Maternal imprinting of the mouse Snrpn gene and conserved linkage homology with the human Prader-Willi syndrome region
Leff, Stuart E, Brannan, Camilynn I, Reed, Martha L, Özçelik, Tayfun, Francke, Uta, Copeland, Neal G, Jenkins, Nancy A
Published in Nature genetics (01.12.1992)
Published in Nature genetics (01.12.1992)
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Regulation of gene expression in vivo following transduction by two separate rAAV vectors
Rendahl, Katherine G, Leff, Stuart E, Otten, Gillis R, Spratt, S. Kaye, Bohl, Delphine, Van Roey, Melinda, Donahue, Brian A, Cohen, Lawrence K, Mandel, Ronald J, Danos, Olivier, Snyder, Richard O
Published in Nature biotechnology (01.08.1998)
Published in Nature biotechnology (01.08.1998)
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A candidate mouse model for Prader-Willi syndrome which shows an absence of Snrpn expression
Cattanach, Bruce M, Barr, Jacqueline A, Evans, Edward P, Burtenshaw, Michael, Beechey, Colin V, Leff, Stuart E, Brannan, Camilynn I, Copeland, Neal G, Jenkins, Nancy A, Jones, Janet
Published in Nature genetics (01.12.1992)
Published in Nature genetics (01.12.1992)
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Journal Article
Age-related decreases in GTP-cyclohydrolase-I immunoreactive neurons in the monkey and human substantia nigra
Chen, Er-Yun, Kallwitz, Eric, Leff, Stuart E., Cochran, Elizabeth J., Mufson, Elliott J., Kordower, Jeffrey H., Mandel, Ronald J.
Published in Journal of comparative neurology (1911) (30.10.2000)
Published in Journal of comparative neurology (1911) (30.10.2000)
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Expression in Brain of a Messenger RNA Encoding a Novel Neuropeptide Homologous to Calcitonin Gene-Related Peptide
Amara, Susan G., Arriza, Jeffrey L., Leff, Stuart E., Swanson, Larry W., Evans, Ronald M., Rosenfeld, Michael G.
Published in Science (American Association for the Advancement of Science) (13.09.1985)
Published in Science (American Association for the Advancement of Science) (13.09.1985)
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Practical Aspects of the Development ofex Vivoandin VivoGene Therapy for Parkinson's Disease
Bankiewicz, Krzysztof S., Leff, Stuart E., Nagy, Dea, Jungles, Steve, Rokovich, Joseph, Spratt, Kaye, Cohen, Lawrence, Libonati, Michele, Snyder, Richard O., Mandel, Ronald J.
Published in Experimental neurology (01.03.1997)
Published in Experimental neurology (01.03.1997)
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In vivo L-DOPA production by genetically modified primary rat fibroblast or 9L gliosarcoma cell grafts via coexpression of GTPcyclohydrolase I with tyrosine hydroxylase
LEFF, S. E, RENDAHL, K. G, SPRATT, S. K, KANG, U. J, MANDEL, R. J
Published in Experimental neurology (01.06.1998)
Published in Experimental neurology (01.06.1998)
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Progress in direct striatal delivery of L-dopa via gene therapy for treatment of Parkinson's disease using recombinant adeno-associated viral vectors
MANDEL, R. J, RENDAHL, K. G, SNYDER, R. O, LEFF, S. E
Published in Experimental neurology (01.09.1999)
Published in Experimental neurology (01.09.1999)
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Conference Proceeding
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Practical aspects of the development of ex vivo and in vivo gene therapy for Parkinson's disease
BANKIEWICZ, K. S, LEFF, S. E, NAGY, D, JUNGLES, S, ROKOVICH, J, SPRATT, K, COHEN, L, LIBONATI, M, SNYDER, R. O, MANDEL, R. J
Published in Experimental neurology (01.03.1997)
Published in Experimental neurology (01.03.1997)
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Conference Proceeding
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Progress in Direct Striatal Delivery of [formula omitted]-Dopa via Gene Therapy for Treatment of Parkinson's Disease Using Recombinant Adeno-Associated Viral Vectors
Mandel, Ronald J., Rendahl, K.G., Snyder, Richard O., Leff, Stuart E.
Published in Experimental neurology (01.09.1999)
Published in Experimental neurology (01.09.1999)
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In VivoL-DOPA Production by Genetically Modified Primary Rat Fibroblast or 9L Gliosarcoma Cell Grafts via Coexpression of GTPcyclohydrolase I with Tyrosine Hydroxylase
Leff, Stuart E., Rendahl, Katherine G., Spratt, S.Kaye, Kang, Un J., Mandel, Ronald J.
Published in Experimental neurology (01.06.1998)
Published in Experimental neurology (01.06.1998)
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Dopamine Receptor Turnover Rates in Rat Striatum are Age-Dependent
Leff, Stuart E., Gariano, Ray, Creese, Ian
Published in Proceedings of the National Academy of Sciences - PNAS (01.06.1984)
Published in Proceedings of the National Academy of Sciences - PNAS (01.06.1984)
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