Effective Management of XLA Associated Enteropathy with Vedolizumab Monotherapy
Rai, Ekra, Doroudchi, Ali, Nulsen, Benjamin, Younes, Ramee, Kuo, Caroline Y.
Published in Journal of clinical immunology (01.10.2024)
Published in Journal of clinical immunology (01.10.2024)
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Journal Article
CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells
Hoban, Megan D, Lumaquin, Dianne, Kuo, Caroline Y, Romero, Zulema, Long, Joseph, Ho, Michelle, Young, Courtney S, Mojadidi, Michelle, Fitz-Gibbon, Sorel, Cooper, Aaron R, Lill, Georgia R, Urbinati, Fabrizia, Campo-Fernandez, Beatriz, Bjurstrom, Carmen F, Pellegrini, Matteo, Hollis, Roger P, Kohn, Donald B
Published in Molecular therapy (01.09.2016)
Published in Molecular therapy (01.09.2016)
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Journal Article
Lentiviral Gene Therapy for Artemis-Deficient SCID
Cowan, Morton J., Yu, Jason, Facchino, Janelle, Fraser-Browne, Carol, Sanford, Ukina, Kawahara, Misako, Dara, Jasmeen, Long-Boyle, Janel, Oh, Jess, Chan, Wendy, Chag, Shivali, Broderick, Lori, Chellapandian, Deepak, Decaluwe, Hélène, Golski, Catherine, Hu, Diana, Kuo, Caroline Y., Miller, Holly K., Petrovic, Aleksandra, Currier, Robert, Hilton, Joan F., Punwani, Divya, Dvorak, Christopher C., Malech, Harry L., McIvor, R. Scott, Puck, Jennifer M.
Published in The New England journal of medicine (22.12.2022)
Published in The New England journal of medicine (22.12.2022)
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Journal Article
Overview of the current status of gene therapy for primary immune deficiencies (PIDs)
Kuo, Caroline Y., Kohn, Donald B.
Published in Journal of allergy and clinical immunology (01.08.2020)
Published in Journal of allergy and clinical immunology (01.08.2020)
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Journal Article
Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome
Kuo, Caroline Y., Long, Joseph D., Campo-Fernandez, Beatriz, de Oliveira, Satiro, Cooper, Aaron R., Romero, Zulema, Hoban, Megan D., Joglekar, Alok V., Lill, Georgia R., Kaufman, Michael L., Fitz-Gibbon, Sorel, Wang, Xiaoyan, Hollis, Roger P., Kohn, Donald B.
Published in Cell reports (Cambridge) (29.05.2018)
Published in Cell reports (Cambridge) (29.05.2018)
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Journal Article
Lentiviral gene therapy for X-linked chronic granulomatous disease
Kohn, Donald B., Booth, Claire, Kang, Elizabeth M., Pai, Sung-Yun, Shaw, Kit L., Santilli, Giorgia, Armant, Myriam, Buckland, Karen F., Choi, Uimook, De Ravin, Suk See, Dorsey, Morna J., Kuo, Caroline Y., Leon-Rico, Diego, Rivat, Christine, Izotova, Natalia, Gilmour, Kimberly, Snell, Katie, Dip, Jinhua Xu-Bayford, Darwish, Jinan, Morris, Emma C., Terrazas, Dayna, Wang, Leo D., Bauser, Christopher A., Paprotka, Tobias, Kuhns, Douglas B., Gregg, John, Raymond, Hayley E., Everett, John K., Honnet, Geraldine, Biasco, Luca, Newburger, Peter E., Bushman, Frederic D., Grez, Manuel, Gaspar, H. Bobby, Williams, David A., Malech, Harry L., Galy, Anne, Thrasher, Adrian J.
