Safety, pharmacokinetics and sialic acid production after oral administration of N-acetylmannosamine (ManNAc) to subjects with GNE myopathy
Xu, Xin, Wang, Amy Q., Latham, Lea L., Celeste, Frank, Ciccone, Carla, Malicdan, May Christine, Goldspiel, Barry, Terse, Pramod, Cradock, James, Yang, Nora, Yorke, Selwyn, McKew, John C., Gahl, William A., Huizing, Marjan, Carrillo, Nuria
Published in Molecular genetics and metabolism (01.09.2017)
Published in Molecular genetics and metabolism (01.09.2017)
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