Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy
Moretti, A, Fonteyne, L, Giesert, F, Hoppmann, P, Meier, A B, Bozoglu, T, Baehr, A, Schneider, C M, Sinnecker, D, Klett, K, Fröhlich, T, Rahman, F Abdel, Haufe, T, Sun, S, Jurisch, V, Kessler, B, Hinkel, R, Dirschinger, R, Martens, E, Jilek, C, Graf, A, Krebs, S, Santamaria, G, Kurome, M, Zakhartchenko, V, Campbell, B, Voelse, K, Wolf, A, Ziegler, T, Reichert, S, Lee, S, Flenkenthaler, F, Dorn, T, Jeremias, I, Blum, H, Dendorfer, A, Schnieke, A, Krause, S, Walter, M C, Klymiuk, N, Laugwitz, K L, Wolf, E, Wurst, W, Kupatt, C
Published in Nature medicine (01.02.2020)
Published in Nature medicine (01.02.2020)
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Journal Article
One‐Year Heterotopic Cardiac Xenograft Survival in a Pig to Baboon Model
Mohiuddin, M. M., Singh, A. K., Corcoran, P. C., Hoyt, R. F., Thomas, M. L., Lewis, B. G. T., Eckhaus, M., Reimann, K. A., Klymiuk, N., Wolf, E., Ayares, D., Horvath, K. A.
Published in American journal of transplantation (01.02.2014)
Published in American journal of transplantation (01.02.2014)
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Journal Article
LEA29Y expression in transgenic neonatal porcine islet-like cluster promotes long-lasting xenograft survival in humanized mice without immunosuppressive therapy
Buerck, L Wolf-van, Schuster, M, Oduncu, F S, Baehr, A, Mayr, T, Guethoff, S, Abicht, J, Reichart, B, Klymiuk, N, Wolf, E, Seissler, J
Published in Scientific reports (15.06.2017)
Published in Scientific reports (15.06.2017)
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Journal Article
The normal trachea is cleaned by MUC5B mucin bundles from the submucosal glands coated with the MUC5AC mucin
Ermund, Anna, Meiss, Lauren N., Rodriguez-Pineiro, Ana M., Bähr, Andrea, Nilsson, Harriet E., Trillo-Muyo, Sergio, Ridley, Caroline, Thornton, David J., Wine, Jeffrey J., Hebert, Hans, Klymiuk, Nikolai, Hansson, Gunnar C.
Published in Biochemical and biophysical research communications (21.10.2017)
Published in Biochemical and biophysical research communications (21.10.2017)
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Journal Article
Granule-stored MUC5B mucins are packed by the non-covalent formation of N-terminal head-to-head tetramers
Trillo-Muyo, Sergio, Nilsson, Harriet E., Recktenwald, Christian V., Ermund, Anna, Ridley, Caroline, Meiss, Lauren N., Bähr, Andrea, Klymiuk, Nikolai, Wine, Jeffrey J., Koeck, Philip J.B., Thornton, David J., Hebert, Hans, Hansson, Gunnar C.
Published in The Journal of biological chemistry (13.04.2018)
Published in The Journal of biological chemistry (13.04.2018)
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Journal Article
Sequential targeting of CFTR by BAC vectors generates a novel pig model of cystic fibrosis
Klymiuk, N., Mundhenk, L., Kraehe, K., Wuensch, A., Plog, S., Emrich, D., Langenmayer, M. C., Stehr, M., Holzinger, A., Kröner, C., Richter, A., Kessler, B., Kurome, M., Eddicks, M., Nagashima, H., Heinritzi, K., Gruber, A. D., Wolf, E.
Published in Journal of molecular medicine (Berlin, Germany) (01.05.2012)
Published in Journal of molecular medicine (Berlin, Germany) (01.05.2012)
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Journal Article
Linkage between growth retardation and pituitary cell morphology in a dystrophin-deficient pig model of Duchenne muscular dystrophy
Hofmann, I., Kemter, E., Theobalt, N., Fiedler, S., Bidlingmaier, M., Hinrichs, A., Aichler, M., Burkhardt, K., Klymiuk, N., Wolf, E., Wanke, R., Blutke, A.
Published in Growth hormone & IGF research (01.04.2020)
Published in Growth hormone & IGF research (01.04.2020)
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Journal Article
Xenotransplantation of Porcine Islet Cells as a Potential Option for the Treatment of Type 1 Diabetes in the Future
Reichart, B., Niemann, H., Chavakis, T., Denner, J., Jaeckel, E., Ludwig, B., Marckmann, G., Schnieke, A., Schwinzer, R., Seissler, J., Tönjes, R. R., Klymiuk, N., Wolf, E., Bornstein, S. R.
