Hepatic cholesteryl ester accumulation in lysosomal acid lipase deficiency: Non-invasive identification and treatment monitoring by magnetic resonance
Thelwall, Peter E, Smith, Fiona E, Leavitt, Mark C, Canty, David, Hu, Wei, Hollingsworth, Kieren G, Thoma, Christian, Trenell, Michael I, Taylor, Roy, Rutkowski, Joseph V, Blamire, Andrew M, Quinn, Anthony G
Published in Journal of hepatology (01.09.2013)
Published in Journal of hepatology (01.09.2013)
Get full text
Journal Article
Intracellular Immunization of Human Fetal Cord Blood Stem/Progenitor Cells with a Ribozyme Against Human Immunodeficiency Virus Type 1
Yu, Mang, Leavitt, Mark C., Maruyama, Midori, Yamada, Osamu, Young, Dennis, Ho, Anthony D., Wong-Staal, Flossie
Published in Proceedings of the National Academy of Sciences - PNAS (31.01.1995)
Published in Proceedings of the National Academy of Sciences - PNAS (31.01.1995)
Get full text
Journal Article
Evaluation of blood–brain barrier integrity and structural abnormalities in MPS IIIB patients using cerebrospinal fluid/serum albumin index (CSF-AI) and multimodal MRI
Vijay, Suresh, Parker, Geoff, Roberts, Caleb, Riches, Victoria, Leavitt, Mark C., Rossomando, Anthony, Kemp, Tracey, Quinn, Anthony G., Patki, Kiran C., Rojas-Caro, Sandra
Published in Molecular genetics and metabolism (01.02.2015)
Published in Molecular genetics and metabolism (01.02.2015)
Get full text
Journal Article
Co-localization of macrophage aggregation and fibrosis in a rat model of lysosomal acid lipase (LAL) deficiency and the effects of enzyme replacement with SBC-102
Rutkowski, Joseph V., Burt, Alastair D., Leavitt, Mark C., Hu, Wei, Canty, David, Quinn, Anthony G.
Published in Molecular genetics and metabolism (01.02.2013)
Published in Molecular genetics and metabolism (01.02.2013)
Get full text
Journal Article
A glycosylated recombinant human granulocyte colony stimulating factor produced in a novel protein production system (AVI-014) in healthy subjects: a first-in human, single dose, controlled study
Varki, Roslyn, Pequignot, Ed, Leavitt, Mark C, Ferber, Andres, Kraft, Walter K
Published in BMC clinical pharmacology (28.01.2009)
Published in BMC clinical pharmacology (28.01.2009)
Get full text
Journal Article
Transfer of an anti-HIV-1 ribozyme gene into primary human lymphocytes
Leavitt, M C, Yu, M, Yamada, O, Kraus, G, Looney, D, Poeschla, E, Wong-Staal, F
Published in Human gene therapy (01.09.1994)
Published in Human gene therapy (01.09.1994)
Get more information
Journal Article
Activity and Cleavage Site Specificity of an Anti-HIV-1 Hairpin Ribozyme in Human T Cells
Yamada, Osamu, Kraus, Günter, Leavitt, Mark C., Yu, Mang, Wong-Staal, Flossie
Published in Virology (New York, N.Y.) (15.11.1994)
Published in Virology (New York, N.Y.) (15.11.1994)
Get full text
Journal Article
In vitro and in vivo characterization of a second functional hairpin ribozyme against HIV-1
Yu, Mang, Poeschla, Eric, Yamada, Osamu, Degrandis, Paula, Leavitt, Mark C., Heusch, Marina, Yees, Jiing-Kuala, Wong-Stahl, Flossie, Hampel, Arnold
Published in Virology (New York, N.Y.) (1995)
Published in Virology (New York, N.Y.) (1995)
Get full text
Journal Article
T5 DNA Polymerase: Structural-Functional Relationships to Other DNA Polymerases
Leavitt, Mark C., Ito, Junetsu
Published in Proceedings of the National Academy of Sciences - PNAS (01.06.1989)
Published in Proceedings of the National Academy of Sciences - PNAS (01.06.1989)
Get full text
Journal Article
Bacteriophage PRD1 DNA Polymerase: Evolution of DNA Polymerases
Jung, Guhung, Leavitt, Mark C., Hsieh, Jui-Cheng, Ito, Junetsu
Published in Proceedings of the National Academy of Sciences - PNAS (01.12.1987)
Published in Proceedings of the National Academy of Sciences - PNAS (01.12.1987)
Get full text
Journal Article
Identification and mapping of inhibitory sequences in the human immunodeficiency virus type 2 vif gene
Reddy, T R, Kraus, G, Suhasini, M, Leavitt, M C, Wong-Staal, F
Published in Journal of Virology (01.08.1995)
Published in Journal of Virology (01.08.1995)
Get full text
Journal Article
Primary structure of the DNA terminal protein of bacteriophage PRD1
JUI-CHENG HSIEH, GUHUNG JUNG, LEAVITT, M. C, ITO, J
Published in Nucleic acids research (11.11.1987)
Published in Nucleic acids research (11.11.1987)
Get full text
Journal Article
Mutagenesis of a highly conserved lysine 340 of the PRD1 DNA polymerase
Zhu, Weiguo, Leavitt, Mark C., Jung, Guhung, Ito, Junetsu
Published in Biochimica et biophysica acta (18.10.1994)
Published in Biochimica et biophysica acta (18.10.1994)
Get full text
Journal Article