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Published in Orphanet journal of rare diseases (27.04.2019)
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Published in Netherlands journal of medicine (01.07.2020)
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Published in Netherlands journal of medicine (01.07.2020)
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Published in European journal of clinical pharmacology (01.04.2014)
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Published in JIMD reports (01.11.2022)
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Published in JIMD Reports, Volume 27 (01.01.2016)
Published in JIMD Reports, Volume 27 (01.01.2016)
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Published in The journal of clinical endocrinology and metabolism (01.11.2001)
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Published in The journal of clinical endocrinology and metabolism (01.05.1998)
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Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria
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