Published in Nature Medicine (01.02.2020)
Published in Nature Medicine (01.02.2020)
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Magazine Article
Editing the Sickle Cell Disease Mutation in Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates
Romero, Zulema, Lomova, Anastasia, Said, Suzanne, Miggelbrink, Alexandra, Kuo, Caroline Y., Campo-Fernandez, Beatriz, Hoban, Megan D., Masiuk, Katelyn E., Clark, Danielle N., Long, Joseph, Sanchez, Julie M., Velez, Miriam, Miyahira, Eric, Zhang, Ruixue, Brown, Devin, Wang, Xiaoyan, Kurmangaliyev, Yerbol Z., Hollis, Roger P., Kohn, Donald B.
Published in Molecular therapy (07.08.2019)
Published in Molecular therapy (07.08.2019)
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Journal Article
The PTH/PTHrP-SIK3 pathway affects skeletogenesis through altered mTOR signaling
Csukasi, Fabiana, Duran, Ivan, Barad, Maya, Barta, Tomas, Gudernova, Iva, Trantirek, Lukas, Martin, Jorge H, Kuo, Caroline Y, Woods, Jeremy, Lee, Hane, Cohn, Daniel H, Krejci, Pavel, Krakow, Deborah
Published in Science translational medicine (19.09.2018)
Published in Science translational medicine (19.09.2018)
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Journal Article
Immune and Genetic Features of the Chromosome 22q11.2 Deletion (DiGeorge Syndrome)
Kuo, Caroline Y., Signer, Rebecca, Saitta, Sulagna C.
Published in Current allergy and asthma reports (01.12.2018)
Published in Current allergy and asthma reports (01.12.2018)
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Journal Article
Gene Therapy for the Treatment of Primary Immune Deficiencies
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Journal Article
Book Review
High Acceptability of HIV Pre-exposure Prophylaxis but Challenges in Adherence and Use: Qualitative Insights from a Phase I Trial of Intermittent and Daily PrEP in At-Risk Populations in Kenya
Van der Elst, Elisabeth Maria, Mbogua, Judie, Operario, Don, Mutua, Gaudensia, Kuo, Caroline, Mugo, Peter, Kanungi, Jennifer, Singh, Sagri, Haberer, Jessica, Priddy, Frances, Sanders, Eduard Joachim
Published in AIDS and behavior (01.07.2013)
Published in AIDS and behavior (01.07.2013)
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Journal Article
Investigating tangible and mental resources as predictors of perceived household food insecurity during pregnancy among women in a South African birth cohort study
Pellowski, Jennifer A., Barnett, Whitney, Kuo, Caroline C., Koen, Nastassja, Zar, Heather J., Stein, Dan J.
Published in Social science & medicine (1982) (01.08.2017)
Published in Social science & medicine (1982) (01.08.2017)
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Intersections between COVID-19 and socio-economic mental health stressors in the lives of South African adolescent girls and young women
Duby, Zoe, Bunce, Brittany, Fowler, Chantal, Bergh, Kate, Jonas, Kim, Dietrich, Janan Janine, Govindasamy, Darshini, Kuo, Caroline, Mathews, Catherine
Published in Child and adolescent psychiatry and mental health (26.03.2022)
Published in Child and adolescent psychiatry and mental health (26.03.2022)
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Journal Article
Identifying Adolescents at Highest Risk of ART Non-adherence, Using the World Health Organization-Endorsed HEADSS and HEADSS+ Checklists
Cluver, Lucie D., Shenderovich, Yulia, Seslija, Marko, Zhou, Siyanai, Toska, Elona, Armstrong, Alice, Gulaid, Laurie A., Ameyan, Wole, Cassolato, Matteo, Kuo, Caroline C., Laurenzi, Christina, Sherr, Lorraine
Published in AIDS and behavior (2024)
Published in AIDS and behavior (2024)
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Journal Article
Pathways From Family Disadvantage via Abusive Parenting and Caregiver Mental Health to Adolescent Health Risks in South Africa
Meinck, Franziska, D.Phil, Cluver, Lucie Dale, D.Phil, Orkin, Frederick Mark, Ph.D, Kuo, Caroline, D.Phil, Sharma, Amogh Dhar, M.Sc, Hensels, Imca Sifra, M.Sc, Sherr, Lorraine, Ph.D
Published in Journal of adolescent health (01.01.2017)
Published in Journal of adolescent health (01.01.2017)
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