Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease
Nicolino, Marc, Byrne, Barry, Wraith, J Edmund, Leslie, Nancy, Mandel, Hanna, Freyer, David R, Arnold, Georgianne L, Pivnick, Eniko K, Ottinger, C J, Robinson, Peter H, Loo, John-Charles A, Smitka, Martin, Jardine, Philip, Tatò, Luciano, Chabrol, Brigitte, McCandless, Shawn, Kimura, Shigemi, Mehta, L, Bali, Deeksha, Skrinar, Alison, Morgan, Claire, Rangachari, Lakshmi, Corzo, Deya, Kishnani, Priya S
Published in Genetics in medicine (01.03.2009)
Published in Genetics in medicine (01.03.2009)
Get full text
Journal Article