Translating an HPFH-Mechanism into Oral Small Molecule Therapy for Beta-Hemoglobinopathies: Clinical Proof-of-Principle
Molokie, Robert, Saraf, Santosh L., Krauz, Lani, Pacini, Michael, Chan, David, Aziz-Bradley, Alana, Gansari, Rebeca, Hassan, Taif, Woost, Philip, Jacobberger, James, Gordeuk, Victor R., Lavelle, Donald E., DeSimone, Joseph, Saunthararajah, Yogenthiran
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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