Gene therapy in rare diseases: the benefits and challenges of developing a patient-centric registry for Strimvelis in ADA-SCID
Stirnadel-Farrant, Heide, Kudari, Mahesh, Garman, Nadia, Imrie, Jessica, Chopra, Bikramjit, Giannelli, Stefania, Gabaldo, Michela, Corti, Ambra, Zancan, Stefano, Aiuti, Alessandro, Cicalese, Maria Pia, Batta, Rohit, Appleby, Jonathan, Davinelli, Mario, Ng, Pauline
Published in Orphanet journal of rare diseases (06.04.2018)
Published in Orphanet journal of rare diseases (06.04.2018)
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Journal Article
Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency
Kohn, Donald B, Booth, Claire, Shaw, Kit L, Xu-Bayford, Jinhua, Garabedian, Elizabeth, Trevisan, Valentina, Carbonaro-Sarracino, Denise A, Soni, Kajal, Terrazas, Dayna, Snell, Katie, Ikeda, Alan, Leon-Rico, Diego, Moore, Theodore B, Buckland, Karen F, Shah, Ami J, Gilmour, Kimberly C, De Oliveira, Satiro, Rivat, Christine, Crooks, Gay M, Izotova, Natalia, Tse, John, Adams, Stuart, Shupien, Sally, Ricketts, Hilory, Davila, Alejandra, Uzowuru, Chilenwa, Icreverzi, Amalia, Barman, Provaboti, Campo Fernandez, Beatriz, Hollis, Roger P, Coronel, Maritess, Yu, Allen, Chun, Krista M, Casas, Christian E, Zhang, Ruixue, Arduini, Serena, Lynn, Frances, Kudari, Mahesh, Spezzi, Andrea, Zahn, Marco, Heimke, Rene, Labik, Ivan, Parrott, Roberta, Buckley, Rebecca H, Reeves, Lilith, Cornetta, Kenneth, Sokolic, Robert, Hershfield, Michael, Schmidt, Manfred, Candotti, Fabio, Malech, Harry L, Thrasher, Adrian J, Gaspar, H. Bobby
Published in The New England journal of medicine (27.05.2021)
Published in The New England journal of medicine (27.05.2021)
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Journal Article
A psychological comparison of temporomandibular disorder and chronic daily headache: are there targets for therapeutic interventions?
Jerjes, Waseem, BDS, MSc, Madland, Geir, BDS, BSc, FDS, PhD, Feinmann, Charlotte, MSc, MD, Hopper, Colin, BDS, MBBS, FDS, FRCS, Kumar, Mahesh, BDS, MBBS, FDS, FRCS, Upile, Tahwinder, FRCS, Kudari, Mahesh, BSc, Newman, Stanton, Dphil
Published in Oral surgery, oral medicine, oral pathology, oral radiology and endodontics (01.03.2007)
Published in Oral surgery, oral medicine, oral pathology, oral radiology and endodontics (01.03.2007)
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FDXR is a biomarker of radiation exposure in vivo
O'Brien, Gráinne, Cruz-Garcia, Lourdes, Majewski, Matthäus, Grepl, Jakub, Abend, Michael, Port, Matthias, Tichý, Aleš, Sirak, Igor, Malkova, Andrea, Donovan, Ellen, Gothard, Lone, Boyle, Sue, Somaiah, Navita, Ainsbury, Elizabeth, Ponge, Lucyna, Slosarek, Krzysztof, Miszczyk, Leszek, Widlak, Piotr, Green, Edward, Patel, Neel, Kudari, Mahesh, Gleeson, Fergus, Vinnikov, Volodymyr, Starenkiy, Viktor, Artiukh, Sergii, Vasyliev, Leonid, Zaman, Azfar, Badie, Christophe
Published in Scientific reports (12.01.2018)
Published in Scientific reports (12.01.2018)
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Journal Article
Lentiviral Gene Therapy with Autologous Hematopoietic Stem and Progenitor Cells (HSPCs) for the Treatment of Severe Combined Immune Deficiency Due to Adenosine Deaminase Deficiency (ADA-SCID): Results in an Expanded Cohort
Kohn, Donald B., Shaw, Kit L., Garabedian, Elizabeth, Carbonaro-Sarracino, Denise Ann, Moore, Theodore B., De Oliveira, Satiro N., Crooks, Gay M., Tse, John, Shupien, Sally, Terrazas, Dayna, Davila, Alejandra, Icreverzi, Amalia, Yu, Allen, Chun, Krista M., Casas, Christian E., Barman, Provaboti, Coronel, Maritess, Campo Fernandez, Beatriz, Zhang, Ruixue, Hollis, Roger P., Uzowuru, Chilenwa, Ricketts, Hilory, Bayford, Jinhua Xu, Trevisan, Valentina, Arduini, Serena, Lynn, Frances, Kudari, Mahesh, Spezzi, Andrea, Reeves, Lilith, Cornetta, Kenneth, Sokolic, Robert A., Parrott, Roberta, Buckley, Rebecca, Booth, Claire, Candotti, Fabio, Malech, Harry L., Thrasher, Adrian J., Gaspar, H. Bobby
Published in Blood (13.11.2019)
Published in Blood (13.11.2019)
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Journal Article
Lessons from The Netherlands
Kwong, Esther, Graft, Bethan, Hussain, Muj, Kudari, Mahesh, Mukhtar, Saheel, Ramanuj, Parashar
Published in The Health service journal (11.10.2013)
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Published in The Health service journal (11.10.2013)
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