Gene therapy comes of age
Dunbar, Cynthia E, High, Katherine A, Joung, J Keith, Kohn, Donald B, Ozawa, Keiya, Sadelain, Michel
Published in Science (American Association for the Advancement of Science) (12.01.2018)
Published in Science (American Association for the Advancement of Science) (12.01.2018)
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European consensus statement on leptospirosis in dogs and cats
Schuller, S., Francey, T., Hartmann, K., Hugonnard, M., Kohn, B., Nally, J. E., Sykes, J.
Published in Journal of small animal practice (01.03.2015)
Published in Journal of small animal practice (01.03.2015)
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Polymeric nanoparticles-based topical delivery systems for the treatment of dermatological diseases
Zhang, Zheng, Tsai, Pei-Chin, Ramezanli, Tannaz, Michniak-Kohn, Bozena B
Published in Wiley interdisciplinary reviews. Nanomedicine and nanobiotechnology (01.05.2013)
Published in Wiley interdisciplinary reviews. Nanomedicine and nanobiotechnology (01.05.2013)
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Selection-free genome editing of the sickle mutation in human adult hematopoietic stem/progenitor cells
DeWitt, Mark A, Magis, Wendy, Bray, Nicolas L, Wang, Tianjiao, Berman, Jennifer R, Urbinati, Fabrizia, Heo, Seok-Jin, Mitros, Therese, Muñoz, Denise P, Boffelli, Dario, Kohn, Donald B, Walters, Mark C, Carroll, Dana, Martin, David I K, Corn, Jacob E
Published in Science translational medicine (12.10.2016)
Published in Science translational medicine (12.10.2016)
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Establishing diagnostic criteria for severe combined immunodeficiency disease (SCID), leaky SCID, and Omenn syndrome: The Primary Immune Deficiency Treatment Consortium experience
Shearer, William T., MD, PhD, Dunn, Elizabeth, MA, Notarangelo, Luigi D., MD, Dvorak, Christopher C., MD, Puck, Jennifer M., MD, Logan, Brent R., PhD, Griffith, Linda M., MD, PhD, Kohn, Donald B., MD, O'Reilly, Richard J., MD, Fleisher, Thomas A., MD, Pai, Sung-Yun, MD, Martinez, Caridad A., MD, Buckley, Rebecca H., MD, Cowan, Morton J., MD
Published in Journal of allergy and clinical immunology (01.04.2014)
Published in Journal of allergy and clinical immunology (01.04.2014)
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Human hematopoietic stem/progenitor cells modified by zinc-finger nucleases targeted to CCR5 control HIV-1 in vivo
Crooks, Gay M, Gregory, Philip D, Cannon, Paula M, Holt, Nathalia, Kim, Kenneth, Friedman, Geoffrey, Taupin, Vanessa, Kohn, Donald B, Wang, Xingchao, Holmes, Michael C, Wang, Jianbin
Published in Nature biotechnology (01.08.2010)
Published in Nature biotechnology (01.08.2010)
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A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells
Young, Courtney S., Hicks, Michael R., Ermolova, Natalia V., Nakano, Haruko, Jan, Majib, Younesi, Shahab, Karumbayaram, Saravanan, Kumagai-Cresse, Chino, Wang, Derek, Zack, Jerome A., Kohn, Donald B., Nakano, Atsushi, Nelson, Stanley F., Miceli, M. Carrie, Spencer, Melissa J., Pyle, April D.
Published in Cell stem cell (07.04.2016)
Published in Cell stem cell (07.04.2016)
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CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells
Hoban, Megan D, Lumaquin, Dianne, Kuo, Caroline Y, Romero, Zulema, Long, Joseph, Ho, Michelle, Young, Courtney S, Mojadidi, Michelle, Fitz-Gibbon, Sorel, Cooper, Aaron R, Lill, Georgia R, Urbinati, Fabrizia, Campo-Fernandez, Beatriz, Bjurstrom, Carmen F, Pellegrini, Matteo, Hollis, Roger P, Kohn, Donald B
Published in Molecular therapy (01.09.2016)
Published in Molecular therapy (01.09.2016)
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Chronic Diarrhea in Dogs – Retrospective Study in 136 Cases
Volkmann, M., Steiner, J.M., Fosgate, G.T., Zentek, J., Hartmann, S., Kohn, B.
Published in Journal of veterinary internal medicine (01.07.2017)
Published in Journal of veterinary internal medicine (01.07.2017)
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Microchemical identification of enantiomers in early-branching animals: Lineage-specific diversification in the usage of D-glutamate and D-aspartate
Moroz, Leonid L., Sohn, Dosung, Romanova, Daria Y., Kohn, Andrea B.
Published in Biochemical and biophysical research communications (05.07.2020)
Published in Biochemical and biophysical research communications (05.07.2020)
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Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells
Hoban, Megan D., Cost, Gregory J., Mendel, Matthew C., Romero, Zulema, Kaufman, Michael L., Joglekar, Alok V., Ho, Michelle, Lumaquin, Dianne, Gray, David, Lill, Georgia R., Cooper, Aaron R., Urbinati, Fabrizia, Senadheera, Shantha, Zhu, Allen, Liu, Pei-Qi, Paschon, David E., Zhang, Lei, Rebar, Edward J., Wilber, Andrew, Wang, Xiaoyan, Gregory, Philip D., Holmes, Michael C., Reik, Andreas, Hollis, Roger P., Kohn, Donald B.
Published in Blood (23.04.2015)
Published in Blood (23.04.2015)
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Improving Gene Editing Outcomes in Human Hematopoietic Stem and Progenitor Cells by Temporal Control of DNA Repair
Lomova, Anastasia, Clark, Danielle N., Campo‐Fernandez, Beatriz, Flores‐Bjurström, Carmen, Kaufman, Michael L., Fitz‐Gibbon, Sorel, Wang, Xiaoyan, Miyahira, Eric Y., Brown, Devin, DeWitt, Mark A., Corn, Jacob E., Hollis, Roger P., Romero, Zulema, Kohn, Donald B.
Published in Stem cells (Dayton, Ohio) (01.02.2019)
Published in Stem cells (Dayton, Ohio) (01.02.2019)
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Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome
Kuo, Caroline Y., Long, Joseph D., Campo-Fernandez, Beatriz, de Oliveira, Satiro, Cooper, Aaron R., Romero, Zulema, Hoban, Megan D., Joglekar, Alok V., Lill, Georgia R., Kaufman, Michael L., Fitz-Gibbon, Sorel, Wang, Xiaoyan, Hollis, Roger P., Kohn, Donald B.
Published in Cell reports (Cambridge) (29.05.2018)
Published in Cell reports (Cambridge) (29.05.2018)
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Prostate cancer originating in basal cells progresses to adenocarcinoma propagated by luminal-like cells
Stoyanova, Tanya, Cooper, Aaron R., Drake, Justin M., Liu, Xian, Armstrong, Andrew J., Pienta, Kenneth J., Zhang, Hong, Kohn, Donald B., Huang, Jiaoti, Witte, Owen N., Goldstein, Andrew S.
Published in Proceedings of the National Academy of Sciences - PNAS (10.12.2013)
Published in Proceedings of the National Academy of Sciences - PNAS (10.12.2013)
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Granulocytic anaplasmosis in 63 dogs: clinical signs, laboratory results, therapy and course of disease
Chirek, A., Silaghi, C., Pfister, K., Kohn, B.
Published in Journal of small animal practice (01.02.2018)
Published in Journal of small animal practice (01.02.2018)
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