Published in Hormone and metabolic research (01.01.2015)
Published in Hormone and metabolic research (01.01.2015)
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Journal Article
WS06.6 Mucociliary transport is impaired in cystic fibrosis pig airways
Ermund, A, Meiss, L.N, Bähr, A, Klymiuk, N, Hansson, G.C
Published in Journal of cystic fibrosis (01.06.2015)
Published in Journal of cystic fibrosis (01.06.2015)
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Journal Article
G.P.82
Walter, M.C, Klymiuk, N, Blutke, A, Graf, A, Krause, S, Wuensch, A, Krebs, S, Kessler, B, Zakhartchenko, V, Kurome, M, Kemter, E, Nagashima, H, Schoser, B, Herbach, N, Blum, H, Wanke, R, Aartsma-Rus, A, Lochmuller, H, Wolf, E
Published in Neuromuscular disorders : NMD (01.10.2014)
Published in Neuromuscular disorders : NMD (01.10.2014)
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Journal Article
Ex vivo xenoperfusion of CD46 & HLA-E double transgenic pig limbs: Effect of transgenic expression of human CD46
Bongoni, B., Constantinescu, M., Kiermeir, D., Pradier, A., Millard, A.L., Bähr, A., Voegelin, E., Seebach, J., Klymiuk, N., Rieben, R.
Published in Molecular immunology (01.08.2011)
Published in Molecular immunology (01.08.2011)
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Journal Article
Transgenic strategies to overcome cell-mediated and acute vascular rejection of pig-to-human xenografts
Klymiuk, N., Keßler, B., Kurome, M., Wuensch, A., Wolf, E.
Published in Xenotransplantation (Københaven) (01.03.2010)
Published in Xenotransplantation (Københaven) (01.03.2010)
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Journal Article
New transgenic pigs for xenotransplantation, part 2: Strategies to overcome cellular rejection
Keßler, B., Kurome, M., Klymiuk, N., Wünsch, A., Seissler, J., Wolf, E.
Published in Xenotransplantation (Københaven) (01.01.2011)
Published in Xenotransplantation (Københaven) (01.01.2011)
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Journal Article
Establishment of genetically modified pig animal models for xenotransplantation
Klymiuk, N., Kessler, B., Kurome, M., Wünsch, A., Wolf, E.
Published in Xenotransplantation (Københaven) (01.09.2008)
Published in Xenotransplantation (Københaven) (01.09.2008)
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Journal Article
AAV.Cas9 and AAV.SERCA2a strategies to mitigate heart failure in DMD pigs
Baehr, A, Hornaschewitz, N, Stirm, M, Hoppmann, P, Bozoglu, T, Klymiuk, N, Laugwitz, K L, Moretti, A, Wolf, E, Hajjar, R, Kupatt, C
Published in European heart journal (09.11.2023)
Published in European heart journal (09.11.2023)
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Journal Article
Migratory and anti-fibrotic programmes define the regenerative potential of human cardiac progenitors
Poch, Christine M, Foo, Kylie S, De Angelis, Maria Teresa, Jennbacken, Karin, Santamaria, Gianluca, Bähr, Andrea, Wang, Qing-Dong, Reiter, Franziska, Hornaschewitz, Nadja, Zawada, Dorota, Bozoglu, Tarik, My, Ilaria, Meier, Anna, Dorn, Tatjana, Hege, Simon, Lehtinen, Miia L, Tsoi, Yat Long, Hovdal, Daniel, Hyllner, Johan, Schwarz, Sascha, Sudhop, Stefanie, Jurisch, Victoria, Sini, Marcella, Fellows, Mick D, Cummings, Matthew, Clarke, Jonathan, Baptista, Ricardo, Eroglu, Elif, Wolf, Eckhard, Klymiuk, Nikolai, Lu, Kun, Tomasi, Roland, Dendorfer, Andreas, Gaspari, Marco, Parrotta, Elvira, Cuda, Giovanni, Krane, Markus, Sinnecker, Daniel, Hoppmann, Petra, Kupatt, Christian, Fritsche-Danielson, Regina, Moretti, Alessandra, Chien, Kenneth R, Laugwitz, Karl-Ludwig
Published in Nature cell biology (01.05.2022)
Published in Nature cell biology (01.05.2022)
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Journal Article
New generation ENaC inhibitors detach cystic fibrosis airway mucus bundles via sodium/hydrogen exchanger inhibition
Giorgetti, Melania, Klymiuk, Nikolai, Bähr, Andrea, Hemmerling, Martin, Jinton, Lisa, Tarran, Robert, Malmgren, Anna, Åstrand, Annika, Hansson, Gunnar C., Ermund, Anna
Published in European journal of pharmacology (05.08.2021)
Published in European journal of pharmacology (05.08.2021)
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