EE401 A Comparison of Health State Occupancy Between Cipaglucosidase Alfa/Miglustat and Alglucosidase Alfa Within a Cost-Effectiveness Modelling Analysis of Late-Onset Pompe Disease
Raza, S., Dymond, A., Green, W., Graham, R., Keyzor, I., Johnson, N., MacCulloch, A., Shohet, S.
Published in Value in health (01.12.2023)
Published in Value in health (01.12.2023)
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Journal Article
HTA103 Systematic Literature Reviews to Identify Clinical and Economic Outcomes in Adults With Pompe Disease
Raza, S., Keyzor, I., Clarke, S., McCaughey, G., Bolan, F., Kaut, J., Ashworth, L., Thurtle, E., Johnson, N.
Published in Value in health (01.12.2023)
Published in Value in health (01.12.2023)
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Journal Article
PCR67 Association of Walking Distance with Quality of Life and Other Patient-Reported Outcomes in Pompe Disease
Raza, S, Keyzor, I, Shohet, S, Chandak, A, Cheng, A, Hummel, N
Published in Value in health (01.07.2022)
Published in Value in health (01.07.2022)
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Journal Article
POSA283 Differential Appraisal of Functional Outcome Measures by Health Technology Assessment (HTA) Agencies When Reviewing Therapies for Rare Muscular, Skeletal and Neurodegenerative Disorders
Raza, S, Keyzor, I, Shohet, S, Zalewska, M, Hummel, N, Brougham, M
Published in Value in health (01.01.2022)
Published in Value in health (01.01.2022)
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Journal Article
RWD131 Investigating Resource Costs and the Experiences of Patients and Healthcare Professionals in the Treatment of Fabry Disease With Enzyme Replacement Therapy – A Multi-Country Study
Keyzor, I, Maria Martins, A, Kalkan Uçar, S, Yamakawa, H, Giuliano, J, Shohet, S, Baldock, L, Andiappan, M
Published in Value in health (01.12.2022)
Published in Value in health (01.12.2022)
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Journal Article
PRO61 Health-Related Quality of Life (HRQOL) and Healthcare Resource Use (HCRU) Associated with the Treatment of Pompe Disease (PD): Targeted Literature Reviews
Keyzor, I., Shohet, S., Fox, B., Sitaraman, S., Bartlett, C., Arber, M., Mahon, J.
Published in Value in health (01.06.2021)
Published in Value in health (01.06.2021)
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