AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington’s Disease Minipig Model
Evers, Melvin M., Miniarikova, Jana, Juhas, Stefan, Vallès, Astrid, Bohuslavova, Bozena, Juhasova, Jana, Skalnikova, Helena Kupcova, Vodicka, Petr, Valekova, Ivona, Brouwers, Cynthia, Blits, Bas, Lubelski, Jacek, Kovarova, Hana, Ellederova, Zdenka, van Deventer, Sander J., Petry, Harald, Motlik, Jan, Konstantinova, Pavlina
Published in Molecular therapy (05.09.2018)
Published in Molecular therapy (05.09.2018)
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Journal Article
Determining sites of interaction between prenisin and its modification enzymes NisB and NisC
Khusainov, Rustem, Heils, René, Lubelski, Jacek, Moll, Gert N., Kuipers, Oscar P.
Published in Molecular microbiology (01.11.2011)
Published in Molecular microbiology (01.11.2011)
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Journal Article
Production of a Class II Two-Component Lantibiotic of Streptococcus pneumoniae Using the Class I Nisin Synthetic Machinery and Leader Sequence
MAJCHRZYKIEWICZ, Joanna A, LUBELSKI, Jacek, MOLL, Gert N, KUIPERS, Anneke, BIJLSMA, Jetta J. E, KUIPERS, Oscar P, RINK, Rick
Published in Antimicrobial Agents and Chemotherapy (01.04.2010)
Published in Antimicrobial Agents and Chemotherapy (01.04.2010)
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Journal Article
Enhanced Factor IX Activity following Administration of AAV5-R338L “Padua” Factor IX versus AAV5 WT Human Factor IX in NHPs
Spronck, Elisabeth A., Liu, Ying Poi, Lubelski, Jacek, Ehlert, Erich, Gielen, Sander, Montenegro-Miranda, Paula, de Haan, Martin, Nijmeijer, Bart, Ferreira, Valerie, Petry, Harald, van Deventer, Sander J.
Published in Molecular therapy. Methods & clinical development (13.12.2019)
Published in Molecular therapy. Methods & clinical development (13.12.2019)
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Journal Article
LmrCD is a major multidrug resistance transporter in Lactococcus lactis
Lubelski, Jacek, De Jong, Anne, Van Merkerk, Ronald, Agustiandari, Herfita, Kuipers, Oscar P., Kok, Jan, Driessen, Arnold J. M.
Published in Molecular microbiology (01.08.2006)
Published in Molecular microbiology (01.08.2006)
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Journal Article
In-Depth Characterization of a Mifepristone-Regulated Expression System for AAV5-Mediated Gene Therapy in the Liver
Liefhebber, Jolanda M., Martier, Raygene, Van der Zon, Tom, Keskin, Sonay, Huseinovic, Angelina, Lubelski, Jacek, Blits, Bas, Petry, Harald, Konstantinova, Pavlina
Published in Molecular therapy. Methods & clinical development (14.06.2019)
Published in Molecular therapy. Methods & clinical development (14.06.2019)
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Journal Article
LmrR Is a Transcriptional Repressor of Expression of the Multidrug ABC Transporter LmrCD in Lactococcus lactis
AGUSTIANDARI, Herfita, LUBELSKI, Jacek, VAN DEN BERG VAN SAPAROEA, H. Bart, KUIPERS, Oscar P, DRIESSEN, Arnold J. M
Published in Journal of Bacteriology (01.01.2008)
Published in Journal of Bacteriology (01.01.2008)
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Journal Article
The ABC-Type Multidrug Resistance Transporter LmrCD Is Responsible for an Extrusion-Based Mechanism of Bile Acid Resistance in Lactococcus lactis
Zaidi, Arsalan Haseeb, Bakkes, Patrick J, Lubelski, Jacek, Agustiandari, Herfita, Kuipers, Oscar P, Driessen, Arnold J M
Published in Journal of Bacteriology (01.11.2008)
Published in Journal of Bacteriology (01.11.2008)
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Journal Article
Influence of Shifting Positions of Ser, Thr, and Cys Residues in Prenisin on the Efficiency of Modification Reactions and on the Antimicrobial Activities of the Modified Prepeptides
Lubelski, Jacek, Overkamp, Wout, Kluskens, Leon D, Moll, Gert N, Kuipers, Oscar P
Published in Applied and Environmental Microbiology (01.08.2008)
Published in Applied and Environmental Microbiology (01.08.2008)
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Journal Article
Conference Proceeding
Optimization of viral protein ratios for production of rAAV serotype 5 in the baculovirus system
Bosma, Bas, du Plessis, Francois, Ehlert, Erich, Nijmeijer, Bart, de Haan, Martin, Petry, Harald, Lubelski, Jacek
Published in Gene therapy (01.09.2018)
Published in Gene therapy (01.09.2018)
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Journal Article
Predictable Protein Expression with Enhanced Factor IX Activity Following Administration of a Modified AAV5-hFIX Vector to Nonhuman Primates
Liu, Ying Poi, Lubelski, Jacek, Ehlert, Erich, Gielen, Sander, Miranda, Paula, de Haan, Martin, Nijmeijer, Bart, Petry, Harald
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Journal Article
AAV 생산을 위한 이중 이기능성 벡터
DU PLESSIS DAVID JOHANNES FRANCOIS, ANGGAKUSUMA, BOSMA SEBASTIAAN MENNO, LUBELSKI JACEK
Year of Publication 12.12.2022
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Year of Publication 12.12.2022
Patent
Embedding siRNA sequences targeting Apolipoprotein B100 in shRNA and miRNA scaffolds results in differential processing and in vivo efficacy
Maczuga, Piotr, Lubelski, Jacek, van Logtenstein, Richard, Borel, Florie, Blits, Bas, Fakkert, Erwin, Costessi, Adalberto, Butler, Derek, van Deventer, Sander, Petry, Harald, Koornneef, Annemart, Konstantinova, Pavlina
Published in Molecular therapy (01.01.2013)
Published in Molecular therapy (01.01.2013)
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Journal Article
I04 AAV5-MIHTT gene therapy demonstrates broad distribution and strong human mutant huntingtin lowering in a huntington disease minipig model
Klima, Jiri, Evers, Melvin M, Miniarikova, Jana, Juhas, Stefan, Vallès, Astrid, Bohuslavova, Bozena, Juhasova, Jana, Skalnikova, Helena Kupcova, Vodicka, Petr, Valekova, Ivona, Brouwers, Cynthia, Blits, Bas, Lubelski, Jacek, Kovarova, Hana, van Deventer, Sander J, Petry, Harald, Motlik, Jan, Konstantinova, Pavlina, Ellederova, Zdenka
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2018)
Published in Journal of neurology, neurosurgery and psychiatry (01.09.2018)
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Journal Article
DNA DNA IMPURITIES IN A COMPOSITION COMPRISING A PARVOVIRAL VIRION
HERMENS WILHELMUS THEODORUS JOHANNES MARIA CHRISTIAAN, LUBELSKI JACEK
Year of Publication 12.07.2017
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Year of Publication 12.07.2017
Patent
곤충 세포에서의 개선된 AAV 캡시드 생산
DU PLESSIS DAVID JOHANNES FRANCOIS, PETRY HARALD PETER ALBERT, TER BRAKE OLIVIER, BOSMA SEBASTIAAN MENNO, LUBELSKI JACEK
Year of Publication 04.05.2020
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Year of Publication 04.05.2020
Patent