A higher dose of alglucosidase alpha in classic infantile Pompe disease positively affects ventilator-free survival and motor outcome: An open-label single-center study
van Gelder, C, Poelman, E, Plug, I, Hoogeveen-Westerveld, M, Kuperus, E, van der Beek, N, Reuser, A, van der Ploeg, A
Published in Neuromuscular disorders : NMD (01.10.2015)
Published in Neuromuscular disorders : NMD (01.10.2015)
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Journal Article
T.P.19
de Vries, J.M, Kuperus, E, Hoogeveen-Westerveld, M, Wens, S.C.A, Kroos, M.A, Kruijshaar, M.E, van Doorn, P.A, van der Ploeg, A.T, Pijnappel, W.W.M
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
P.219 - Long-term efficacy of enzyme-replacement therapy in 102 adult Pompe patients: a 5-year nationwide prospective cohort study
Harlaar, L., Kuperus, E., Kruijshaar, M., Wens, S., de Vries, J., Favejee, M., van der Meijden, J., Rizopoulos, D., Brusse, E., van Doorn, P., van der Ploeg, A., van der Beek, N.
Published in Neuromuscular disorders : NMD (01.10.2017)
Published in Neuromuscular disorders : NMD (01.10.2017)
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Journal Article
Long-term efficacy of enzyme-replacement therapy in 102 adult Pompe patients: a 5-year nationwide prospective cohort study
Harlaar, L., Kuperus, E., Kruijshaar, M., Wens, S., de Vries, J., Favejee, M., van der Meijden, J., Rizopoulos, D., Brusse, E., van Doorn, P., van der Ploeg, A., van der Beek, N.
Published in Neuromuscular disorders : NMD (01.10.2017)
Published in Neuromuscular disorders : NMD (01.10.2017)
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Journal Article
G.P.10 - A higher dose of alglucosidase alpha in classic infantile Pompe disease positively affects ventilator-free survival and motor outcome: An open-label single-center study
van Gelder, C., Poelman, E., Plug, I., Hoogeveen-Westerveld, M., Kuperus, E., van der Beek, N., Reuser, A., van der Ploeg, A.
Published in Neuromuscular disorders : NMD (01.10.2015)
Published in Neuromuscular disorders : NMD (01.10.2015)
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Journal Article
T.P.19: Effects of antibody formation during enzyme replacement therapy in 73 adult patients with Pompe disease
de Vries, J.M., Kuperus, E., Hoogeveen-Westerveld, M., Wens, S.C.A., Kroos, M.A., Kruijshaar, M.E., van Doorn, P.A., van der Ploeg, A.T., Pijnappel, W.W.M.
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
Get full text
Journal Article