Intravenous SBC-103, a recombinant human alpha-N-acetylglucosaminidase reduces CNS heparan sulfate content in a mucopolysaccharidosis type IIIB mouse model
Rutkowski, Joseph V., Harbert, Kari, Xu, Hao, Hu, Wei, Renninger, Matthew, Leavitt, Mark C.C., Chen, Qinming, Rojas-Caro, Sandra, Quinn, Anthony G.
Published in Molecular genetics and metabolism (01.02.2014)
Published in Molecular genetics and metabolism (01.02.2014)
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