Autologous intramuscular transplantation of engineered satellite cells induces exosome-mediated systemic expression of Fukutin-related protein and rescues disease phenotype in a murine model of limb-girdle muscular dystrophy type 2I
Frattini, Paola, Villa, Chiara, De Santis, Francesca, Meregalli, Mirella, Belicchi, Marzia, Erratico, Silvia, Bella, Pamela, Raimondi, Manuela Teresa, Lu, Qilong, Torrente, Yvan
Published in Human molecular genetics (01.10.2017)
Published in Human molecular genetics (01.10.2017)
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Muscle and Heart Function Restoration in a Limb Girdle Muscular Dystrophy 2I (LGMD2I) Mouse Model by Systemic FKRP Gene Delivery
Qiao, Chunping, Wang, Chi-Hsien, Zhao, Chunxia, Lu, Peijuan, Awano, Hiroyuki, Xiao, Bin, Li, Jianbin, Yuan, Zhenhua, Dai, Yi, Martin, Carrie Bette, Li, Juan, Lu, Qilong, Xiao, Xiao
Published in Molecular therapy (01.11.2014)
Published in Molecular therapy (01.11.2014)
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Aminoglycoside Enhances the Delivery of Antisense Morpholino Oligonucleotides In Vitro and in mdx Mice
Wang, Mingxing, Wu, Bo, Shah, Sapana N., Lu, Peijuan, Lu, Qilong
Published in Molecular therapy. Nucleic acids (07.06.2019)
Published in Molecular therapy. Nucleic acids (07.06.2019)
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Saponins as Natural Adjuvant for Antisense Morpholino Oligonucleotides Delivery In Vitro and in mdx Mice
Wang, Mingxing, Wu, Bo, Shah, Sapana N., Lu, Peijuan, Lu, Qilong
Published in Molecular therapy. Nucleic acids (01.06.2018)
Published in Molecular therapy. Nucleic acids (01.06.2018)
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Triazine-cored polymeric vectors for antisense oligonucleotide delivery in vitro and in vivo
Wang, Mingxing, Wu, Bo, Tucker, Jason D, Shah, Sapana N, Lu, Peijuan, Lu, Qilong
Published in Journal of nanobiotechnology (18.02.2020)
Published in Journal of nanobiotechnology (18.02.2020)
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Poly(ester amine) Composed of Polyethylenimine and Pluronic Enhance Delivery of Antisense Oligonucleotides In Vitro and in Dystrophic mdx Mice
Wang, Mingxing, Wu, Bo, Tucker, Jason D, Bollinger, Lauren E, Lu, Peijuan, Lu, Qilong
Published in Molecular therapy. Nucleic acids (02.08.2016)
Published in Molecular therapy. Nucleic acids (02.08.2016)
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Tween 85-Modified Low Molecular Weight PEI Enhances Exon-Skipping of Antisense Morpholino Oligomer In Vitro and in mdx Mice
Wang, Mingxing, Wu, Bo, Tucker, Jason D., Shah, Sapana N., Lu, Peijuan, Bollinger, Lauren E., Lu, Qilong
Published in Molecular therapy. Nucleic acids (15.12.2017)
Published in Molecular therapy. Nucleic acids (15.12.2017)
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Post-Natal Knockdown of Fukutin-Related Protein Expression in Muscle by Long-Term RNA Interference Induces Dystrophic Pathology
Wang, Chi-Hsien, Chan, Yiumo Michael, Tang, Ru-Hang, Xiao, Bin, Lu, Peijuan, Keramaris-Vrantsis, Elizabeth, Zheng, Hui, Qiao, Chunping, Jiang, Jiangang, Li, Juan, Ma, Hsin-I, Lu, Qilong, Xiao, Xiao
Published in The American journal of pathology (2011)
Published in The American journal of pathology (2011)
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Poly(ester amine) constructed from polyethylenimine and pluronic for gene delivery in vitro and in vivo
Wang, Mingxing, Wu, Bo, Tucker, Jason D., Lu, Peijuan, Lu, Qilong
Published in Drug delivery (21.11.2016)
Published in Drug delivery (21.11.2016)
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Polyethylenimine-modified Pluronics (PCMs) Improve Morpholino Oligomer Delivery in Cell Culture and Dystrophic mdx Mice
Wang, Mingxing, Wu, Bo, Lu, Peijuan, Cloer, Caryn, Tucker, Jay D, Lu, Qilong
Published in Molecular therapy (01.01.2013)
Published in Molecular therapy (01.01.2013)
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Tris[2-(acryloyloxy)ethyl]isocyanurate Cross-Linked Low-Molecular-Weight Polyethylenimine as Gene Delivery Carriers in Cell Culture and Dystrophic mdx Mice
Wang, Mingxing, Tucker, Jay D, Lu, Peijuan, Wu, Bo, Cloer, Caryn, Lu, Qilong
Published in Bioconjugate chemistry (18.04.2012)
Published in Bioconjugate chemistry (18.04.2012)
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Tween 85 grafted PEIs enhanced delivery of antisense 2′-O-methyl phosphorothioate oligonucleotides in vitro and in dystrophic mdx mice
Wang, Mingxing, Wu, Bo, Tucker, Jason D, Lu, Peijuan, Bollinger, Lauren E, Lu, Qilong
Published in Journal of materials chemistry. B, Materials for biology and medicine (14.07.2015)
Published in Journal of materials chemistry. B, Materials for biology and medicine (14.07.2015)
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Saponins enhance exon skipping of 2'-O-methyl phosphorothioate oligonucleotide in vitro and in vivo
Wang, Mingxing, Wu, Bo, Shah, Sapana N, Lu, Peijuan, Lu, Qilong
Published in Drug design, development and therapy (01.01.2018)
Published in Drug design, development and therapy (01.01.2018)
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