Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors
Sabatino, Denise E, Lange, Amy M, Altynova, Ekaterina S, Sarkar, Rita, Zhou, Shangzhen, Merricks, Elizabeth P, Franck, Helen G, Nichols, Timothy C, Arruda, Valder R, Kazazian Jr, Haig H
Published in Molecular therapy (01.03.2011)
Published in Molecular therapy (01.03.2011)
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Light Chain of Factor VIII Is Sufficient for Accelerating Cleavage of von Willebrand Factor by ADAMTS13 Metalloprotease
Cao, Wenjing, Sabatino, Denise E., Altynova, Ekaterina, Lange, Amy M., Casina, Veronica C., Camire, Rodney M., Zheng, X.Long
Published in The Journal of biological chemistry (21.09.2012)
Published in The Journal of biological chemistry (21.09.2012)
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Journal Article
Successful Long Term Therapeutic Expression of Factor VIII in Hemophilia A Dogs After Administration of AAV-cFVIII Using a Two-Chain or Single Chain Delivery Approach
Sabatino, Denise E., Altynova, Ekaterina, Lange, Amy M., Zhou, Shangzhen, Merricks, Elizabeth P., Dillow, Aaron M., Nichols, Timothy C., Arruda, Valder R., Kazazian, Haig H.
Published in Blood (20.11.2009)
Published in Blood (20.11.2009)
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Long Term Dose-Dependent Correction of Hemophilia A Dogs Using AAV-8 and AAV-9-Mediated FVIII Gene Transfer
Sabatino, Denise E., Lange, Amy M., Mucci, Melinda, Sarkar, Rita, Dillow, Aaron M., Nichols, Timothy C., Arruda, Valder R., Kazazian, Haig H.
Published in Blood (16.11.2006)
Published in Blood (16.11.2006)
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