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Published in Journal of cachexia, sarcopenia and muscle (01.04.2022)
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CRISPR-mediated correction of skeletal muscle Ca2+ handling in a novel DMD patient-derived pluripotent stem cell model
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Published in Neuromuscular disorders : NMD (01.12.2022)
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Optogenetic modeling of human neuromuscular circuits in Duchenne muscular dystrophy with CRISPR and pharmacological corrections
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Published in Science advances (10.09.2021)
Published in Science advances (10.09.2021)
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Journal Article
CRISPR-mediated correction of skeletal muscle Ca 2+ handling in a novel DMD patient-derived pluripotent stem cell model
Morera, Cristina, Kim, Jihee, Paredes-Redondo, Amaia, Nobles, Muriel, Rybin, Denis, Moccia, Robert, Kowala, Anna, Meng, Jinhong, Garren, Seth, Liu, Pentao, Morgan, Jennifer E, Muntoni, Francesco, Christoforou, Nicolas, Owens, Jane, Tinker, Andrew, Lin, Yung-Yao
Published in Neuromuscular disorders : NMD (01.12.2022)
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Published in Neuromuscular disorders : NMD (01.12.2022)
Journal Article
CRISPR-mediated correction of skeletal muscle Ca2+ handling in a novel DMD patient-derived pluripotent stem cell model
Morera, Cristina, Kim, Jihee, Paredes-Redondo, Amaia, Nobles, Muriel, Rybin, Denis, Moccia, Robert, Kowala, Anna, Meng, Jinhong, Garren, Seth, Liu, Pentao, Morgan, Jennifer E, Muntoni, Francesco, Christoforou, Nicolas, Owens, Jane, Tinker, Andrew, Yung-Yao, Lin
Published in bioRxiv (09.03.2022)
Published in bioRxiv (09.03.2022)
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