Isogenic GAA-KO Murine Muscle Cell Lines Mimicking Severe Pompe Mutations as Preclinical Models for the Screening of Potential Gene Therapy Strategies
Aguilar-González, Araceli, González-Correa, Juan Elías, Barriocanal-Casado, Eliana, Ramos-Hernández, Iris, Lerma-Juárez, Miguel A, Greco, Sara, Rodríguez-Sevilla, Juan José, Molina-Estévez, Francisco Javier, Montalvo-Romeral, Valle, Ronzitti, Giuseppe, Sánchez-Martín, Rosario María, Martín, Francisco, Muñoz, Pilar
Published in International journal of molecular sciences (04.06.2022)
Published in International journal of molecular sciences (04.06.2022)
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