollet, A., Prudhon, B., Lorain, S., Bertrand, A., Bonne, G.
Published in Neuromuscular disorders : NMD (01.10.2015)
Published in Neuromuscular disorders : NMD (01.10.2015)
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Journal Article
P.237 - MicroRNAs involved in nNOS regulation in dystrophic context
Guilbaud, M., Gentil, C., Holtzmann, I., Gruszczynski, C., Falcone, S., Peccate, C., Benkhelifa-Ziyyat, S., Lorain, S., Aurade, F., Jeanson-Leh, L., Piétri-Rouxel, F.
Published in Neuromuscular disorders : NMD (01.10.2017)
Published in Neuromuscular disorders : NMD (01.10.2017)
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Journal Article
MicroRNAs involved in nNOS regulation in dystrophic context
Guilbaud, M., Gentil, C., Holtzmann, I., Gruszczynski, C., Falcone, S., Peccate, C., Benkhelifa-Ziyyat, S., Lorain, S., Aurade, F., Jeanson-Leh, L., Piétri-Rouxel, F.
Published in Neuromuscular disorders : NMD (01.10.2017)
Published in Neuromuscular disorders : NMD (01.10.2017)
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Journal Article
Delivery is key: lessons learnt from developing splice‐switching antisense therapies
Godfrey, Caroline, Desviat, Lourdes R, Smedsrød, Bård, Piétri‐Rouxel, France, Denti, Michela A, Disterer, Petra, Lorain, Stéphanie, Nogales‐Gadea, Gisela, Sardone, Valentina, Anwar, Rayan, EL Andaloussi, Samir, Lehto, Taavi, Khoo, Bernard, Brolin, Camilla, Roon‐Mom, Willeke MC, Goyenvalle, Aurélie, Aartsma‐Rus, Annemieke, Arechavala‐Gomeza, Virginia
Published in EMBO molecular medicine (01.05.2017)
Published in EMBO molecular medicine (01.05.2017)
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Journal Article
G.P.93 : Entry and intracellular trafficking of adeno-associated viral 8 (AAV8) vector in DMD muscular cells
Maniangou, B., Cadot, B., Dorna, M., Holtzman, I., Pontoriero, M., Jollet, A., Mamchaoui, K., Lorain, S., Voit, T., Pietri-Rouxel, F., Benkhelifa-Ziyyat, S.
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
Core Histones and HIRIP3, a Novel Histone-Binding Protein, Directly Interact with WD Repeat Protein HIRA
Lorain, S, Quivy, J P, Monier-Gavelle, F, Scamps, C, Lécluse, Y, Almouzni, G, Lipinski, M
Published in Molecular and Cellular Biology (01.09.1998)
Published in Molecular and Cellular Biology (01.09.1998)
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