Precise correction of the dystrophin gene in duchenne muscular dystrophy patient induced pluripotent stem cells by TALEN and CRISPR-Cas9
Li, Hongmei Lisa, Fujimoto, Naoko, Sasakawa, Noriko, Shirai, Saya, Ohkame, Tokiko, Sakuma, Tetsushi, Tanaka, Michihiro, Amano, Naoki, Watanabe, Akira, Sakurai, Hidetoshi, Yamamoto, Takashi, Yamanaka, Shinya, Hotta, Akitsu
Published in Stem cell reports (13.01.2015)
Published in Stem cell reports (13.01.2015)
Get full text
Journal Article
Concordant but Varied Phenotypes among Duchenne Muscular Dystrophy Patient-Specific Myoblasts Derived using a Human iPSC-Based Model
Choi, In Young, Lim, HoTae, Estrellas, Kenneth, Mula, Jyothi, Cohen, Tatiana V., Zhang, Yuanfan, Donnelly, Christopher J., Richard, Jean-Philippe, Kim, Yong Jun, Kim, Hyesoo, Kazuki, Yasuhiro, Oshimura, Mitsuo, Li, Hongmei Lisa, Hotta, Akitsu, Rothstein, Jeffrey, Maragakis, Nicholas, Wagner, Kathryn R., Lee, Gabsang
Published in Cell reports (Cambridge) (07.06.2016)
Published in Cell reports (Cambridge) (07.06.2016)
Get full text
Journal Article
Genetic correction using engineered nucleases for gene therapy applications
Lisa Li, Hongmei, Nakano, Takao, Hotta, Akitsu
Published in Development, growth & differentiation (01.01.2014)
Published in Development, growth & differentiation (01.01.2014)
Get full text
Journal Article
Efficient genomic correction methods in human iPS cells using CRISPR–Cas9 system
Li, Hongmei Lisa, Gee, Peter, Ishida, Kentaro, Hotta, Akitsu
Published in Methods (San Diego, Calif.) (15.05.2016)
Published in Methods (San Diego, Calif.) (15.05.2016)
Get full text
Journal Article
The Epithelial Sodium Channel Is a Modifier of the Long-Term Nonprogressive Phenotype Associated with F508del CFTR Mutations
Agrawal, Pankaj B, Wang, Ruobing, Li, Hongmei Lisa, Schmitz-Abe, Klaus, Simone-Roach, Chantelle, Chen, Jingxin, Shi, Jiahai, Louie, Tin, Sheng, Shaohu, Towne, Meghan C, Brainson, Christine F, Matthay, Michael A, Kim, Carla F, Bamshad, Michael, Emond, Mary J, Gerard, Norma P, Kleyman, Thomas R, Gerard, Craig
Published in American journal of respiratory cell and molecular biology (01.12.2017)
Published in American journal of respiratory cell and molecular biology (01.12.2017)
Get full text
Journal Article
Pluripotent Stem Cell Model of Nakajo-Nishimura Syndrome Untangles Proinflammatory Pathways Mediated by Oxidative Stress
Honda-Ozaki, Fumiko, Terashima, Madoka, Niwa, Akira, Saiki, Norikazu, Kawasaki, Yuri, Ito, Haruna, Hotta, Akitsu, Nagahashi, Ayako, Igura, Koichi, Asaka, Isao, Li, Hongmei Lisa, Yanagimachi, Masakatsu, Furukawa, Fukumi, Kanazawa, Nobuo, Nakahata, Tatsutoshi, Saito, Megumu K.
Published in Stem cell reports (05.06.2018)
Published in Stem cell reports (05.06.2018)
Get full text
Journal Article