Pre-existing immunity does not impair the engraftment of CRISPR-Cas9-edited cells in rhesus macaques conditioned with busulfan or radiation
Essawi, Khaled, Hakami, Waleed, Naeem Khan, Muhammad Behroz, Martin, Reid, Zeng, Jing, Chu, Rebecca, Uchida, Naoya, Bonifacino, Aylin C., Krouse, Allen E., Linde, Nathaniel S., Donahue, Robert E., Blobel, Gerd A., Gerdemann, Ulrike, Kean, Leslie S., Maitland, Stacy A., Wolfe, Scot A., Metais, Jean-Yves, Gottschalk, Stephen, Bauer, Daniel E., Tisdale, John F., Demirci, Selami
Published in Molecular therapy. Methods & clinical development (08.06.2023)
Published in Molecular therapy. Methods & clinical development (08.06.2023)
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Journal Article
In Vitro and In Vivo Studies for the Investigation of γ-Globin Gene Induction by Adhatoda vasica : A Pre-Clinical Study of HbF Inducers for β-Thalassemia
Iftikhar, Fizza, Rahman, Saeedur, Khan, Muhammad Behroz Naeem, Khan, Kanwal, Khan, Muhammad Noman, Uddin, Reaz, Musharraf, Syed Ghulam
Published in Frontiers in pharmacology (29.03.2022)
Published in Frontiers in pharmacology (29.03.2022)
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Journal Article
Monoterpenes as therapeutic candidates to induce fetal hemoglobin synthesis and up-regulation of gamma-globin gene: An in vitro and in vivo investigation
Iftikhar, Fizza, Khan, Muhammad Behroz Naeem, Musharraf, Syed Ghulam
Published in European journal of pharmacology (15.01.2021)
Published in European journal of pharmacology (15.01.2021)
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Journal Article
BCL11A-targeted γ-globin gene induction by triterpenoid glycosides of Fagonia indica: A preclinical scientific validation of indigenous herb for the treatment of β-hemoglobinopathies
Iftikhar, Fizza, Khan, Muhammad Behroz Naeem, Tehreem, Syeda, Kanwal, Nayab, Musharraf, Syed Ghulam
Published in Bioorganic chemistry (01.11.2023)
Published in Bioorganic chemistry (01.11.2023)
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Journal Article
XMN polymorphism along with HU administration renders alterations to RBC membrane lipidome in β-thalassemia patients
Khan, Muhammad Behroz Naeem, Iftikhar, Fizza, Ali, Muhammad, Danish, Asma, Shamsi, Tahir, Musharraf, Syed Ghulam, Siddiqui, Amna Jabbar
Published in Chemistry and physics of lipids (01.05.2022)
Published in Chemistry and physics of lipids (01.05.2022)
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Journal Article
IVS I-5 (G > C) is associated with changes to the RBC membrane lipidome in response to hydroxyurea treatment in β-thalassemia patients
Khan, Muhammad Behroz Naeem, Iftikhar, Fizza, Khan, Tajwali, Danish, Asma, Shamsi, Tahir, Musharraf, Syed Ghulam, Siddiqui, Amna Jabbar
Published in Molecular omics (11.07.2022)
Published in Molecular omics (11.07.2022)
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Journal Article